Design of trans-splicing adeno-associated viral vectors for duchenne muscular dystrophy gene therapy

Methods in Molecular Biology

Volumn 433, Issue , 2008, Pages 259-275

  Lai, Yi ^a   Li, Dejia ^a   Yue, Yongping ^a   Duan, Dongsheng ^a  

^a University of Missouri   (United States)

Author keywords

AAV; Adeno associated virus; Duchenne muscular dystrophy; Dystrophin; Gene therapy; Mdx; Mini dystrophin; Muscle; Trans splicing

Indexed keywords

ADENO-ASSOCIATED VIRUS;

EID: 84934439534     PISSN: 10643745     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-59745-237-3_16     Document Type: Article

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