A PiggyBac-mediated approach for muscle gene transfer or cell therapy

Stem Cell Research

Volumn , Issue Part A, 2014, Pages 390-403

  Ley, Déborah ^a   Van Zwieten, Ruthger ^a   Puttini, Stefania ^a   Iyer, Pavithra ^a   Cochard, Alessia ^a   Mermod, Nicolas ^a  

^a UNIVERSITY OF LAUSANNE   (Switzerland)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA ACTININ; DYSTROPHIN; GENOMIC DNA; GREEN FLUORESCENT PROTEIN; PIGGYBAC TRANSPOSASE; PLASMID VECTOR; PUROMYCIN; TRANSPOSASE; UNCLASSIFIED DRUG; GREEN FLUORESCENT PROTEINS;

3' UNTRANSLATED REGION; 5' UNTRANSLATED REGION; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL DIFFERENTIATION; CELL THERAPY; CONTROLLED STUDY; DNA SEQUENCE; DNA TRANSFER; DUCHENNE MUSCULAR DYSTROPHY; ELECTROPORATION; EXPRESSION VECTOR; GENE DELIVERY SYSTEM; GENE DOSAGE; GENE TRANSFER; GENE VECTOR; IN VITRO STUDY; IN VIVO STUDY; INVERTED TERMINAL REPEAT; MOUSE; MUSCLE CELL; MUSCLE DEVELOPMENT; MUSCLE STEM CELL; NONHUMAN; PROTEIN EXPRESSION; STABLE EXPRESSION; TIBIALIS ANTERIOR MUSCLE; TRANSGENE; TRANSPOSON; ANIMALS; CELL- AND TISSUE-BASED THERAPY; CELLS, CULTURED; CHROMOSOMES, ARTIFICIAL, BACTERIAL; CYTOLOGY; FEMALE; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; GENETICS; HUMANS; METABOLISM; METHODS; MICE; MICE, INBRED C57BL; MICE, NUDE; MICROSCOPY, FLUORESCENCE; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE; PATHOLOGY;

ANIMALS; CELL DIFFERENTIATION; CELL- AND TISSUE-BASED THERAPY; CELLS, CULTURED; CHROMOSOMES, ARTIFICIAL, BACTERIAL; FEMALE; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; GREEN FLUORESCENT PROTEINS; HUMANS; MICE; MICE, INBRED C57BL; MICE, NUDE; MICROSCOPY, FLUORESCENCE; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE;

EID: 84908046588     PISSN: 18735061     EISSN: 18767753     Source Type: Journal    
DOI: 10.1016/j.scr.2014.08.007     Document Type: Article

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