Failure of SCID-X1 gene therapy in older patients

Blood

Volumn 105, Issue 11, 2005, Pages 4255-4257

  Thrasher, Adrian J ^b   Hacein Bey Abina, Salima ^b   Gaspar, H Bobby ^b   Blanche, Stephane ^b   Davies, E Graham ^b   Parsley, Kathryn ^b   Gilmour, Kimberly ^b   King, Douglas ^b   Howe, Steven ^b   Sinclair, Joanna ^b   Hue, Christophe ^b   Carlier, Frédérique ^b   Von Kalle, Christof ^b   De Saint Basile, Geneviève ^b   Le Deist, Françoise ^b   Fischer, Alain ^b   Cavazzana Calvo, Marina ^a  

^a HÔPITAL NECKER ENFANTS MALADES   (France)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

CD34 ANTIGEN; RECOMBINANT DNA;

ADULT; ANAMNESIS; ARTICLE; BLOOD DONOR; BRONCHIECTASIS; CASE REPORT; CHRONIC DISEASE; CLINICAL FEATURE; COMBINED IMMUNODEFICIENCY; DIARRHEA; DRUG EFFICACY; GENE THERAPY; GENE TRANSFER; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEPATITIS; HERPES ZOSTER; HLA SYSTEM; HUMAN; LUNG INSUFFICIENCY; MALE; PRIORITY JOURNAL; PROTEIN LOSING GASTROENTEROPATHY; RECURRENT DISEASE; TREATMENT FAILURE; X CHROMOSOME LINKED DISORDER;

EID: 21144439712     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood-2004-12-4837     Document Type: Article

References (19)

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