Gene therapy for chronic granulomatous disease

Methods in Enzymology

Volumn 507, Issue , 2012, Pages 125-154

  Kang, Elizabeth M ^a   Malech, Harry L ^a  

^a NATIONAL INSTITUTE OF ALLERGY AND INFECTIOUS DISEASES   (United States)

Author keywords

Busulfan conditioning; Chronic granulomatous disease; Ex vivo transduction; Gene therapy; Hematopoietic stem cells; Induced pluripotent stem cells; Lentivirus vector; Murine retrovirus vector; Neutrophils; Phagocyte NADPH oxidase; Zinc finger nuclease

Indexed keywords

BUSULFAN; NUCLEASE; OXIDOREDUCTASE; REDUCED NICOTINAMIDE ADENINE DINUCLEOTIDE PHOSPHATE OXIDASE; REDUCED NICOTINAMIDE ADENINE DINUCLEOTIDE PHOSPHATE OXIDASE 2; RETROVIRUS VECTOR; VIRUS VECTOR; ZINC FINGER PROTEIN;

ARTICLE; AUTOLOGOUS HEMATOPOIETIC STEM CELL TRANSPLANTATION; BLOOD CELL COUNT; BONE MARROW EXAMINATION; CHRONIC GRANULOMATOUS DISEASE; CLINICAL TRIAL (TOPIC); EX VIVO GENE TRANSFER; GENE FUNCTION; GENE MUTATION; GENE TARGETING; GENE THERAPY; HUMAN; INFLAMMATION; KNOCKOUT MOUSE; NEUTROPHIL; NONHUMAN; NONMYELOABLATIVE CONDITIONING; PATIENT CARE; PATIENT MONITORING; PHAGOCYTE; PLURIPOTENT STEM CELL; PRIORITY JOURNAL; RECURRENT INFECTION; SALVAGE THERAPY; TARGET CELL; TRANSGENE; XENOGRAFT; ZINC FINGER MOTIF;

LENTIVIRUS; MURINAE;

EID: 84857621011     PISSN: 00766879     EISSN: 15577988     Source Type: Book Series    
DOI: 10.1016/B978-0-12-386509-0.00007-7     Document Type: Chapter

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