Long-term cure of the photosensitivity of murine erythropoietic protoporphyria by preselective gene therapy

Nature Medicine

Volumn 5, Issue 7, 1999, Pages 768-773

  Pawliuk, Robert ^a,b   Bachelot, Thomas ^a   Wise, Robert J ^c   Mathews Roth, Micheline M ^c   Leboulch, Philippe ^a,b,c  

^a MASSACHUSETTS INSTITUTE OF TECHNOLOGY   (United States)

^b Genetix Pharmaceuticals Inc   (United States)

^c BRIGHAM AND WOMEN S HOSPITAL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

FERROCHELATASE; PROTOPORPHYRIN;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BONE MARROW TRANSPLANTATION; CELL SELECTION; ERYTHROPOIETIC PROTOPORPHYRIA; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; HEME SYNTHESIS; MOUSE; NONHUMAN; PHOTOSENSITIVITY; PRIORITY JOURNAL;

ANIMALIA; MURINAE; UNIDENTIFIED RETROVIRUS;

EID: 0033021063     PISSN: 10788956     EISSN: None     Source Type: Journal    
DOI: 10.1038/10488     Document Type: Article

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