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S.R. Miranda, S. Erlich, V.L. Friedrich Jr., et al. (2000) Hematopoietic Stem Cell Gene Therapy Leads to Marked Visceral Organ Improvements and a Delayed Onset of Neurological Abnormalities in the Acid Sphingomyelinase Deficient Mouse Model of Niemann–Pick Disease. Gen. The. 7 1768.
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(2000)
Gen. The.
, vol.7
, pp. 1768
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Miranda, S.R.1
Erlich, S.2
Friedrich, V.L.3
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