Adeno-associated virus (AAV) gene therapy for neurological disease

Neuropharmacology

Volumn 69, Issue , 2013, Pages 82-88

  Weinberg, Marc S ^a   Samulski, R Jude ^a   McCown, Thomas J ^a  

^a UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

Author keywords

Adeno associated virus; Gene therapy

Indexed keywords

GLIAL FIBRILLARY ACIDIC PROTEIN; MYELIN BASIC PROTEIN; NEUTRALIZING ANTIBODY; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ALZHEIMER DISEASE; AMYOTROPHIC LATERAL SCLEROSIS; ANIMAL EXPERIMENT; ANIMAL MODEL; CENTRAL NERVOUS SYSTEM DISEASE; DRUG EFFICACY; DRUG SAFETY; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; HUNTINGTON CHOREA; LEUKODYSTROPHY; MOUSE; NEUROLOGIC DISEASE; NONHUMAN; PARKINSON DISEASE; PRIORITY JOURNAL; REVIEW; VIRUS GENOME;

ANIMALS; DEPENDOVIRUS; GENE EXPRESSION; GENETIC THERAPY; GENETIC VECTORS; HUMANS; INJECTIONS, INTRAVENTRICULAR; NERVOUS SYSTEM DISEASES; TRANSGENES;

EID: 84875240244     PISSN: 00283908     EISSN: 18737064     Source Type: Journal    
DOI: 10.1016/j.neuropharm.2012.03.004     Document Type: Review

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