Successful correction of the human β-thalassemia major phenotype using a lentiviral vector

Blood

Volumn 104, Issue 12, 2004, Pages 3445-3453

  Puthenveetil, Geetha ^b   Scholes, Jessica ^b   Carbonell, Denysha ^b   Qureshi, Naveen ^b   Xia, Ping ^b   Zeng, Licheng ^b   Li, Shulian ^b   Yu, Ying ^b   Hiti, Alan L ^b   Yee, Jiing Kuan ^b   Malik, Punam ^a  

^a CHILDREN S HOSPITAL LOS ANGELES   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLOBIN; LENTIVIRUS VECTOR; RETROVIRUS VECTOR;

ADULT; ALPHA THALASSEMIA; APOPTOSIS; ARTICLE; CELL CULTURE; CELL DIFFERENTIATION; CHILD; CHROMATIN; CONTROLLED STUDY; DNA MODIFICATION; ERYTHROID CELL; GENE CASSETTE; GENE EXPRESSION; GENE THERAPY; HUMAN; HUMAN CELL; IMMUNE DEFICIENCY; INFANT; MOUSE; NONHUMAN; NUCLEOTIDE SEQUENCE; PHENOTYPE; PRIORITY JOURNAL; STEM CELL TRANSPLANTATION; XENOTRANSPLANTATION;

EID: 9444281434     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood-2004-04-1427     Document Type: Article

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