MECP2 isoform-specific vectors with regulated expression for Rett Syndrome gene therapy

PLoS ONE

Volumn 4, Issue 8, 2009, Pages

  Rastegar, Mojgan ^a,d   Hotta, Akitsu ^a   Pasceri, Peter ^a   Makarem, Maisam ^a   Cheung, Aaron Y L ^a,b   Elliott, Shauna ^a   Park, Katya J ^a,b   Adachi, Megumi ^c   Jones, Frederick S ^c   Clarke, Ian D ^a   Dirks, Peter ^a   Ellis, James ^a,b  

^a HOSPITAL FOR SICK CHILDREN   (Canada)

^b UNIVERSITY OF TORONTO   (Canada)

^c NEUROSCIENCES INSTITUTE   (United States)

^d UNIVERSITY OF MANITOBA   (Canada)

Author keywords

[No Author keywords available]

Indexed keywords

EPIDERMAL GROWTH FACTOR; LENTIVIRUS VECTOR; METHYL CPG BINDING PROTEIN 2; MECP2 PROTEIN, HUMAN;

ANIMAL CELL; ANIMAL TISSUE; ARTICLE; CELL DIFFERENTIATION; CONTROLLED STUDY; DENDRITE; DNA METHYLATION; FEMALE; GENE EXPRESSION REGULATION; GENE INACTIVATION; GENE SILENCING; GENETIC TRANSDUCTION; GLIA CELL; HETEROCHROMATIN; MOUSE; NERVE CELL; NEURAL STEM CELL; NONHUMAN; PROGENY; PROMOTER REGION; RETT SYNDROME; VIRAL GENE THERAPY; ANIMAL; GENE THERAPY; GENE VECTOR; GENETICS; HUMAN; LENTIVIRINAE;

AVES; MURINAE; MUS;

ANIMALS; FEMALE; GENE EXPRESSION REGULATION; GENE THERAPY; GENETIC VECTORS; HUMANS; LENTIVIRUS; METHYL-CPG-BINDING PROTEIN 2; MICE; PROMOTER REGIONS, GENETIC; RETT SYNDROME; TRANSDUCTION, GENETIC;

EID: 69449090636     PISSN: None     EISSN: 19326203     Source Type: Journal    
DOI: 10.1371/journal.pone.0006810     Document Type: Article

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