Successful correction of the human Cooley's anemia β-thalassemia major phenotype using a lentiviral vector flanked by the chicken hypersensitive site 4 chromatin insulator

Annals of the New York Academy of Sciences

Volumn 1054, Issue , 2005, Pages 238-249

  Malik, Punam ^a,b   Arumugam, Paritha I ^a   Yee, Jing Kuan ^c   Puthenveetil, Geetha ^a  

^a CHILDREN S HOSPITAL LOS ANGELES   (United States)

^b UNIVERSITY OF SOUTHERN CALIFORNIA   (United States)

^c CITY OF HOPE NATIONAL MEDICAL CENTER   (United States)

Author keywords

Lentiviral vector; globin; thalassemia

Indexed keywords

ALPHA GLOBIN; BETA GLOBIN; LENTIVIRUS VECTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; APOPTOSIS; CELL DIFFERENTIATION; CHROMATIN; CONFERENCE PAPER; CONTROLLED STUDY; ERYTHROID CELL; ERYTHROPOIESIS; GENE CASSETTE; GENE THERAPY; GENE TRANSFER; IMMUNE DEFICIENCY; METHYLATION; MOUSE; NONHUMAN; PHENOTYPE; PROVIRUS; STEM CELL; THALASSEMIA MAJOR; VIRUS INACTIVATION; XENOTRANSPLANTATION;

ANIMALIA; LENTIVIRUS;

EID: 29744454288     PISSN: 00778923     EISSN: None     Source Type: Book Series    
DOI: 10.1196/annals.1345.030     Document Type: Conference Paper

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