Adenovirus expressing an NPC1-GFP fusion gene corrects neuronal and nonneuronal defects associated with Niemann Pick type C disease

Journal of Neuroscience Research

Volumn 81, Issue 5, 2005, Pages 706-719

  Paul, C A ^a,e   Reid, P C ^a,f   Boegle, A K ^a   Karten, B ^b   Zhang, M ^c,g   Jiang, Z G ^d,h   Franz, D ^a,i   Lin, L ^a,j   Chang, T Y ^a   Vance, J E ^b   Blanchette Mackie, J ^c   Maue, Robert A ^a  

^a DARTMOUTH MEDICAL SCHOOL   (United States)

^b UNIVERSITY OF ALBERTA   (Canada)

^c NATIONAL INSTITUTE OF DIABETES AND DIGESTIVE AND KIDNEY DISEASES   (United States)

^d NATIONAL INSTITUTE OF MENTAL HEALTH   (United States)

^e St Thomas Aquinas College   (United States)

^f UNIVERSITY OF TOKYO   (Japan)

^g Synta Pharmaceuticals Corp   (United States)

^h Panacea Pharmaceuticals Inc   (United States)

ⁱ UNIVERSITY OF ARIZONA   (United States)

^j UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

more..

Author keywords

Adenovirus; Astrocytes; Cholesterol; Neurons; Niemann Pick disease

Indexed keywords

COMPLEMENTARY DNA; GREEN FLUORESCENT PROTEIN; HYBRID PROTEIN; PROTEIN NPC1; UNCLASSIFIED DRUG; CARRIER PROTEIN; CHOLESTEROL; MEMBRANE PROTEIN; NPC1 PROTEIN, HUMAN;

ADENOVIRUS; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; ASTROCYTE; CARBOXY TERMINAL SEQUENCE; CELLULAR DISTRIBUTION; CENTRAL NERVOUS SYSTEM; CONTROLLED STUDY; CYTOMEGALOVIRUS; FLUORESCENCE MICROSCOPY; FUSION GENE; HUMAN; HUMAN CELL; MOUSE; NERVE CELL; NIEMANN PICK DISEASE; NONHUMAN; OVARY CELL; PRIORITY JOURNAL; VIRUS RECOMBINANT; ANIMAL; BRAIN; CHO CELL; COMPARATIVE STUDY; CYTOLOGY; FEMALE; FIBROBLAST; GENETIC PROCEDURES; GENETIC TRANSDUCTION; GENETIC TRANSFECTION; GENETICS; HAMSTER; METABOLISM; OVARY; PHYSIOLOGY; RAT; TRANSPORT AT THE CELLULAR LEVEL;

ADENOVIRIDAE; ANIMALS; ASTROCYTES; BIOLOGICAL TRANSPORT; BRAIN; CARRIER PROTEINS; CHO CELLS; CHOLESTEROL; CRICETINAE; FEMALE; FIBROBLASTS; GENETIC TECHNIQUES; GREEN FLUORESCENT PROTEINS; HUMANS; MEMBRANE GLYCOPROTEINS; MICE; MICROSCOPY, FLUORESCENCE; NEURONS; NIEMANN-PICK DISEASES; OVARY; RATS; RECOMBINANT FUSION PROTEINS; TRANSDUCTION, GENETIC; TRANSFECTION;

EID: 27244456227     PISSN: 03604012     EISSN: None     Source Type: Journal    
DOI: 10.1002/jnr.20592     Document Type: Article

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