Confirmation of donor-derived dystrophin in a duchenne muscular dystrophy patient allotransplanted with normal myoblasts

Muscle and Nerve

Volumn 54, Issue 5, 2016, Pages 979-981

[No Author Info available]

Author keywords

[No Author keywords available]

Indexed keywords

DEFLAZACORT; DYSTROPHIN; EPITOPE; MONOCLONAL ANTIBODY; TACROLIMUS; LEUKOCYTE ANTIGEN;

ACUTE GRAFT REJECTION; ALLOTRANSPLANTATION; CELL TRANSPLANTATION; DUCHENNE MUSCULAR DYSTROPHY; EXON; GENE DELETION; HUMAN; IMMUNODETECTION; IMMUNOSUPPRESSIVE TREATMENT; MUSCLE BIOPSY; MYOBLAST; NONHUMAN; NOTE; PHASE 1 CLINICAL TRIAL (TOPIC); PRIORITY JOURNAL; TIBIALIS ANTERIOR MUSCLE; ADOLESCENT; DONOR; FEMALE; GENETICS; MALE; METABOLISM; PATHOLOGY; SKELETAL MUSCLE; TRANSPLANTATION;

ADOLESCENT; ANTIGENS, CD; DYSTROPHIN; EXONS; FEMALE; HUMANS; MALE; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE; MYOBLASTS; TISSUE DONORS;

EID: 84991821774     PISSN: 0148639X     EISSN: 10974598     Source Type: Journal    
DOI: 10.1002/mus.25129     Document Type: Note

References (7)

1. Skuk D, Goulet M, Roy B, Chapdelaine P, Bouchard JP, Roy R, et al. Dystrophin expression in muscles of Duchenne muscular dystrophy patients after high-density injections of normal myogenic cells. J Neuropathol Exp Neurol 2006;65:371–386.
2. Skuk D, Roy B, Goulet M, Chapdelaine P, Bouchard JP, Roy R, et al. Dystrophin expression in myofibers of Duchenne muscular dystrophy patients following intramuscular injections of normal myogenic cells. Mol Ther 2004;9:475–482.
3. Kinoshita I, Roy R, Dugre FJ, Gravel C, Roy B, Goulet M, et al. Myoblast transplantation in monkeys: control of immune response by FK506. J Neuropathol Exp Neurol 1996;55:687–697.
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7. Skuk D. Myoblast transplantation for inherited myopathies: a clinical approach. Exp Opin Biol Ther 2004;4:1871–1885.