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Volumn 58, Issue 2, 1996, Pages 156-167

Long-term and high-dose trials of enzyme replacement therapy in the canine model of mucopolysaccharidosis I

Author keywords

[No Author keywords available]

Indexed keywords

GLYCOSAMINOGLYCAN; LEVO IDURONIDASE; RECOMBINANT PROTEIN;

EID: 0030221033     PISSN: 10773150     EISSN: None     Source Type: Journal    
DOI: 10.1006/bmme.1996.0044     Document Type: Article
Times cited : (164)

References (32)
  • 1
    • 4244187045 scopus 로고
    • Long-term and high dose enzyme replacement therapy in the canine mucopolysaccharidosis I model
    • Abstract
    • 1. Kakkis ED, Shull RM, McEntee MF, Schmidtchen A, Neufeld EF. Long-term and high dose enzyme replacement therapy in the canine mucopolysaccharidosis I model. Am J Hum Genet 57:A39(193), 1995. [Abstract]
    • (1995) Am J Hum Genet , vol.57 A39 , Issue.193
    • Kakkis, E.D.1    Shull, R.M.2    McEntee, M.F.3    Schmidtchen, A.4    Neufeld, E.F.5
  • 2
    • 0000436145 scopus 로고
    • From cytases to lysosomes
    • 2. De Duve C. From cytases to lysosomes. Fed Proc 23:1045-1049, 1964.
    • (1964) Fed Proc , vol.23 , pp. 1045-1049
    • De Duve, C.1
  • 3
    • 0001767013 scopus 로고
    • Inborn lysosomal diseases
    • 3. Hers HG. Inborn lysosomal diseases. Prog Gastroent 48:625-633, 1965.
    • (1965) Prog Gastroent , vol.48 , pp. 625-633
    • Hers, H.G.1
  • 4
    • 0000820862 scopus 로고
    • The mucopolysaccharidoses
    • (Scriver CR, Beaudet AL, Sly WS, Valle D, Eds.) editors. New York: McGraw-Hill
    • 4. Neufeld EF, Muenzer J. The mucopolysaccharidoses. In The Metabolic and Molecular Bases of Inherited Disease (Scriver CR, Beaudet AL, Sly WS, Valle D, Eds.) editors). New York: McGraw-Hill, 1995, pp 2465-2494.
    • (1995) The Metabolic and Molecular Bases of Inherited Disease , pp. 2465-2494
    • Neufeld, E.F.1    Muenzer, J.2
  • 6
    • 0027318762 scopus 로고
    • Binding, internalization and degradation of mannose-terminated glucocerebrosidase by macrophages
    • 6. Sato Y, Beutler E. Binding, internalization and degradation of mannose-terminated glucocerebrosidase by macrophages. J Clin Invest 91:1909-1917, 1993.
    • (1993) J Clin Invest , vol.91 , pp. 1909-1917
    • Sato, Y.1    Beutler, E.2
  • 7
    • 0014567351 scopus 로고
    • The defect in Hurler and Hunter syndromes, II. Deficiency of specific factors involved in mucopolysaccharide degradation
    • 7. Frantantoni JC, Hall CW, Neufeld EF. The defect in Hurler and Hunter syndromes, II. Deficiency of specific factors involved in mucopolysaccharide degradation. Proc Natl Acad Sci USA 64:360-366, 1969.
    • (1969) Proc Natl Acad Sci USA , vol.64 , pp. 360-366
    • Frantantoni, J.C.1    Hall, C.W.2    Neufeld, E.F.3
  • 8
    • 0028841213 scopus 로고
    • Molecular genetics of mucopolysaccharidosis type I: Diagnostic, clinical and biological implications
    • 8. Scott HS, Bunge S, Gal A, Clarke LA, Morris CP, Hopwood JJ. Molecular genetics of mucopolysaccharidosis type I: Diagnostic, clinical and biological implications. Hum Mutat 6:288-302, 1995.
    • (1995) Hum Mutat , vol.6 , pp. 288-302
    • Scott, H.S.1    Bunge, S.2    Gal, A.3    Clarke, L.A.4    Morris, C.P.5    Hopwood, J.J.6
  • 11
    • 4244187093 scopus 로고
    • Cloning and expression of cDNA encoding the human lysosomal enzyme, α-L-iduronidase
    • Abstract
    • 11. Moskowitz SM, Dlott B, Chuang PD, Neufeld EF. Cloning and expression of cDNA encoding the human lysosomal enzyme, α-L-iduronidase. FASEB J 6:A77, 1992. [Abstract]
    • (1992) FASEB J , vol.6 A77
    • Moskowitz, S.M.1    Dlott, B.2    Chuang, P.D.3    Neufeld, E.F.4
  • 12
    • 0028449393 scopus 로고
    • Overexpression of the human lysosomal enzyme α-L-iduronidase in Chinese hamster ovary cells
    • 12. Kakkis ED, Matynia A, Jonas AJ, Neufeld EF. Overexpression of the human lysosomal enzyme α-L-iduronidase in Chinese hamster ovary cells. Protein Expression Purif 5:225-232, 1992.
    • (1992) Protein Expression Purif , vol.5 , pp. 225-232
    • Kakkis, E.D.1    Matynia, A.2    Jonas, A.J.3    Neufeld, E.F.4
  • 14
    • 0026595304 scopus 로고
    • Architecture of the canine IDUA gene and mutation underlying canine mucopolysaccharidosis type I
    • 14. Menon KP, Tieu PT, Neufeld EF. Architecture of the canine IDUA gene and mutation underlying canine mucopolysaccharidosis type I. Genomics 14:763-768, 1992.
    • (1992) Genomics , vol.14 , pp. 763-768
    • Menon, K.P.1    Tieu, P.T.2    Neufeld, E.F.3
  • 16
    • 0027300720 scopus 로고
    • Simultaneous preparation and quantification of proteoglycans by precipitation with Alcian blue
    • 16. Bjornsson S. Simultaneous preparation and quantification of proteoglycans by precipitation with Alcian blue. Anal Biochem 210:282-291, 1993.
    • (1993) Anal Biochem , vol.210 , pp. 282-291
    • Bjornsson, S.1
  • 17
    • 0003929159 scopus 로고
    • Washington, DC.: Am. Registry of Pathol.
    • 17. Laboratory Methods in Histotechnology. Washington, DC.: Am. Registry of Pathol. 1992, pp. 162-163.
    • (1992) Laboratory Methods in Histotechnology , pp. 162-163
  • 18
    • 0017843818 scopus 로고
    • Human kidney α-L-iduronidase: Purification and characterization
    • 18. Rome LH, Garvin AJ, Neufeld EF. Human kidney α-L-iduronidase: purification and characterization. Arch Biochem Biophys 189:344-353, 1978.
    • (1978) Arch Biochem Biophys , vol.189 , pp. 344-353
    • Rome, L.H.1    Garvin, A.J.2    Neufeld, E.F.3
  • 21
    • 0027427381 scopus 로고
    • Transport of insulin-related peptides and glucose across the blood-brain barrier
    • 21. Pardridge WM. Transport of insulin-related peptides and glucose across the blood-brain barrier. Ann NY Acad Sci 692:126-137, 1993.
    • (1993) Ann NY Acad Sci , vol.692 , pp. 126-137
    • Pardridge, W.M.1
  • 22
    • 0021673364 scopus 로고
    • Mannose-specific oligosaccharide recognition by mononuclear phagocytes
    • 22. Stahl PD, Wileman TE, Diment S, Shepherd VL. Mannose-specific oligosaccharide recognition by mononuclear phagocytes. Biol Cell 51:215-218, 1984.
    • (1984) Biol Cell , vol.51 , pp. 215-218
    • Stahl, P.D.1    Wileman, T.E.2    Diment, S.3    Shepherd, V.L.4
  • 23
    • 0017861074 scopus 로고
    • Hepatic receptor that specifically binds oligosaccharides containing fucosyl α1-3 N-acetylglucosamine linkages
    • 23. Prieels JP, Pizzo SV, Glasgow LR, Paulson JC, Hill RL. Hepatic receptor that specifically binds oligosaccharides containing fucosyl α1-3 N-acetylglucosamine linkages. Proc Natl Acad Sci USA 75:2215-2219, 1978.
    • (1978) Proc Natl Acad Sci USA , vol.75 , pp. 2215-2219
    • Prieels, J.P.1    Pizzo, S.V.2    Glasgow, L.R.3    Paulson, J.C.4    Hill, R.L.5
  • 24
    • 0028177015 scopus 로고
    • Fucose-mediated binding and degradation of tissue-type plasminogen activator by HepG2 cells
    • 24. Hajjar KA, Reynolds CM. Fucose-mediated binding and degradation of tissue-type plasminogen activator by HepG2 cells. J Clin Invest 93:703-710, 1994.
    • (1994) J Clin Invest , vol.93 , pp. 703-710
    • Hajjar, K.A.1    Reynolds, C.M.2
  • 25
    • 0019150849 scopus 로고
    • Fucose plays a role in the clearance and uptake of glucocerebrosidase by rat liver cells
    • 25. Furbish FS, Krett NL, Barranger JA, Brady RO. Fucose plays a role in the clearance and uptake of glucocerebrosidase by rat liver cells. Biochem Biophys Res Commun 95:1768-1774, 1980.
    • (1980) Biochem Biophys Res Commun , vol.95 , pp. 1768-1774
    • Furbish, F.S.1    Krett, N.L.2    Barranger, J.A.3    Brady, R.O.4
  • 29
    • 0027216474 scopus 로고
    • Antibody response in patients with Gaucher disease after repeated infusion with macrophage-targeted glucocerebrosidase
    • 29. Richards SM, Olson TA, McPherson JM. Antibody response in patients with Gaucher disease after repeated infusion with macrophage-targeted glucocerebrosidase. Blood 82:1402-1409, 1993.
    • (1993) Blood , vol.82 , pp. 1402-1409
    • Richards, S.M.1    Olson, T.A.2    McPherson, J.M.3
  • 30
    • 0026659050 scopus 로고
    • IgG antibody response to polyethylene glycol-modified adenosine deaminase in patients with adenosine deaminase deficiency
    • 30. Chaffee S, Mary A, Stiehm ER, Girault D, Fischer A, Hershfield MS. IgG antibody response to polyethylene glycol-modified adenosine deaminase in patients with adenosine deaminase deficiency. J Clin Invest 89:1643-1651, 1993.
    • (1993) J Clin Invest , vol.89 , pp. 1643-1651
    • Chaffee, S.1    Mary, A.2    Stiehm, E.R.3    Girault, D.4    Fischer, A.5    Hershfield, M.S.6
  • 31
    • 0021298629 scopus 로고
    • Overview of inhibitors to factor VIII and IX
    • 31. Roberts HR, Cromartie R. Overview of inhibitors to factor VIII and IX. Prog Clin Biol Res 150:1-18, 1984.
    • (1984) Prog Clin Biol Res , vol.150 , pp. 1-18
    • Roberts, H.R.1    Cromartie, R.2
  • 32
    • 0021984346 scopus 로고
    • Systemic allergy to human (recombinant DNA) insulin
    • 32. Gossain VV, Rovner RR, Mohan K. Systemic allergy to human (recombinant DNA) insulin. Ann Allergy 55:116-118, 1985.
    • (1985) Ann Allergy , vol.55 , pp. 116-118
    • Gossain, V.V.1    Rovner, R.R.2    Mohan, K.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.