On the genetics of retinitis pigmentosa and on mutation-independent approaches to therapeutic intervention

EMBO Journal

Volumn 21, Issue 5, 2002, Pages 857-864

  Farrar, G Jane ^a   Kenna, Paul F ^a   Humphries, Peter ^a  

^a TRINITY COLLEGE DUBLIN   (Ireland)

Author keywords

Gene therapy; Inherited eye disease; Photoreceptors; Retinitis pigmentosa; Ribozymes

Indexed keywords

GENE MUTATION; GENE THERAPY; HEREDITY; HUMAN; LIGHT ADAPTATION; PHOTORECEPTOR; PRIORITY JOURNAL; RETINITIS PIGMENTOSA; REVIEW;

3' UNTRANSLATED REGIONS; 5' UNTRANSLATED REGIONS; ANIMALS; APOPTOSIS; DISEASE PROGRESSION; EYE PROTEINS; GENE THERAPY; GENES, DOMINANT; GENES, RECESSIVE; GENETIC HETEROGENEITY; HUMANS; LINKAGE (GENETICS); MAMMALS; MICE; MICE, KNOCKOUT; MODELS, ANIMAL; NERVE GROWTH FACTORS; OPTIC ATROPHY, HEREDITARY, LEBER; RETINA; RETINITIS PIGMENTOSA; RHODOPSIN; RNA, CATALYTIC; RNA, MESSENGER; RODS (RETINA); SYNDROME; TRANSCRIPTION FACTORS; X CHROMOSOME;

EID: 0036500230     PISSN: 02614189     EISSN: None     Source Type: Journal    
DOI: 10.1093/emboj/21.5.857     Document Type: Review

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