A demonstration using mouse models that successful gene therapy for cystic fibrosis requires only partial gene correction

Gene Therapy

Volumn 3, Issue 9, 1996, Pages 797-801

  Dorin, J R ^a   Farley, R ^b   Webb, S ^a   Smith, S N ^b   Farini, E ^a   Delaney, S J ^c   Wainwright, B J ^c   Alton, E W F W ^b   Porteous, D J ^a  

^a WESTERN GENERAL HOSPITAL   (United Kingdom)

^b NATIONAL HEART AND LUNG INSTITUTE   (United Kingdom)

^c UNIVERSITY OF QUEENSLAND   (Australia)

Author keywords

Cystic fibrosis; Gene therapy; Mouse models

Indexed keywords

CHLORIDE ION; TRANSMEMBRANE CONDUCTANCE REGULATOR;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CHLORIDE TRANSPORT; CONTROLLED STUDY; CYSTIC FIBROSIS; ENTEROPATHY; GENE EXPRESSION; GENE THERAPY; MOUSE; NONHUMAN; PRIORITY JOURNAL; TRANSGENE;

ANIMALS; CHLORIDES; CROSSES, GENETIC; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; ELECTRIC CONDUCTIVITY; FORSKOLIN; GENE EXPRESSION; GENE THERAPY; GENES, RECESSIVE; GENOTYPE; INTESTINES; MICE; MICE, MUTANT STRAINS; PHENOTYPE; RNA, MESSENGER;

ANIMALIA;

EID: 0029813969     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

References (16)

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