Gene therapy progress and prospects: Hydrodynamic gene delivery

Gene Therapy

Volumn 14, Issue 2, 2007, Pages 99-107

  Herweijer, H ^a   Wolff, J A ^a,b  

^a Mirus Bio Corporation   (United States)

^b UNIVERSITY OF WISCONSIN SCHOOL OF MEDICINE AND PUBLIC HEALTH   (United States)

Author keywords

Hydrodynamic delivery; Naked plasmid DNA; Non viral

Indexed keywords

BETA GALACTOSIDASE; DYSTROPHIN; GLUCURONOSYLTRANSFERASE 1A1; GLYCOPROTEIN B; HERPES SIMPLEX VACCINE; LUCIFERASE; NAKED DNA; PLASMID DNA; SMALL INTERFERING RNA;

BLOOD PRESSURE; BRAIN TUMOR; CELL SURVIVAL; CLINICAL TRIAL; CRIGLER NAJJAR SYNDROME; DISEASE MODEL; DRUG EFFICACY; DRUG SAFETY; DUCHENNE MUSCULAR DYSTROPHY; GENE EXPRESSION; GENE TRANSFER; GENETIC TRANSFECTION; HERPES SIMPLEX; HUMAN; HYDRODYNAMICS; HYPERBILIRUBINEMIA; IMMUNE RESPONSE; IN VIVO STUDY; LIVER CELL; MUSCLE DISEASE; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; NONVIRAL GENE THERAPY; PRIORITY JOURNAL; PROCESS OPTIMIZATION; PROMOTER REGION; REPORTER GENE; REVIEW; RNA INTERFERENCE; SKELETAL MUSCLE; TRANSGENE; TRANSGENIC ANIMAL; VACCINATION;

ANIMALS; DNA; GENE THERAPY; HUMANS; INJECTIONS, INTRAVENOUS; LIVER; MICE; MODELS, ANIMAL; MUSCLE, SKELETAL; RNA, SMALL INTERFERING; TRANSFECTION;

ANIMALIA; RODENTIA;

EID: 33846022383     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/sj.gt.3302891     Document Type: Review

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