Efficient recovery of dysferlin deficiency by dual adeno-associated vector-mediated gene transfer

Human Molecular Genetics

Volumn 19, Issue 10, 2010, Pages 1897-1907

  Lostal, William ^a   Bartoli, Marc ^a   Bourg, Nathalie ^a   Roudaut, Carinne ^a   Bentaïb, Azeddine ^a   Miyake, Katsuya ^b   Guerchet, Nicolas ^a   Fougerousse, Françoise ^a   McNeil, Paul ^b   Richard, Isabelle ^a  

^a GÉNÉTHON   (France)

^b MEDICAL COLLEGE OF GEORGIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; DYSFERLIN; PARVOVIRUS VECTOR;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DRUG EFFICACY; DRUG MECHANISM; EXON; FEMALE; GENE EXPRESSION; HISTOPATHOLOGY; LIMB GIRDLE MUSCULAR DYSTROPHY; LOCOMOTION; MALE; MIYOSHI MYOPATHY; MOLECULAR CLONING; MOUSE; MUSCLE NECROSIS; NONHUMAN; NUCLEOTIDE SEQUENCE; PRIORITY JOURNAL; SYSTEMIC THERAPY; TRANSGENE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY;

ADENO-ASSOCIATED VIRUS;

EID: 77952502008     PISSN: 09646906     EISSN: 14602083     Source Type: Journal    
DOI: 10.1093/hmg/ddq065     Document Type: Article

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