Effective Gene Therapy of Mice with Congenital Erythropoietic Porphyria Is Facilitated by a Survival Advantage of Corrected Erythroid Cells

American Journal of Human Genetics

Volumn 82, Issue 1, 2008, Pages 113-124

  Robert Richard, Elodie ^a,b   Moreau Gaudry, François ^a,b   Lalanne, Magalie ^a,b   Lamrissi Garcia, Isabelle ^a,b   Cario André, Muriel ^a,b   Guyonnet Dupérat, Véronique ^a,b   Taine, Laurence ^a,b   Ged, Cécile ^a,b   de Verneuil, Hubert ^a,b  

^a INSERM   (France)

^b UNIVERSITÉ DE BORDEAUX   (France)

Author keywords

[No Author keywords available]

Indexed keywords

UROPORPHYRINOGEN III SYNTHASE;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONGENITAL ERYTHROPOIETIC PORPHYRIA; ENZYME ACTIVITY; ERYTHROID CELL; GENE THERAPY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; METABOLIC REGULATION; MOUSE; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; SURVIVAL; ANIMAL; BAGG ALBINO MOUSE; CELL SURVIVAL; DISEASE MODEL; ERYTHROCYTE; FEMALE; GENE VECTOR; GENETICS; HEMATOPOIETIC STEM CELL; LENTIVIRINAE; MALE;

LENTIVIRUS; MURINAE; MUS;

ANIMALS; CELL SURVIVAL; DISEASE MODELS, ANIMAL; ERYTHROCYTES; FEMALE; GENE THERAPY; GENETIC VECTORS; HEMATOPOIETIC STEM CELLS; LENTIVIRUS; MALE; MICE; MICE, INBRED BALB C; PORPHYRIA, ERYTHROPOIETIC; UROPORPHYRINOGEN III SYNTHETASE;

EID: 38749144819     PISSN: 00029297     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.ajhg.2007.09.007     Document Type: Article

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