Infusion of α-galactosidase A reduces tissue globotriaosylceramide storage in patients with Fabry disease

Proceedings of the National Academy of Sciences of the United States of America

Volumn 97, Issue 1, 2000, Pages 365-370

  Schiffmann, R ^a,d   Murray, G J ^a   Treco, D ^c   Daniel, P ^c   Sellos Moura, M ^c   Myers, M ^c   Quirk, J M ^a   Zirzow, G C ^a   Borowski, M ^c   Loveday, K ^c   Anderson, T ^c   Gillespie, F ^c   Oliver, K L ^a   Jeffries, N O ^a   Doo, E ^b   Liang, T J ^b   Kreps, C ^a   Gunter, K ^c   Frei, K ^a   Crutchfield, K ^a   Selden, R F ^c   Brady, R O ^a   more..

^a NATIONAL INSTITUTE OF NEUROLOGICAL DISORDERS AND STROKE   (United States)

^b NATIONAL INSTITUTE OF DIABETES AND DIGESTIVE AND KIDNEY DISEASES   (United States)

^c Shire Canada   (Canada)

^d NATIONAL INSTITUTES OF HEALTH   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA GALACTOSIDASE; GLOBOTRIAOSYLCERAMIDE; SOMATOMEDIN B RECEPTOR;

ADULT; ARTICLE; CLINICAL ARTICLE; ENZYME REPLACEMENT; FABRY DISEASE; HALF LIFE TIME; HUMAN; HUMAN TISSUE; IMMUNOHISTOCHEMISTRY; LIVER; MALE; PHARMACODYNAMICS; PHARMACOKINETICS; PLASMA; PRIORITY JOURNAL; SAFETY; URINE SEDIMENT;

ADULT; ALPHA-GALACTOSIDASE; FABRY DISEASE; HUMANS; IMMUNOHISTOCHEMISTRY; LIVER; MALE; MIDDLE AGED; TRIHEXOSYLCERAMIDES; URINALYSIS;

EID: 12944265457     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.97.1.365     Document Type: Article

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