-
1
-
-
80053552544
-
Viral and non-viral approaches for transient delivery of mRNA and proteins
-
J.W. Schott, M. Galla, T. Godinho, C. Baum, and A. Schambach Viral and non-viral approaches for transient delivery of mRNA and proteins Curr Gene Ther 11 2011 382 398
-
(2011)
Curr Gene Ther
, vol.11
, pp. 382-398
-
-
Schott, J.W.1
Galla, M.2
Godinho, T.3
Baum, C.4
Schambach, A.5
-
2
-
-
6344243521
-
Retroviral pseudotransduction for targeted cell manipulation
-
M. Galla, E. Will, J. Kraunus, L. Chen, and C. Baum Retroviral pseudotransduction for targeted cell manipulation Mol Cell 16 2004 309 315
-
(2004)
Mol Cell
, vol.16
, pp. 309-315
-
-
Galla, M.1
Will, E.2
Kraunus, J.3
Chen, L.4
Baum, C.5
-
3
-
-
84910142498
-
Improved retroviral episome transfer of transcription factors enables sustained cell fate modification
-
J.W. Schott, D. Hoffmann, T. Maetzig, F.J. Müller, D. Steinemann, D. Zychlinski, T. Cantz, C. Baum, and A. Schambach Improved retroviral episome transfer of transcription factors enables sustained cell fate modification Gene Ther 21 2014 938 949
-
(2014)
Gene Ther
, vol.21
, pp. 938-949
-
-
Schott, J.W.1
Hoffmann, D.2
Maetzig, T.3
Müller, F.J.4
Steinemann, D.5
Zychlinski, D.6
Cantz, T.7
Baum, C.8
Schambach, A.9
-
4
-
-
33646875083
-
Retrovirus vectors: Toward the plentivirus?
-
C. Baum, A. Schambach, J. Bohne, and M. Galla Retrovirus vectors: toward the plentivirus? Mol Ther 13 2006 1050 1063
-
(2006)
Mol Ther
, vol.13
, pp. 1050-1063
-
-
Baum, C.1
Schambach, A.2
Bohne, J.3
Galla, M.4
-
5
-
-
79957792110
-
Gammaretroviral vectors: Biology, technology and application
-
T. Maetzig, M. Galla, C. Baum, and A. Schambach Gammaretroviral vectors: biology, technology and application Viruses 3 2011 677 713
-
(2011)
Viruses
, vol.3
, pp. 677-713
-
-
Maetzig, T.1
Galla, M.2
Baum, C.3
Schambach, A.4
-
6
-
-
68249112926
-
Integration-deficient lentiviral vectors: A slow coming of age
-
K. Wanisch, and R.J. Yáñez-Muñoz Integration-deficient lentiviral vectors: a slow coming of age Mol Ther 17 2009 1316 1332
-
(2009)
Mol Ther
, vol.17
, pp. 1316-1332
-
-
Wanisch, K.1
Yáñez-Muñoz, R.J.2
-
7
-
-
84867004626
-
Retroviral protein transfer: Falling apart to make an impact
-
T. Maetzig, C. Baum, and A. Schambach Retroviral protein transfer: falling apart to make an impact Curr Gene Ther 12 2012 389 409
-
(2012)
Curr Gene Ther
, vol.12
, pp. 389-409
-
-
Maetzig, T.1
Baum, C.2
Schambach, A.3
-
8
-
-
0031710033
-
A third-generation lentivirus vector with a conditional packaging system
-
T. Dull, R. Zufferey, M. Kelly, R.J. Mandel, M. Nguyen, D. Trono, and L. Naldini A third-generation lentivirus vector with a conditional packaging system J Virol 72 1998 8463 8471
-
(1998)
J Virol
, vol.72
, pp. 8463-8471
-
-
Dull, T.1
Zufferey, R.2
Kelly, M.3
Mandel, R.J.4
Nguyen, M.5
Trono, D.6
Naldini, L.7
-
9
-
-
27744489220
-
Silencing and variegation of gammaretrovirus and lentivirus vectors
-
J. Ellis Silencing and variegation of gammaretrovirus and lentivirus vectors Hum Gene Ther 16 2005 1241 1246
-
(2005)
Hum Gene Ther
, vol.16
, pp. 1241-1246
-
-
Ellis, J.1
-
10
-
-
84862785016
-
Chromatin domains, insulators, and the regulation of gene expression
-
R. Ghirlando, K. Giles, H. Gowher, T. Xiao, Z. Xu, H. Yao, and G. Felsenfeld Chromatin domains, insulators, and the regulation of gene expression Biochim Biophys Acta 1819 2012 644 651
-
(2012)
Biochim Biophys Acta
, vol.1819
, pp. 644-651
-
-
Ghirlando, R.1
Giles, K.2
Gowher, H.3
Xiao, T.4
Xu, Z.5
Yao, H.6
Felsenfeld, G.7
-
11
-
-
84881313556
-
Kinetics and epigenetics of retroviral silencing in mouse embryonic stem cells defined by deletion of the D4Z4 element
-
S. Rival-Gervier, M.Y. Lo, S. Khattak, P. Pasceri, M.C. Lorincz, and J. Ellis Kinetics and epigenetics of retroviral silencing in mouse embryonic stem cells defined by deletion of the D4Z4 element Mol Ther 21 2013 1536 1550
-
(2013)
Mol Ther
, vol.21
, pp. 1536-1550
-
-
Rival-Gervier, S.1
Lo, M.Y.2
Khattak, S.3
Pasceri, P.4
Lorincz, M.C.5
Ellis, J.6
-
12
-
-
0023663887
-
Position-independent, high-level expression of the human beta-globin gene in transgenic mice
-
F. Grosveld, G.B. van Assendelft, D.R. Greaves, and G. Kollias Position-independent, high-level expression of the human beta-globin gene in transgenic mice Cell 51 1987 975 985
-
(1987)
Cell
, vol.51
, pp. 975-985
-
-
Grosveld, F.1
Van Assendelft, G.B.2
Greaves, D.R.3
Kollias, G.4
-
13
-
-
4944234406
-
Extended beta-globin locus control region elements promote consistent therapeutic expression of a gamma-globin lentiviral vector in murine beta-thalassemia
-
H. Hanawa, P.W. Hargrove, S. Kepes, D.K. Srivastava, A.W. Nienhuis, and D.A. Persons Extended beta-globin locus control region elements promote consistent therapeutic expression of a gamma-globin lentiviral vector in murine beta-thalassemia Blood 104 2004 2281 2290
-
(2004)
Blood
, vol.104
, pp. 2281-2290
-
-
Hanawa, H.1
Hargrove, P.W.2
Kepes, S.3
Srivastava, D.K.4
Nienhuis, A.W.5
Persons, D.A.6
-
14
-
-
84876575492
-
Optimizing retroviral gene expression for effective therapies
-
M.N. Antoniou, K.A. Skipper, and O. Anakok Optimizing retroviral gene expression for effective therapies Hum Gene Ther 24 2013 363 374
-
(2013)
Hum Gene Ther
, vol.24
, pp. 363-374
-
-
Antoniou, M.N.1
Skipper, K.A.2
Anakok, O.3
-
15
-
-
77956265818
-
A ubiquitous chromatin opening element (UCOE) confers resistance to DNA methylation-mediated silencing of lentiviral vectors
-
F. Zhang, A.R. Frost, M.P. Blundell, O. Bales, M.N. Antoniou, and A.J. Thrasher A ubiquitous chromatin opening element (UCOE) confers resistance to DNA methylation-mediated silencing of lentiviral vectors Mol Ther 18 2010 1640 1649
-
(2010)
Mol Ther
, vol.18
, pp. 1640-1649
-
-
Zhang, F.1
Frost, A.R.2
Blundell, M.P.3
Bales, O.4
Antoniou, M.N.5
Thrasher, A.J.6
-
16
-
-
84867402831
-
Physiological regulation of transgene expression by a lentiviral vector containing the A2UCOE linked to a myeloid promoter
-
C. Brendel, U. Muller-Kuller, S. Schultze-Strasser, S. Stein, L. Chen-Wichmann, A. Krattenmacher, H. Kunkel, A. Dillmann, M.N. Antoniou, and M. Grez Physiological regulation of transgene expression by a lentiviral vector containing the A2UCOE linked to a myeloid promoter Gene Ther 19 2012 1018 1029
-
(2012)
Gene Ther
, vol.19
, pp. 1018-1029
-
-
Brendel, C.1
Muller-Kuller, U.2
Schultze-Strasser, S.3
Stein, S.4
Chen-Wichmann, L.5
Krattenmacher, A.6
Kunkel, H.7
Dillmann, A.8
Antoniou, M.N.9
Grez, M.10
-
17
-
-
84874870904
-
A ubiquitous chromatin opening element prevents transgene silencing in pluripotent stem cells and their differentiated progeny
-
N. Pfaff, N. Lachmann, M. Ackermann, S. Kohlscheen, C. Brendel, T. Maetzig, H. Niemann, M.N. Antoniou, M. Grez, A. Schambach, and et al. A ubiquitous chromatin opening element prevents transgene silencing in pluripotent stem cells and their differentiated progeny Stem Cells 31 2013 488 499
-
(2013)
Stem Cells
, vol.31
, pp. 488-499
-
-
Pfaff, N.1
Lachmann, N.2
Ackermann, M.3
Kohlscheen, S.4
Brendel, C.5
Maetzig, T.6
Niemann, H.7
Antoniou, M.N.8
Grez, M.9
Schambach, A.10
-
18
-
-
84890141894
-
Promoter and lineage independent anti-silencing activity of the A2 ubiquitous chromatin opening element for optimized human pluripotent stem cell-based gene therapy
-
M. Ackermann, N. Lachmann, S. Hartung, R. Eggenschwiler, N. Pfaff, C. Happle, A. Mucci, G. Gohring, H. Niemann, G. Hansen, and et al. Promoter and lineage independent anti-silencing activity of the A2 ubiquitous chromatin opening element for optimized human pluripotent stem cell-based gene therapy Biomaterials 35 2014 1531 1542
-
(2014)
Biomaterials
, vol.35
, pp. 1531-1542
-
-
Ackermann, M.1
Lachmann, N.2
Hartung, S.3
Eggenschwiler, R.4
Pfaff, N.5
Happle, C.6
Mucci, A.7
Gohring, G.8
Niemann, H.9
Hansen, G.10
-
19
-
-
84936777038
-
A minimal ubiquitous chromatin opening element (UCOE) effectively prevents silencing of juxtaposed heterologous promoters by epigenetic remodeling in multipotent and pluripotent stem cells
-
U. Müller-Kuller, M. Ackermann, S. Kolodziej, C. Brendel, J. Fritsch, N. Lachmann, H. Kunkel, J. Lausen, A. Schambach, T. Moritz, and et al. A minimal ubiquitous chromatin opening element (UCOE) effectively prevents silencing of juxtaposed heterologous promoters by epigenetic remodeling in multipotent and pluripotent stem cells Nucleic Acids Res 43 2015 1577 1592
-
(2015)
Nucleic Acids Res
, vol.43
, pp. 1577-1592
-
-
Müller-Kuller, U.1
Ackermann, M.2
Kolodziej, S.3
Brendel, C.4
Fritsch, J.5
Lachmann, N.6
Kunkel, H.7
Lausen, J.8
Schambach, A.9
Moritz, T.10
-
20
-
-
33947373010
-
High-frequency epigenetic repression and silencing of retroviruses can be antagonized by histone deacetylase inhibitors and transcriptional activators, but uniform reactivation in cell clones is restricted by additional mechanisms
-
R.A. Katz, E. Jack-Scott, A. Narezkina, I. Palagin, P. Boimel, J. Kulkosky, E. Nicolas, J.G. Greger, and A.M. Skalka High-frequency epigenetic repression and silencing of retroviruses can be antagonized by histone deacetylase inhibitors and transcriptional activators, but uniform reactivation in cell clones is restricted by additional mechanisms J Virol 81 2007 2592 2604
-
(2007)
J Virol
, vol.81
, pp. 2592-2604
-
-
Katz, R.A.1
Jack-Scott, E.2
Narezkina, A.3
Palagin, I.4
Boimel, P.5
Kulkosky, J.6
Nicolas, E.7
Greger, J.G.8
Skalka, A.M.9
-
21
-
-
84878870410
-
Vectofusin-1, a new viral entry enhancer, strongly promotes lentiviral transduction of human hematopoietic stem cells
-
D. Fenard, D. Ingrao, A. Seye, J. Buisset, S. Genries, S. Martin, A. Kichler, and A. Galy Vectofusin-1, a new viral entry enhancer, strongly promotes lentiviral transduction of human hematopoietic stem cells Mol Ther Nucleic Acids 2 2013 e90
-
(2013)
Mol Ther Nucleic Acids
, vol.2
, pp. e90
-
-
Fenard, D.1
Ingrao, D.2
Seye, A.3
Buisset, J.4
Genries, S.5
Martin, S.6
Kichler, A.7
Galy, A.8
-
22
-
-
84927175081
-
High-throughput screening identifies compounds that enhance lentiviral transduction
-
J.M. Johnston, G. Denning, R. Moot, D. Whitehead, J. Shields, J.M. Le Doux, C.B. Doering, and H.T. Spencer High-throughput screening identifies compounds that enhance lentiviral transduction Gene Ther 21 2014 1008 1020
-
(2014)
Gene Ther
, vol.21
, pp. 1008-1020
-
-
Johnston, J.M.1
Denning, G.2
Moot, R.3
Whitehead, D.4
Shields, J.5
Le Doux, J.M.6
Doering, C.B.7
Spencer, H.T.8
-
23
-
-
0037448352
-
A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency
-
S. Hacein-Bey-Abina, C. von Kalle, M. Schmidt, F. Le Deist, N. Wulffraat, E. McIntyre, I. Radford, J.L. Villeval, C.C. Fraser, M. Cavazzana-Calvo, and et al. A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency N Engl J Med 348 2003 255 256
-
(2003)
N Engl J Med
, vol.348
, pp. 255-256
-
-
Hacein-Bey-Abina, S.1
Von Kalle, C.2
Schmidt, M.3
Le Deist, F.4
Wulffraat, N.5
McIntyre, E.6
Radford, I.7
Villeval, J.L.8
Fraser, C.C.9
Cavazzana-Calvo, M.10
-
24
-
-
0142084745
-
LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1
-
S. Hacein-Bey-Abina, C. Von Kalle, M. Schmidt, M.P. McCormack, N. Wulffraat, P. Leboulch, A. Lim, C.S. Osborne, R. Pawliuk, E. Morillon, and et al. LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1 Science 302 2003 415 419
-
(2003)
Science
, vol.302
, pp. 415-419
-
-
Hacein-Bey-Abina, S.1
Von Kalle, C.2
Schmidt, M.3
McCormack, M.P.4
Wulffraat, N.5
Leboulch, P.6
Lim, A.7
Osborne, C.S.8
Pawliuk, R.9
Morillon, E.10
-
25
-
-
51349090473
-
Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1
-
S. Hacein-Bey-Abina, A. Garrigue, G.P. Wang, J. Soulier, A. Lim, E. Morillon, E. Clappier, L. Caccavelli, E. Delabesse, K. Beldjord, and et al. Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1 J Clin Invest 118 2008 3132 3142
-
(2008)
J Clin Invest
, vol.118
, pp. 3132-3142
-
-
Hacein-Bey-Abina, S.1
Garrigue, A.2
Wang, G.P.3
Soulier, J.4
Lim, A.5
Morillon, E.6
Clappier, E.7
Caccavelli, L.8
Delabesse, E.9
Beldjord, K.10
-
26
-
-
51349158298
-
Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients
-
S.J. Howe, M.R. Mansour, K. Schwarzwaelder, C. Bartholomae, M. Hubank, H. Kempski, M.H. Brugman, K. Pike-Overzet, S.J. Chatters, D. de Ridder, and et al. Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients J Clin Invest 118 2008 3143 3150
-
(2008)
J Clin Invest
, vol.118
, pp. 3143-3150
-
-
Howe, S.J.1
Mansour, M.R.2
Schwarzwaelder, K.3
Bartholomae, C.4
Hubank, M.5
Kempski, H.6
Brugman, M.H.7
Pike-Overzet, K.8
Chatters, S.J.9
De Ridder, D.10
-
27
-
-
76249131912
-
Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease
-
S. Stein, M.G. Ott, S. Schultze-Strasser, A. Jauch, B. Burwinkel, A. Kinner, M. Schmidt, A. Kramer, J. Schwable, H. Glimm, and et al. Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease Nat Med 16 2010 198 204
-
(2010)
Nat Med
, vol.16
, pp. 198-204
-
-
Stein, S.1
Ott, M.G.2
Schultze-Strasser, S.3
Jauch, A.4
Burwinkel, B.5
Kinner, A.6
Schmidt, M.7
Kramer, A.8
Schwable, J.9
Glimm, H.10
-
28
-
-
84897550064
-
Gene therapy for Wiskott-Aldrich syndrome - Long-term efficacy and genotoxicity
-
C.J. Braun, K. Boztug, A. Paruzynski, M. Witzel, A. Schwarzer, M. Rothe, U. Modlich, R. Beier, G. Gohring, D. Steinemann, and et al. Gene therapy for Wiskott-Aldrich syndrome - long-term efficacy and genotoxicity Sci Transl Med 6 2014 227ra33
-
(2014)
Sci Transl Med
, vol.6
, pp. 227ra33
-
-
Braun, C.J.1
Boztug, K.2
Paruzynski, A.3
Witzel, M.4
Schwarzer, A.5
Rothe, M.6
Modlich, U.7
Beier, R.8
Gohring, G.9
Steinemann, D.10
-
29
-
-
0037162715
-
HIV-1 integration in the human genome favors active genes and local hotspots
-
A.R. Schröder, P. Shinn, H. Chen, C. Berry, J.R. Ecker, and F. Bushman HIV-1 integration in the human genome favors active genes and local hotspots Cell 110 2002 521 529
-
(2002)
Cell
, vol.110
, pp. 521-529
-
-
Schröder, A.R.1
Shinn, P.2
Chen, H.3
Berry, C.4
Ecker, J.R.5
Bushman, F.6
-
30
-
-
0037841763
-
Transcription start regions in the human genome are favored targets for MLV integration
-
X. Wu, Y. Li, B. Crise, and S.M. Burgess Transcription start regions in the human genome are favored targets for MLV integration Science 300 2003 1749 1751
-
(2003)
Science
, vol.300
, pp. 1749-1751
-
-
Wu, X.1
Li, Y.2
Crise, B.3
Burgess, S.M.4
-
31
-
-
19344375031
-
Retroviral DNA integration: ASLV, HIV, and MLV show distinct target site preferences
-
R.S. Mitchell, B.F. Beitzel, A.R. Schroder, P. Shinn, H. Chen, C.C. Berry, J.R. Ecker, and F.D. Bushman Retroviral DNA integration: ASLV, HIV, and MLV show distinct target site preferences PLoS Biol 2 2004 E234
-
(2004)
PLoS Biol
, vol.2
, pp. E234
-
-
Mitchell, R.S.1
Beitzel, B.F.2
Schroder, A.R.3
Shinn, P.4
Chen, H.5
Berry, C.C.6
Ecker, J.R.7
Bushman, F.D.8
-
32
-
-
70449127230
-
Insertional transformation of hematopoietic cells by self-inactivating lentiviral and gammaretroviral vectors
-
U. Modlich, S. Navarro, D. Zychlinski, T. Maetzig, S. Knoess, M.H. Brugman, A. Schambach, S. Charrier, A. Galy, A.J. Thrasher, and et al. Insertional transformation of hematopoietic cells by self-inactivating lentiviral and gammaretroviral vectors Mol Ther 17 2009 1919 1928
-
(2009)
Mol Ther
, vol.17
, pp. 1919-1928
-
-
Modlich, U.1
Navarro, S.2
Zychlinski, D.3
Maetzig, T.4
Knoess, S.5
Brugman, M.H.6
Schambach, A.7
Charrier, S.8
Galy, A.9
Thrasher, A.J.10
-
33
-
-
84924764258
-
Safety of gene therapy: New insights to a puzzling case
-
M. Rothe, A. Schambach, and L. Biasco Safety of gene therapy: new insights to a puzzling case Curr Gene Ther 14 2014 429 436
-
(2014)
Curr Gene Ther
, vol.14
, pp. 429-436
-
-
Rothe, M.1
Schambach, A.2
Biasco, L.3
-
34
-
-
70449427834
-
Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy
-
N. Cartier, S. Hacein-Bey-Abina, C.C. Bartholomae, G. Veres, M. Schmidt, I. Kutschera, M. Vidaud, U. Abel, L. Dal-Cortivo, L. Caccavelli, and et al. Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy Science 326 2009 818 823
-
(2009)
Science
, vol.326
, pp. 818-823
-
-
Cartier, N.1
Hacein-Bey-Abina, S.2
Bartholomae, C.C.3
Veres, G.4
Schmidt, M.5
Kutschera, I.6
Vidaud, M.7
Abel, U.8
Dal-Cortivo, L.9
Caccavelli, L.10
-
35
-
-
77956928344
-
Transfusion independence and HMGA2 activation after gene therapy of human beta-thalassaemia
-
M. Cavazzana-Calvo, E. Payen, O. Negre, G. Wang, K. Hehir, F. Fusil, J. Down, M. Denaro, T. Brady, K. Westerman, and et al. Transfusion independence and HMGA2 activation after gene therapy of human beta-thalassaemia Nature 467 2010 318 322
-
(2010)
Nature
, vol.467
, pp. 318-322
-
-
Cavazzana-Calvo, M.1
Payen, E.2
Negre, O.3
Wang, G.4
Hehir, K.5
Fusil, F.6
Down, J.7
Denaro, M.8
Brady, T.9
Westerman, K.10
-
36
-
-
84879867061
-
Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome
-
A. Aiuti, L. Biasco, S. Scaramuzza, F. Ferrua, M.P. Cicalese, C. Baricordi, F. Dionisio, A. Calabria, S. Giannelli, M.C. Castiello, and et al. Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome Science 341 2013 1233151
-
(2013)
Science
, vol.341
, pp. 1233151
-
-
Aiuti, A.1
Biasco, L.2
Scaramuzza, S.3
Ferrua, F.4
Cicalese, M.P.5
Baricordi, C.6
Dionisio, F.7
Calabria, A.8
Giannelli, S.9
Castiello, M.C.10
-
37
-
-
84879873039
-
Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy
-
A. Biffi, E. Montini, L. Lorioli, M. Cesani, F. Fumagalli, T. Plati, C. Baldoli, S. Martino, A. Calabria, S. Canale, and et al. Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy Science 341 2013 1233158
-
(2013)
Science
, vol.341
, pp. 1233158
-
-
Biffi, A.1
Montini, E.2
Lorioli, L.3
Cesani, M.4
Fumagalli, F.5
Plati, T.6
Baldoli, C.7
Martino, S.8
Calabria, A.9
Canale, S.10
-
38
-
-
65249101260
-
The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy
-
E. Montini, D. Cesana, M. Schmidt, F. Sanvito, C.C. Bartholomae, M. Ranzani, F. Benedicenti, L.S. Sergi, A. Ambrosi, M. Ponzoni, and et al. The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy J Clin Invest 119 2009 964 975
-
(2009)
J Clin Invest
, vol.119
, pp. 964-975
-
-
Montini, E.1
Cesana, D.2
Schmidt, M.3
Sanvito, F.4
Bartholomae, C.C.5
Ranzani, M.6
Benedicenti, F.7
Sergi, L.S.8
Ambrosi, A.9
Ponzoni, M.10
-
39
-
-
0346132122
-
Self-inactivating retroviral vectors designed for transfer of whole genes into mammalian cells
-
S.F. Yu, T. von Rüden, P.W. Kantoff, C. Garber, M. Seiberg, U. Rüther, W.F. Anderson, E.F. Wagner, and E. Gilboa Self-inactivating retroviral vectors designed for transfer of whole genes into mammalian cells Proc Natl Acad Sci U S A 83 1986 3194 3198
-
(1986)
Proc Natl Acad Sci U S A
, vol.83
, pp. 3194-3198
-
-
Yu, S.F.1
Von Rüden, T.2
Kantoff, P.W.3
Garber, C.4
Seiberg, M.5
Rüther, U.6
Anderson, W.F.7
Wagner, E.F.8
Gilboa, E.9
-
40
-
-
0031743608
-
Self-inactivating lentivirus vector for safe and efficient in vivo gene delivery
-
R. Zufferey, T. Dull, R.J. Mandel, A. Bukovsky, D. Quiroz, L. Naldini, and D. Trono Self-inactivating lentivirus vector for safe and efficient in vivo gene delivery J Virol 72 1998 9873 9880
-
(1998)
J Virol
, vol.72
, pp. 9873-9880
-
-
Zufferey, R.1
Dull, T.2
Mandel, R.J.3
Bukovsky, A.4
Quiroz, D.5
Naldini, L.6
Trono, D.7
-
41
-
-
84907880404
-
A modified gamma-retrovirus vector for X-linked severe combined immunodeficiency
-
S. Hacein-Bey-Abina, S.Y. Pai, H.B. Gaspar, M. Armant, C.C. Berry, S. Blanche, J. Bleesing, J. Blondeau, H. de Boer, K.F. Buckland, and et al. A modified gamma-retrovirus vector for X-linked severe combined immunodeficiency N Engl J Med 371 2014 1407 1417
-
(2014)
N Engl J Med
, vol.371
, pp. 1407-1417
-
-
Hacein-Bey-Abina, S.1
Pai, S.Y.2
Gaspar, H.B.3
Armant, M.4
Berry, C.C.5
Blanche, S.6
Bleesing, J.7
Blondeau, J.8
De Boer, H.9
Buckland, K.F.10
-
42
-
-
84860505761
-
Alpharetroviral self-inactivating vectors: Long-term transgene expression in murine hematopoietic cells and low genotoxicity
-
J.D. Suerth, T. Maetzig, M.H. Brugman, N. Heinz, J.U. Appelt, K.B. Kaufmann, M. Schmidt, M. Grez, U. Modlich, C. Baum, and et al. Alpharetroviral self-inactivating vectors: long-term transgene expression in murine hematopoietic cells and low genotoxicity Mol Ther 20 2012 1022 1032
-
(2012)
Mol Ther
, vol.20
, pp. 1022-1032
-
-
Suerth, J.D.1
Maetzig, T.2
Brugman, M.H.3
Heinz, N.4
Appelt, J.U.5
Kaufmann, K.B.6
Schmidt, M.7
Grez, M.8
Modlich, U.9
Baum, C.10
-
43
-
-
84875218155
-
Alpharetroviral vector-mediated gene therapy for X-CGD: Functional correction and lack of aberrant splicing
-
K.B. Kaufmann, C. Brendel, J.D. Suerth, U. Mueller-Kuller, L. Chen-Wichmann, J. Schwable, S. Pahujani, H. Kunkel, A. Schambach, C. Baum, and et al. Alpharetroviral vector-mediated gene therapy for X-CGD: functional correction and lack of aberrant splicing Mol Ther 21 2013 648 661
-
(2013)
Mol Ther
, vol.21
, pp. 648-661
-
-
Kaufmann, K.B.1
Brendel, C.2
Suerth, J.D.3
Mueller-Kuller, U.4
Chen-Wichmann, L.5
Schwable, J.6
Pahujani, S.7
Kunkel, H.8
Schambach, A.9
Baum, C.10
-
44
-
-
84902261338
-
Genome-wide analysis of alpharetroviral integration in human hematopoietic stem/progenitor cells
-
A. Moiani, J.D. Suerth, F. Gandolfi, E. Rizzi, M. Severgnini, G. De Bellis, A. Schambach, and F. Mavilio Genome-wide analysis of alpharetroviral integration in human hematopoietic stem/progenitor cells Genes (Basel) 5 2014 415 429
-
(2014)
Genes (Basel)
, vol.5
, pp. 415-429
-
-
Moiani, A.1
Suerth, J.D.2
Gandolfi, F.3
Rizzi, E.4
Severgnini, M.5
De Bellis, G.6
Schambach, A.7
Mavilio, F.8
-
45
-
-
76749152709
-
Integrase-defective lentiviral vectors: Progress and applications
-
M.B. Banasik, and P.B. McCray Jr. Integrase-defective lentiviral vectors: progress and applications Gene Ther 17 2010 150 157
-
(2010)
Gene Ther
, vol.17
, pp. 150-157
-
-
Banasik, M.B.1
McCray Jr, . P.B.2
-
46
-
-
56749185598
-
A large U3 deletion causes increased in vivo expression from a nonintegrating lentiviral vector
-
M. Bayer, B. Kantor, A. Cockrell, H. Ma, B. Zeithaml, X. Li, T. McCown, and T. Kafri A large U3 deletion causes increased in vivo expression from a nonintegrating lentiviral vector Mol Ther 16 2008 1968 1976
-
(2008)
Mol Ther
, vol.16
, pp. 1968-1976
-
-
Bayer, M.1
Kantor, B.2
Cockrell, A.3
Ma, H.4
Zeithaml, B.5
Li, X.6
McCown, T.7
Kafri, T.8
-
47
-
-
0036200163
-
Intrinsic stability of episomal circles formed during human immunodeficiency virus type 1 replication
-
T.C. Pierson, T.L. Kieffer, C.T. Ruff, C. Buck, S.J. Gange, and R.F. Siliciano Intrinsic stability of episomal circles formed during human immunodeficiency virus type 1 replication J Virol 76 2002 4138 4144
-
(2002)
J Virol
, vol.76
, pp. 4138-4144
-
-
Pierson, T.C.1
Kieffer, T.L.2
Ruff, C.T.3
Buck, C.4
Gange, S.J.5
Siliciano, R.F.6
-
48
-
-
35548987090
-
Stable gene transfer to muscle using non-integrating lentiviral vectors
-
L. Apolonia, S.N. Waddington, C. Fernandes, N.J. Ward, G. Bouma, M.P. Blundell, A.J. Thrasher, M.K. Collins, and N.J. Philpott Stable gene transfer to muscle using non-integrating lentiviral vectors Mol Ther 15 2007 1947 1954
-
(2007)
Mol Ther
, vol.15
, pp. 1947-1954
-
-
Apolonia, L.1
Waddington, S.N.2
Fernandes, C.3
Ward, N.J.4
Bouma, G.5
Blundell, M.P.6
Thrasher, A.J.7
Collins, M.K.8
Philpott, N.J.9
-
49
-
-
33644822908
-
Effective gene therapy with nonintegrating lentiviral vectors
-
R.J. Yáñez-Muñoz, K.S. Balaggan, A. MacNeil, S.J. Howe, M. Schmidt, A.J. Smith, P. Buch, R.E. MacLaren, P.N. Anderson, S.E. Barker, and et al. Effective gene therapy with nonintegrating lentiviral vectors Nat Med 12 2006 348 353
-
(2006)
Nat Med
, vol.12
, pp. 348-353
-
-
Yáñez-Muñoz, R.J.1
Balaggan, K.S.2
MacNeil, A.3
Howe, S.J.4
Schmidt, M.5
Smith, A.J.6
Buch, P.7
MacLaren, R.E.8
Anderson, P.N.9
Barker, S.E.10
-
50
-
-
33845187432
-
Lentiviral vectors with a defective integrase allow efficient and sustained transgene expression in vitro and in vivo
-
S. Philippe, C. Sarkis, M. Barkats, H. Mammeri, C. Ladroue, C. Petit, J. Mallet, and C. Serguera Lentiviral vectors with a defective integrase allow efficient and sustained transgene expression in vitro and in vivo Proc Natl Acad Sci U S A 103 2006 17684 17689
-
(2006)
Proc Natl Acad Sci U S A
, vol.103
, pp. 17684-17689
-
-
Philippe, S.1
Sarkis, C.2
Barkats, M.3
Mammeri, H.4
Ladroue, C.5
Petit, C.6
Mallet, J.7
Serguera, C.8
-
51
-
-
84898989692
-
S/MAR sequence confers long-term mitotic stability on non-integrating lentiviral vector episomes without selection
-
S.C. Verghese, N.A. Goloviznina, A.M. Skinner, H.J. Lipps, and P. Kurre S/MAR sequence confers long-term mitotic stability on non-integrating lentiviral vector episomes without selection Nucleic Acids Res 42 2014 e53
-
(2014)
Nucleic Acids Res
, vol.42
, pp. e53
-
-
Verghese, S.C.1
Goloviznina, N.A.2
Skinner, A.M.3
Lipps, H.J.4
Kurre, P.5
-
52
-
-
56349129585
-
Conditionally replicating lentiviral-hybrid episomal vectors for suicide gene therapy
-
J. Vargas Jr., M.E. Klotman, and A. Cara Conditionally replicating lentiviral-hybrid episomal vectors for suicide gene therapy Antiviral Res 80 2008 288 294
-
(2008)
Antiviral Res
, vol.80
, pp. 288-294
-
-
Vargas Jr, . J.1
Klotman, M.E.2
Cara, A.3
-
53
-
-
0347949575
-
Simian virus 40-based replication of catalytically inactive human immunodeficiency virus type 1 integrase mutants in nonpermissive T cells and monocyte-derived macrophages
-
R. Lu, N. Nakajima, W. Hofmann, M. Benkirane, K.T. Jeang, J. Sodroski, and A. Engelman Simian virus 40-based replication of catalytically inactive human immunodeficiency virus type 1 integrase mutants in nonpermissive T cells and monocyte-derived macrophages J Virol 78 2004 658 668
-
(2004)
J Virol
, vol.78
, pp. 658-668
-
-
Lu, R.1
Nakajima, N.2
Hofmann, W.3
Benkirane, M.4
Jeang, K.T.5
Sodroski, J.6
Engelman, A.7
-
54
-
-
84901203834
-
Long-term episomal transgene expression from mitotically stable integration-deficient lentiviral vectors
-
H. Kymäläinen, J.U. Appelt, F.A. Giordano, A.F. Davies, C.M. Ogilvie, S.G. Ahmed, S. Laufs, M. Schmidt, J. Bode, R.J. Yáñez-Muñoz, and et al. Long-term episomal transgene expression from mitotically stable integration-deficient lentiviral vectors Hum Gene Ther 25 2014 428 442
-
(2014)
Hum Gene Ther
, vol.25
, pp. 428-442
-
-
Kymäläinen, H.1
Appelt, J.U.2
Giordano, F.A.3
Davies, A.F.4
Ogilvie, C.M.5
Ahmed, S.G.6
Laufs, S.7
Schmidt, M.8
Bode, J.9
Yáñez-Muñoz, R.J.10
-
55
-
-
84928190908
-
Deciphering the impact of parameters influencing transgene expression kinetics after repeated cell transduction with integration-deficient retroviral vectors
-
J.W. Schott, N.M. Jaeschke, D. Hoffmann, T. Maetzig, M. Ballmaier, T. Godinho, T. Cathomen, and A. Schambach Deciphering the impact of parameters influencing transgene expression kinetics after repeated cell transduction with integration-deficient retroviral vectors Cytometry A 2015
-
(2015)
Cytometry A
-
-
Schott, J.W.1
Jaeschke, N.M.2
Hoffmann, D.3
Maetzig, T.4
Ballmaier, M.5
Godinho, T.6
Cathomen, T.7
Schambach, A.8
-
56
-
-
84898659454
-
Non-integrating gamma-retroviral vectors as a versatile tool for transient zinc-finger nuclease delivery
-
S. Bobis-Wozowicz, M. Galla, J. Alzubi, J. Kuehle, C. Baum, A. Schambach, and T. Cathomen Non-integrating gamma-retroviral vectors as a versatile tool for transient zinc-finger nuclease delivery Sci Rep 4 2014 4656
-
(2014)
Sci Rep
, vol.4
, pp. 4656
-
-
Bobis-Wozowicz, S.1
Galla, M.2
Alzubi, J.3
Kuehle, J.4
Baum, C.5
Schambach, A.6
Cathomen, T.7
-
57
-
-
1842686860
-
Novel integrase-defective lentiviral episomal vectors for gene transfer
-
J. Vargas Jr., G.L. Gusella, V. Najfeld, M.E. Klotman, and A. Cara Novel integrase-defective lentiviral episomal vectors for gene transfer Hum Gene Ther 15 2004 361 372
-
(2004)
Hum Gene Ther
, vol.15
, pp. 361-372
-
-
Vargas Jr, . J.1
Gusella, G.L.2
Najfeld, V.3
Klotman, M.E.4
Cara, A.5
-
58
-
-
0025720570
-
Productive human immunodeficiency virus type 1 (HIV-1) infection of nonproliferating human monocytes
-
J.B. Weinberg, T.J. Matthews, B.R. Cullen, and M.H. Malim Productive human immunodeficiency virus type 1 (HIV-1) infection of nonproliferating human monocytes J Exp Med 174 1991 1477 1482
-
(1991)
J Exp Med
, vol.174
, pp. 1477-1482
-
-
Weinberg, J.B.1
Matthews, T.J.2
Cullen, B.R.3
Malim, M.H.4
-
59
-
-
0026770379
-
Active nuclear import of human immunodeficiency virus type 1 preintegration complexes
-
M.I. Bukrinsky, N. Sharova, M.P. Dempsey, T.L. Stanwick, A.G. Bukrinskaya, S. Haggerty, and M. Stevenson Active nuclear import of human immunodeficiency virus type 1 preintegration complexes Proc Natl Acad Sci U S A 89 1992 6580 6584
-
(1992)
Proc Natl Acad Sci U S A
, vol.89
, pp. 6580-6584
-
-
Bukrinsky, M.I.1
Sharova, N.2
Dempsey, M.P.3
Stanwick, T.L.4
Bukrinskaya, A.G.5
Haggerty, S.6
Stevenson, M.7
-
60
-
-
0027158091
-
Integration of murine leukemia virus DNA depends on mitosis
-
T. Roe, T.C. Reynolds, G. Yu, and P.O. Brown Integration of murine leukemia virus DNA depends on mitosis Embo J 12 1993 2099 2108
-
(1993)
Embo J
, vol.12
, pp. 2099-2108
-
-
Roe, T.1
Reynolds, T.C.2
Yu, G.3
Brown, P.O.4
-
61
-
-
84857788410
-
MuLV in mutants responsive to HDAC inhibitors enhance transcription from unintegrated retroviral DNA
-
W.M. Schneider, D.T. Wu, V. Amin, S. Aiyer, and M.J. Roth MuLV IN mutants responsive to HDAC inhibitors enhance transcription from unintegrated retroviral DNA Virology 426 2012 188 196
-
(2012)
Virology
, vol.426
, pp. 188-196
-
-
Schneider, W.M.1
Wu, D.T.2
Amin, V.3
Aiyer, S.4
Roth, M.J.5
-
62
-
-
84872776482
-
Histone deacetylase inhibition activates transgene expression from integration-defective lentiviral vectors in dividing and non-dividing cells
-
L.P. Pelascini, J.M. Janssen, and M.A. Gonçalves Histone deacetylase inhibition activates transgene expression from integration-defective lentiviral vectors in dividing and non-dividing cells Hum Gene Ther 24 2013 78 96
-
(2013)
Hum Gene Ther
, vol.24
, pp. 78-96
-
-
Pelascini, L.P.1
Janssen, J.M.2
Gonçalves, M.A.3
-
63
-
-
84890362377
-
Histone deacetylase inhibition rescues gene knockout levels achieved with integrase-defective lentiviral vectors encoding zinc-finger nucleases
-
L.P. Pelascini, I. Maggio, J. Liu, M. Holkers, T. Cathomen, and M.A. Goncalves Histone deacetylase inhibition rescues gene knockout levels achieved with integrase-defective lentiviral vectors encoding zinc-finger nucleases Hum Gene Ther Methods 24 2013 399 411
-
(2013)
Hum Gene Ther Methods
, vol.24
, pp. 399-411
-
-
Pelascini, L.P.1
Maggio, I.2
Liu, J.3
Holkers, M.4
Cathomen, T.5
Goncalves, M.A.6
-
64
-
-
84895434154
-
Integration-deficient lentiviral vectors expressing codon-optimized R338L human FIX restore normal hemostasis in Hemophilia B mice
-
T. Suwanmanee, G. Hu, T. Gui, C.C. Bartholomae, I. Kutschera, C. von Kalle, M. Schmidt, P.E. Monahan, and T. Kafri Integration-deficient lentiviral vectors expressing codon-optimized R338L human FIX restore normal hemostasis in Hemophilia B mice Mol Ther 22 2014 567 574
-
(2014)
Mol Ther
, vol.22
, pp. 567-574
-
-
Suwanmanee, T.1
Hu, G.2
Gui, T.3
Bartholomae, C.C.4
Kutschera, I.5
Von Kalle, C.6
Schmidt, M.7
Monahan, P.E.8
Kafri, T.9
-
65
-
-
40049083276
-
Transient gene expression mediated by integrase-defective retroviral vectors
-
S.S. Yu, K. Dan, H. Chono, E. Chatani, J. Mineno, and I. Kato Transient gene expression mediated by integrase-defective retroviral vectors Biochem Biophys Res Commun 368 2008 942 947
-
(2008)
Biochem Biophys Res Commun
, vol.368
, pp. 942-947
-
-
Yu, S.S.1
Dan, K.2
Chono, H.3
Chatani, E.4
Mineno, J.5
Kato, I.6
-
66
-
-
33744468295
-
Transient gene expression by nonintegrating lentiviral vectors
-
S.J. Nightingale, R.P. Hollis, K.A. Pepper, D. Petersen, X.J. Yu, C. Yang, I. Bahner, and D.B. Kohn Transient gene expression by nonintegrating lentiviral vectors Mol Ther 13 2006 1121 1132
-
(2006)
Mol Ther
, vol.13
, pp. 1121-1132
-
-
Nightingale, S.J.1
Hollis, R.P.2
Pepper, K.A.3
Petersen, D.4
Yu, X.J.5
Yang, C.6
Bahner, I.7
Kohn, D.B.8
-
67
-
-
0034856864
-
Capture of DNA sequences at double-strand breaks in mammalian chromosomes
-
Y. Lin, and A.S. Waldman Capture of DNA sequences at double-strand breaks in mammalian chromosomes Genetics 158 2001 1665 1674
-
(2001)
Genetics
, vol.158
, pp. 1665-1674
-
-
Lin, Y.1
Waldman, A.S.2
-
68
-
-
84858074311
-
Integrase-independent HIV-1 infection is augmented under conditions of DNA damage and produces a viral reservoir
-
H. Ebina, Y. Kanemura, Y. Suzuki, K. Urata, N. Misawa, and Y. Koyanagi Integrase-independent HIV-1 infection is augmented under conditions of DNA damage and produces a viral reservoir Virology 427 2012 44 50
-
(2012)
Virology
, vol.427
, pp. 44-50
-
-
Ebina, H.1
Kanemura, Y.2
Suzuki, Y.3
Urata, K.4
Misawa, N.5
Koyanagi, Y.6
-
69
-
-
79952192386
-
Notable reduction in illegitimate integration mediated by a PPT-deleted, nonintegrating lentiviral vector
-
B. Kantor, M. Bayer, H. Ma, J. Samulski, C. Li, T. McCown, and T. Kafri Notable reduction in illegitimate integration mediated by a PPT-deleted, nonintegrating lentiviral vector Mol Ther 19 2010 547 556
-
(2010)
Mol Ther
, vol.19
, pp. 547-556
-
-
Kantor, B.1
Bayer, M.2
Ma, H.3
Samulski, J.4
Li, C.5
McCown, T.6
Kafri, T.7
-
70
-
-
84895464998
-
Design of a novel integration-deficient lentivector technology that incorporates genetic and posttranslational elements to target human dendritic cells
-
S.U. Tareen, B. Kelley-Clarke, C.J. Nicolai, L.A. Cassiano, L.T. Nelson, M.M. Slough, C.D. Vin, J.M. Odegard, D.D. Sloan, N. Van Hoeven, and et al. Design of a novel integration-deficient lentivector technology that incorporates genetic and posttranslational elements to target human dendritic cells Mol Ther 22 2014 575 587
-
(2014)
Mol Ther
, vol.22
, pp. 575-587
-
-
Tareen, S.U.1
Kelley-Clarke, B.2
Nicolai, C.J.3
Cassiano, L.A.4
Nelson, L.T.5
Slough, M.M.6
Vin, C.D.7
Odegard, J.M.8
Sloan, D.D.9
Van Hoeven, N.10
-
71
-
-
84927025052
-
One-year follow-up of transgene expression by integrase-defective lentiviral vectors and their therapeutic potential in spinocerebellar ataxia model mice
-
H. Saida, Y. Matsuzaki, K. Takayama, A. Iizuka, A. Konno, S. Yanagi, and H. Hirai One-year follow-up of transgene expression by integrase-defective lentiviral vectors and their therapeutic potential in spinocerebellar ataxia model mice Gene Ther 21 2014 820 827
-
(2014)
Gene Ther
, vol.21
, pp. 820-827
-
-
Saida, H.1
Matsuzaki, Y.2
Takayama, K.3
Iizuka, A.4
Konno, A.5
Yanagi, S.6
Hirai, H.7
-
72
-
-
79959629606
-
Avoiding cytotoxicity of transposases by dose-controlled mRNA delivery
-
M. Galla, A. Schambach, C.S. Falk, T. Maetzig, J. Kuehle, K. Lange, D. Zychlinski, N. Heinz, M.H. Brugman, G. Göhring, and et al. Avoiding cytotoxicity of transposases by dose-controlled mRNA delivery Nucleic Acids Res 39 2011 7147 7160
-
(2011)
Nucleic Acids Res
, vol.39
, pp. 7147-7160
-
-
Galla, M.1
Schambach, A.2
Falk, C.S.3
Maetzig, T.4
Kuehle, J.5
Lange, K.6
Zychlinski, D.7
Heinz, N.8
Brugman, M.H.9
Göhring, G.10
-
73
-
-
0036207464
-
Improving the post-transcriptional aspects of lentiviral vectors
-
T. Hope Improving the post-transcriptional aspects of lentiviral vectors Curr Top Microbiol Immunol 261 2002 179 189
-
(2002)
Curr Top Microbiol Immunol
, vol.261
, pp. 179-189
-
-
Hope, T.1
-
74
-
-
84905448172
-
Efficient transient genetic manipulation in vitro and in vivo by prototype foamy virus-mediated nonviral RNA transfer
-
M.V. Hamann, N. Stanke, E. Müllers, K. Stirnnagel, S. Hütter, B. Artegiani, S. Bragado Alonso, F. Calegari, and D. Lindemann Efficient transient genetic manipulation in vitro and in vivo by prototype foamy virus-mediated nonviral RNA transfer Mol Ther 22 2014 1460 1471
-
(2014)
Mol Ther
, vol.22
, pp. 1460-1471
-
-
Hamann, M.V.1
Stanke, N.2
Müllers, E.3
Stirnnagel, K.4
Hütter, S.5
Artegiani, B.6
Bragado Alonso, S.7
Calegari, F.8
Lindemann, D.9
-
75
-
-
77952368672
-
Protein transduction from retroviral Gag precursors
-
C. Voelkel, M. Galla, T. Maetzig, E. Warlich, J. Kuehle, D. Zychlinski, J. Bode, T. Cantz, A. Schambach, and C. Baum Protein transduction from retroviral Gag precursors Proc Natl Acad Sci U S A 107 2010 7805 7810
-
(2010)
Proc Natl Acad Sci U S A
, vol.107
, pp. 7805-7810
-
-
Voelkel, C.1
Galla, M.2
Maetzig, T.3
Warlich, E.4
Kuehle, J.5
Zychlinski, D.6
Bode, J.7
Cantz, T.8
Schambach, A.9
Baum, C.10
-
76
-
-
77951971713
-
Production of HIV-1 integrase fusion protein-carrying lentiviral vectors for gene therapy and protein transduction
-
D. Schenkwein, V. Turkki, H.R. Kärkkäinen, K. Airenne, and S. Ylä-Herttuala Production of HIV-1 integrase fusion protein-carrying lentiviral vectors for gene therapy and protein transduction Hum Gene Ther 21 2010 589 602
-
(2010)
Hum Gene Ther
, vol.21
, pp. 589-602
-
-
Schenkwein, D.1
Turkki, V.2
Kärkkäinen, H.R.3
Airenne, K.4
Ylä-Herttuala, S.5
-
77
-
-
80052564938
-
Protein transduction by pseudotyped lentivirus-like nanoparticles
-
T. Aoki, K. Miyauchi, E. Urano, R. Ichikawa, and J. Komano Protein transduction by pseudotyped lentivirus-like nanoparticles Gene Ther 18 2011 936 941
-
(2011)
Gene Ther
, vol.18
, pp. 936-941
-
-
Aoki, T.1
Miyauchi, K.2
Urano, E.3
Ichikawa, R.4
Komano, J.5
-
78
-
-
0029039296
-
Targeting foreign proteins to human immunodeficiency virus particles via fusion with Vpr and Vpx
-
X. Wu, H. Liu, H. Xiao, J. Kim, P. Seshaiah, G. Natsoulis, J.D. Boeke, B.H. Hahn, and J.C. Kappes Targeting foreign proteins to human immunodeficiency virus particles via fusion with Vpr and Vpx J Virol 69 1995 3389 3398
-
(1995)
J Virol
, vol.69
, pp. 3389-3398
-
-
Wu, X.1
Liu, H.2
Xiao, H.3
Kim, J.4
Seshaiah, P.5
Natsoulis, G.6
Boeke, J.D.7
Hahn, B.H.8
Kappes, J.C.9
-
79
-
-
28444447368
-
Cell death induced by the herpes simplex virus-1 thymidine kinase delivered by human immunodeficiency virus-1-based virus-like particles
-
S. Peretti, I. Schiavoni, K. Pugliese, and M. Federico Cell death induced by the herpes simplex virus-1 thymidine kinase delivered by human immunodeficiency virus-1-based virus-like particles Mol Ther 12 2005 1185 1196
-
(2005)
Mol Ther
, vol.12
, pp. 1185-1196
-
-
Peretti, S.1
Schiavoni, I.2
Pugliese, K.3
Federico, M.4
-
80
-
-
32644447640
-
Therapeutic protein transduction of mammalian cells and mice by nucleic acid-free lentiviral nanoparticles
-
N. Link, C. Aubel, J.M. Kelm, R.R. Marty, D. Greber, V. Djonov, J. Bourhis, W. Weber, and M. Fussenegger Therapeutic protein transduction of mammalian cells and mice by nucleic acid-free lentiviral nanoparticles Nucleic Acids Res 34 2006 e16
-
(2006)
Nucleic Acids Res
, vol.34
, pp. e16
-
-
Link, N.1
Aubel, C.2
Kelm, J.M.3
Marty, R.R.4
Greber, D.5
Djonov, V.6
Bourhis, J.7
Weber, W.8
Fussenegger, M.9
-
81
-
-
3042642144
-
The stoichiometry of Gag protein in HIV-1
-
J.A. Briggs, M.N. Simon, I. Gross, H.G. Krausslich, S.D. Fuller, V.M. Vogt, and M.C. Johnson The stoichiometry of Gag protein in HIV-1 Nat Struct Mol Biol 11 2004 672 675
-
(2004)
Nat Struct Mol Biol
, vol.11
, pp. 672-675
-
-
Briggs, J.A.1
Simon, M.N.2
Gross, I.3
Krausslich, H.G.4
Fuller, S.D.5
Vogt, V.M.6
Johnson, M.C.7
-
82
-
-
77956613752
-
Improvement of lentiviral vector-mediated gene transduction by genetic engineering of the structural protein Pr55 Gag
-
T. Aoki, S. Shimizu, E. Urano, Y. Futahashi, M. Hamatake, H. Tamamura, K. Terashima, T. Murakami, N. Yamamoto, and J. Komano Improvement of lentiviral vector-mediated gene transduction by genetic engineering of the structural protein Pr55 Gag Gene Ther 17 2010 1124 1133
-
(2010)
Gene Ther
, vol.17
, pp. 1124-1133
-
-
Aoki, T.1
Shimizu, S.2
Urano, E.3
Futahashi, Y.4
Hamatake, M.5
Tamamura, H.6
Terashima, K.7
Murakami, T.8
Yamamoto, N.9
Komano, J.10
-
83
-
-
84904088882
-
MLV based viral-like-particles for delivery of toxic proteins and nuclear transcription factors
-
D.T. Wu, and M.J. Roth MLV based viral-like-particles for delivery of toxic proteins and nuclear transcription factors Biomaterials 35 2014 8416 8426
-
(2014)
Biomaterials
, vol.35
, pp. 8416-8426
-
-
Wu, D.T.1
Roth, M.J.2
-
84
-
-
80054762005
-
Protein delivery using engineered virus-like particles
-
S.J. Kaczmarczyk, K. Sitaraman, H.A. Young, S.H. Hughes, and D.K. Chatterjee Protein delivery using engineered virus-like particles Proc Natl Acad Sci U S A 108 2011 16998 17003
-
(2011)
Proc Natl Acad Sci U S A
, vol.108
, pp. 16998-17003
-
-
Kaczmarczyk, S.J.1
Sitaraman, K.2
Young, H.A.3
Hughes, S.H.4
Chatterjee, D.K.5
-
85
-
-
77956650867
-
Viral vector-mediated RNA interference
-
L.B. Couto, and K.A. High Viral vector-mediated RNA interference Curr Opin Pharmacol 10 2010 534 542
-
(2010)
Curr Opin Pharmacol
, vol.10
, pp. 534-542
-
-
Couto, L.B.1
High, K.A.2
-
86
-
-
84862114271
-
Lentiviral vectors encoding short hairpin RNAs efficiently transduce and knockdown LINGO-1 but induce an interferon response and cytotoxicity in central nervous system neurones
-
T.H. Hutson, E. Foster, J.M. Dawes, R. Hindges, R.J. Yanez-Munoz, and L.D. Moon Lentiviral vectors encoding short hairpin RNAs efficiently transduce and knockdown LINGO-1 but induce an interferon response and cytotoxicity in central nervous system neurones J Gene Med 14 2012 299 315
-
(2012)
J Gene Med
, vol.14
, pp. 299-315
-
-
Hutson, T.H.1
Foster, E.2
Dawes, J.M.3
Hindges, R.4
Yanez-Munoz, R.J.5
Moon, L.D.6
-
87
-
-
40149090498
-
Cellular restriction of retrovirus particle-mediated mRNA transfer
-
M. Galla, A. Schambach, G.J. Towers, and C. Baum Cellular restriction of retrovirus particle-mediated mRNA transfer J Virol 82 2008 3069 3077
-
(2008)
J Virol
, vol.82
, pp. 3069-3077
-
-
Galla, M.1
Schambach, A.2
Towers, G.J.3
Baum, C.4
-
88
-
-
85044694762
-
Targeted genome editing by lentiviral protein transduction of zinc-finger and TAL-effector nucleases
-
Y. Cai, R.O. Bak, and J.G. Mikkelsen Targeted genome editing by lentiviral protein transduction of zinc-finger and TAL-effector nucleases Elife 3 2014 e01911
-
(2014)
Elife
, vol.3
, pp. e01911
-
-
Cai, Y.1
Bak, R.O.2
Mikkelsen, J.G.3
-
89
-
-
84899925923
-
Modified lentiviral LTRs allow Flp recombinase-mediated cassette exchange and in vivo tracing of "factor-free induced pluripotent stem cells
-
J. Kuehle, S. Turan, T. Cantz, D. Hoffmann, J.D. Suerth, T. Maetzig, D. Zychlinski, C. Klein, D. Steinemann, C. Baum, and et al. Modified lentiviral LTRs allow Flp recombinase-mediated cassette exchange and in vivo tracing of "factor-free induced pluripotent stem cells Mol Ther 22 2014 919 928
-
(2014)
Mol Ther
, vol.22
, pp. 919-928
-
-
Kuehle, J.1
Turan, S.2
Cantz, T.3
Hoffmann, D.4
Suerth, J.D.5
Maetzig, T.6
Zychlinski, D.7
Klein, C.8
Steinemann, D.9
Baum, C.10
-
90
-
-
84874444963
-
Recombinant retrovirus-derived virus-like particle-based vaccines induce hepatitis C virus-specific cellular and neutralizing immune responses in mice
-
C. Huret, D. Desjardins, M. Miyalou, B. Levacher, M. Amadoudji Zin, O. Bonduelle, B. Combadiere, C. Dalba, D. Klatzmann, and B. Bellier Recombinant retrovirus-derived virus-like particle-based vaccines induce hepatitis C virus-specific cellular and neutralizing immune responses in mice Vaccine 31 2013 1540 1547
-
(2013)
Vaccine
, vol.31
, pp. 1540-1547
-
-
Huret, C.1
Desjardins, D.2
Miyalou, M.3
Levacher, B.4
Amadoudji Zin, M.5
Bonduelle, O.6
Combadiere, B.7
Dalba, C.8
Klatzmann, D.9
Bellier, B.10
|