Mitochondrial gene therapy: The tortuous path from bench to bedside

Mitochondrion

Volumn 11, Issue 6, 2011, Pages 839-844

  Adhya, Samit ^a   Mahato, Biraj ^a   Jash, Sukanta ^a   Koley, Sandip ^a   Dhar, Gunjan ^a   Chowdhury, Tapas ^a  

^a INDIAN INSTITUTE OF CHEMICAL BIOLOGY   (India)

Author keywords

Dysfunction; Gene therapy; Mitochondria

Indexed keywords

ADENOSINE TRIPHOSPHATE; LIPOSOME; MITOCHONDRIAL DNA; ND1 PROTEIN; ND4 PROTEIN; OLIGORIBONUCLEOTIDE; PEPTIDE NUCLEIC ACID; RESTRICTION ENDONUCLEASE; TRANSFER RNA; TRANSFER RNA IMPORT COMPLEX; UNCLASSIFIED DRUG;

ALLOTOPIC EXPRESSION; CELL RESPIRATION; CLONAL VARIATION; ELECTROPORATION; GENE; GENE DELIVERY SYSTEM; GENE EXPRESSION; GENE MUTATION; GENE PRODUCT; GENE THERAPY; HETEROPLASMY; HUMAN; INTERNALIZATION; INTRACELLULAR TRANSPORT; LEBER HEREDITARY OPTIC NEUROPATHY; LIPOSOMAL GENE DELIVERY SYSTEM; MERRF SYNDROME; MITOCHONDRIAL DYSFUNCTION; MITOCHONDRIAL GENE; MITOCHONDRIAL GENE THERAPY; MITOCHONDRIAL GENOME; MITOCHONDRIAL TARGETING SIGNAL; MITOCHONDRIAL TRANSFER RNA GENE; MITOCHONDRION; MITOCHONDRIOTROPISM; ND1 GENE; ND4 GENE; NONHUMAN; PRIORITY JOURNAL; PROTEIN TARGETING; REVIEW; RNA GENE;

GENE THERAPY; GENES, MITOCHONDRIAL; HUMANS; MITOCHONDRIA; MITOCHONDRIAL DISEASES;

EID: 82755182930     PISSN: 15677249     EISSN: 18728278     Source Type: Journal    
DOI: 10.1016/j.mito.2011.06.003     Document Type: Review

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