The emerging role of viral vectors as vehicles for DMD gene editing

Genome Medicine

Volumn 8, Issue 1, 2016, Pages

  Maggio, Ignazio ^a   Chen, Xiaoyu ^a   Gonçalves, Manuel A F V ^a  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; DYSTROPHIN; VIRUS VECTOR; ZINC FINGER NUCLEASE; DMD PROTEIN, HUMAN;

ARTICLE; BIOMIMETICS; CELL DIFFERENTIATION; CYTOSKELETON; DMD GENE; DNA HYBRIDIZATION; DUCHENNE MUSCULAR DYSTROPHY; EX VIVO STUDY; EXON SKIPPING; GENE; GENE LOCUS; HUMAN; LIFE EXPECTANCY; MITOSIS; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; PROGENY; PROTEIN DNA BINDING; PROTEIN SYNTHESIS; RNA EDITING; RNA HYBRIDIZATION; SIGNAL TRANSDUCTION; STOP CODON; TISSUE ENGINEERING; VIRAL GENE DELIVERY SYSTEM; ANIMAL; CRISPR CAS SYSTEM; DISEASE MODEL; ENZYMOLOGY; GENE EDITING; GENE VECTOR; GENETICS; METABOLISM; MUSCULAR DYSTROPHY, DUCHENNE; PROCEDURES; VIRUS;

ANIMALS; CRISPR-CAS SYSTEMS; DISEASE MODELS, ANIMAL; DYSTROPHIN; GENE EDITING; GENETIC VECTORS; HUMANS; MUSCULAR DYSTROPHY, DUCHENNE; VIRUSES;

EID: 84969504485     PISSN: None     EISSN: 1756994X     Source Type: Journal    
DOI: 10.1186/s13073-016-0316-x     Document Type: Article

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