Endonucleases: Tools to correct the dystrophin gene

Journal of Gene Medicine

Volumn 13, Issue 10, 2011, Pages 522-537

  Rousseau, Joel ^a   Chapdelaine, Pierre ^a   Boisvert, Sébastien ^a,b   Almeida, Luciana P ^c   Corbeil, Jacques ^b   Montpetit, Alexandre ^d   Tremblay, Jacques P ^a,b  

^a LAVAL UNIVERSITY   (Canada)

^b UNIVERSITÉ LAVAL   (Canada)

^c UNIVERSITY OF SÃO PAULO   (Brazil)

^d MCGILL UNIVERSITY   (Canada)

Author keywords

Duchenne muscular dystrophy; Dystrophin; Endonuclease; Meganuclease; Micro deletion; Micro insertion; Reading frame correction; Zinc finger nuclease

Indexed keywords

DYSTROPHIN; ENDONUCLEASE; LENTIVIRUS VECTOR; RAG1 PROTEIN; ZINC FINGER PROTEIN;

AMPLICON; ARTICLE; DUCHENNE MUSCULAR DYSTROPHY; FAR WESTERN BLOTTING; FRAMESHIFT MUTATION; GENE AMPLIFICATION; GENE DELETION; GENETIC TRANSFECTION; HUMAN; HUMAN CELL; INTRON; KNOCKOUT GENE; MYOBLAST; MYOTUBE; NUCLEOTIDE SEQUENCE; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; STOP CODON;

CELL LINE; CODON, NONSENSE; DYSTROPHIN; ENDONUCLEASES; EXONS; FRAMESHIFT MUTATION; GENES, RAG-1; HUMANS; INDEL MUTATION; LENTIVIRUS; MUSCULAR DYSTROPHY, DUCHENNE; MYOBLASTS; READING FRAMES; ZINC FINGERS;

EID: 80054910436     PISSN: 1099498X     EISSN: 15212254     Source Type: Journal    
DOI: 10.1002/jgm.1611     Document Type: Article

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