Increased levels of spliced RNA account for augmented expression from the MFG retroviral vector in hematopoietic cells

Gene Therapy

Volumn 3, Issue 1, 1996, Pages 37-48

  Krall, W J ^a,b   Skelton, D C ^a,b   Yu, X J ^a,b   Riviere, I ^c   Lehn, P ^c   Mulligan, R C ^c   Kohn, D B ^a,b  

^a CHILDREN S HOSPITAL LOS ANGELES   (United States)

^b UNIVERSITY OF SOUTHERN CALIFORNIA   (United States)

^c WHITEHEAD INSTITUTE FOR BIOMEDICAL RESEARCH   (United States)

Author keywords

gene therapy; glucocerebrosidase; MFG; retroviral vector; splicing

Indexed keywords

GLUCOSYLCERAMIDASE; MESSENGER RNA; RNA; VIRUS VECTOR;

ARTICLE; CONTROLLED STUDY; GENE THERAPY; HEMATOPOIETIC CELL; HUMAN; HUMAN CELL; NONHUMAN; PRIORITY JOURNAL; RETROVIRUS; RNA SPLICING; SPLEEN CELL; VIRUS EXPRESSION;

ANIMALS; BLOTTING, WESTERN; CELLS, CULTURED; CODON, INITIATOR; GENE EXPRESSION REGULATION, VIRAL; GENETIC VECTORS; GLUCOSYLCERAMIDASE; HUMANS; MALE; MICE; MICE, INBRED C57BL; MOLONEY MURINE LEUKEMIA VIRUS; PROTEIN BIOSYNTHESIS; RETROVIRIDAE; RNA SPLICING; SPLEEN;

EID: 0029965285     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

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