Restoration of dystrophin expression in mdx mice by intravascular injection of naked DNA containing full-length dystrophin cDNA

Gene Therapy

Volumn 11, Issue 11, 2004, Pages 901-908

  Liang, K W ^a   Nishikawa, M ^a   Lui, F ^a   Sun, B ^a   Ye, Q ^b   Huang, L ^a  

^a UNIVERSITY OF PITTSBURGH   (United States)

^b CARNEGIE MELLON UNIVERSITY   (United States)

Author keywords

Duchenne muscular dystrophy; Muscle; Naked DNA; Nonviral vector

Indexed keywords

BETA GALACTOSIDASE; COMPLEMENTARY DNA; DYSTROPHIN; LUCIFERASE; NAKED DNA; PLASMID DNA; VIRUS VECTOR;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; AORTA CLAMPING; ARTICLE; CAVA VEIN; CONTROLLED STUDY; DISEASE MODEL; DOSE RESPONSE; DUCHENNE MUSCULAR DYSTROPHY; GENE LOCATION; GENE TRANSFER; HINDLIMB; ISCHEMIA; LETHALITY; LONG TERM CARE; MOUSE; MOUSE STRAIN; MUSCLE CELL; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; NONVIRAL GENE THERAPY; PRIORITY JOURNAL; PROTEIN EXPRESSION; SKELETAL MUSCLE; TAIL ARTERY; TISSUE DISTRIBUTION; X CHROMOSOME LINKED DISORDER;

ANIMALS; AORTA; BETA-GALACTOSIDASE; DNA; DYSTROPHIN; GENE EXPRESSION; GENE THERAPY; HINDLIMB; INJECTIONS, INTRAVENOUS; LIGATION; LUCIFERASES; MICE; MICE, INBRED MDX; MUSCULAR DYSTROPHY, DUCHENNE; TAIL; TRANSFECTION; VENAE CAVAE;

ANIMALIA;

EID: 2942724130     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3302239     Document Type: Article

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