-
1
-
-
17144401470
-
Novel molecular approaches to cystic fibrosis gone therapy
-
Lee TWR, Matthews DA, Blair GE: Novel molecular approaches to cystic fibrosis gone therapy. Biochem J (2005) 387(1):1-15.
-
(2005)
Biochem J
, vol.387
, Issue.1
, pp. 1-15
-
-
Lee, T.W.R.1
Matthews, D.A.2
Blair, G.E.3
-
2
-
-
0024550966
-
In vitro translation, posttranslational processing and secretion of pulmonary surfactant protein B precursors
-
O'Reilly MA, Weaver TE, Pilot-Matias TJ, Sarin VK, Gazdar AF, Whitsett JA: In vitro translation, posttranslational processing and secretion of pulmonary surfactant protein B precursors. Biochim Biophys Acta (1989) 1011(2-3):140-148.
-
(1989)
Biochim Biophys Acta
, vol.1011
, Issue.2-3
, pp. 140-148
-
-
O'Reilly, M.A.1
Weaver, T.E.2
Pilot-Matias, T.J.3
Sarin, V.K.4
Gazdar, A.F.5
Whitsett, J.A.6
-
3
-
-
0030724604
-
Lung transplantation for treatment of Infants with surfactant protein B deficiency
-
Hamvas A, Nogee LM, Mallory GB, Spray TL, Huddleston CB, August A, Dehner LP, deMello DE, Moxley M, Nelson R, Cole FS et al: Lung transplantation for treatment of Infants with surfactant protein B deficiency. J Pediatr (1997) 130(2):231-239.
-
(1997)
J Pediatr
, vol.130
, Issue.2
, pp. 231-239
-
-
Hamvas, A.1
Nogee, L.M.2
Mallory, G.B.3
Spray, T.L.4
Huddleston, C.B.5
August, A.6
Dehner, L.P.7
deMello, D.E.8
Moxley, M.9
Nelson, R.10
Cole, F.S.11
-
4
-
-
0029096591
-
Targeted disruption of the surfactant protein B gene disrupts surfactant homeostasis, causing respiratory failure in newborn mice
-
Clark JC, Wert SE, Bachurski CJ, Stahiman MT, Stripp, BR, Weaver TE, Whitsett JA: Targeted disruption of the surfactant protein B gene disrupts surfactant homeostasis, causing respiratory failure in newborn mice. Proc Natl Acad Sci USA (1995) 92(17):7794-7798.
-
(1995)
Proc Natl Acad Sci USA
, vol.92
, Issue.17
, pp. 7794-7798
-
-
Clark, J.C.1
Wert, S.E.2
Bachurski, C.J.3
Stahiman, M.T.4
Stripp, B.R.5
Weaver, T.E.6
Whitsett, J.A.7
-
5
-
-
3042663294
-
Genetic mechanisms of surfactant deficiency
-
Nogee LM: Genetic mechanisms of surfactant deficiency. Biol Neonate (2004) 85(4):314-318.
-
(2004)
Biol Neonate
, vol.85
, Issue.4
, pp. 314-318
-
-
Nogee, L.M.1
-
6
-
-
0033883899
-
Prolonged survival in hereditary surfactant protein B (SP-B) deficiency associated with a novel splicing mutation
-
Dunbar AE III, Wert SE, Ikegami M, Whitsett JA, Hamvas A, White FV, Piedboeuf B, Jobin C, Guttentag S, Nogee LM: Prolonged survival in hereditary surfactant protein B (SP-B) deficiency associated with a novel splicing mutation. Pediatr Res (2000) 48(3)275-282
-
(2000)
Pediatr Res
, vol.48
, Issue.3
, pp. 275-282
-
-
Dunbar III, A.E.1
Wert, S.E.2
Ikegami, M.3
Whitsett, J.A.4
Hamvas, A.5
White, F.V.6
Piedboeuf, B.7
Jobin, C.8
Guttentag, S.9
Nogee, L.M.10
-
7
-
-
0033041764
-
Normal lung function in subjects heterozygous for surfactant protein-B deficiency
-
Yusen, RD, Cohen, AH, Hamvas, A: Normal lung function in subjects heterozygous for surfactant protein-B deficiency. Am J Respir Crit Care Med (11999) 159(2):411-414.
-
(1999)
Am J Respir Crit Care Med
, vol.159
, Issue.2
, pp. 411-414
-
-
Yusen, R.D.1
Cohen, A.H.2
Hamvas, A.3
-
8
-
-
0028807727
-
T lymphocyte-directed gone therapy for ADA-SCID: Initial trial results after 4 years
-
Blaese RM, Culver KW, Miller AD, Fleisher T, Clerici M, Shearer G, Chang L, Chiang Y, Tolstoshev, P, Greenblatt JJ, Rosenberg SA et al: T lymphocyte-directed gone therapy for ADA-SCID: Initial trial results after 4 years. Science (1995) 270(5235):475-480.
-
(1995)
Science
, vol.270
, Issue.5235
, pp. 475-480
-
-
Blaese, R.M.1
Culver, K.W.2
Miller, A.D.3
Fleisher, T.4
Clerici, M.5
Shearer, G.6
Chang, L.7
Chiang, Y.8
Tolstoshev, P.9
Greenblatt, J.J.10
Rosenberg, S.A.11
-
9
-
-
0031564175
-
Lentiviral vectors for gene therapy of cystic fibrosis
-
Goldman MJ, Lee PS, Yang JS, Wilson JM: Lentiviral vectors for gene therapy of cystic fibrosis. Hum Gene Ther (1997) 8(18):2261-2268.
-
(1997)
Hum Gene Ther
, vol.8
, Issue.18
, pp. 2261-2268
-
-
Goldman, M.J.1
Lee, P.S.2
Yang, J.S.3
Wilson, J.M.4
-
10
-
-
0033428995
-
Feline immunodeficiency virus vectors persistently transduce non-dividing airway epithelia and correct the cystic fibrosis defect
-
Wang GSV, Zabner J, Keshavjee S, Johnston JC, Sauter SL, Jolly DJ, Dubensky TW Jr, Davidson BL, McCray PB Jr: Feline immunodeficiency virus vectors persistently transduce non-dividing airway epithelia and correct the cystic fibrosis defect J Clin Invest (1999) 104(11): R55-62.
-
(1999)
J Clin Invest
, vol.104
, Issue.11
-
-
Wang, G.S.V.1
Zabner, J.2
Keshavjee, S.3
Johnston, J.C.4
Sauter, S.L.5
Jolly, D.J.6
Dubensky Jr, T.W.7
Davidson, B.L.8
McCray Jr., P.B.9
-
11
-
-
17144421636
-
Stable and efficient gene transfer in airway of non-human primates with HIV vector pseudotyped with deletion mutant of Ebola envelope glycoproteins
-
Abs 209
-
Kobinger GP, Schumer GP, Medina MF, Weiner DJ, Wilson JM: Stable and efficient gene transfer in airway of non-human primates with HIV vector pseudotyped with deletion mutant of Ebola envelope glycoproteins. Pediatr Pulmonol Suppl (2003) 25:Abs 209.
-
(2003)
Pediatr Pulmonol Suppl
, vol.25
-
-
Kobinger, G.P.1
Schumer, G.P.2
Medina, M.F.3
Weiner, D.J.4
Wilson, J.M.5
-
12
-
-
0142084745
-
LMO2-associated clonal T-cell proliferation in two patients after gene therapy for SCID-X1
-
Hacein-Bey-Abina S, Von Kalle C, Schmidt M, McCormack MP, Wulffraat N, Leboulch P, Lim A, Osborne CS, Pawliuk R, Morillon E, Sorensen R et al: LMO2-associated clonal T-cell proliferation in two patients after gene therapy for SCID-X1. Science (2003) 302(5644):415-419.
-
(2003)
Science
, vol.302
, Issue.5644
, pp. 415-419
-
-
Hacein-Bey-Abina, S.1
Von Kalle, C.2
Schmidt, M.3
McCormack, M.P.4
Wulffraat, N.5
Leboulch, P.6
Lim, A.7
Osborne, C.S.8
Pawliuk, R.9
Morillon, E.10
Sorensen, R.11
-
13
-
-
0027967986
-
Inefficient gene transfer of adenovirus vector to cystic fibrosis airway epithelia of mice and humans
-
Grubb BR, Pickles RJ, Ye H, Yankaskas JR, Vick RN, Engelhardt JF, Wilson JM, Johnson LG, Boucher RC: Inefficient gene transfer of adenovirus vector to cystic fibrosis airway epithelia of mice and humans. Nature (1994) 371(6500):802-806.
-
(1994)
Nature
, vol.371
, Issue.6500
, pp. 802-806
-
-
Grubb, B.R.1
Pickles, R.J.2
Ye, H.3
Yankaskas, J.R.4
Vick, R.N.5
Engelhardt, J.F.6
Wilson, J.M.7
Johnson, L.G.8
Boucher, R.C.9
-
14
-
-
0034044848
-
Retargeting the coxsacklevirus and adenovirus receptor to the apical surface of polarised epithelial cells reveals the glycocalyx as a barrier to adenovirus mediated gene transfer
-
Pickles RJ, Fahmer JA Petrella JM, Boucher, RC, Bergelson JM: Retargeting the coxsacklevirus and adenovirus receptor to the apical surface of polarised epithelial cells reveals the glycocalyx as a barrier to adenovirus mediated gene transfer. J Virol (2000) 74(13):6050-6057.
-
(2000)
J Virol
, vol.74
, Issue.13
, pp. 6050-6057
-
-
Pickles, R.J.1
Fahmer, J.A.2
Petrella, J.M.3
Boucher, R.C.4
Bergelson, J.M.5
-
15
-
-
0033537837
-
Basolateral localization of fiber receptors limits adenovirus infection from the apleall surface of airway epithelia
-
Walters, RW, Grunst, T, Bergelson, JM, Finberg, RW, Welsh, MJ, Zabner J: Basolateral localization of fiber receptors limits adenovirus infection from the apleall surface of airway epithelia. J Biol Chem (1999) 274(15):10219-10226.
-
(1999)
J Biol Chem
, vol.274
, Issue.15
, pp. 10219-10226
-
-
Walters, R.W.1
Grunst, T.2
Bergelson, J.M.3
Finberg, R.W.4
Welsh, M.J.5
Zabner, J.6
-
16
-
-
0028991821
-
In vitro and in vivo transfer and expression of human surfactant SP-A- and SP-B-associated protein cDNAs mediated by replication deficient, recombinant adenoviral vectors
-
Korst RJ, Bewig B, Crystal RG: In vitro and in vivo transfer and expression of human surfactant SP-A- and SP-B-associated protein cDNAs mediated by replication deficient, recombinant adenoviral vectors. Hum Gene Ther (1995) 6(3):277-287.
-
(1995)
Hum Gene Ther
, vol.6
, Issue.3
, pp. 277-287
-
-
Korst, R.J.1
Bewig, B.2
Crystal, R.G.3
-
17
-
-
0031034030
-
Innate Immune mechanisms dominate elimination of adenoviral vectors following in vivo administration
-
Orgall S, Wolff G, Falck-Pedersen E, Crystal RG: Innate Immune mechanisms dominate elimination of adenoviral vectors following in vivo administration. Hum Gene Ther (1997) 8(1):37-44.
-
(1997)
Hum Gene Ther
, vol.8
, Issue.1
, pp. 37-44
-
-
Orgall, S.1
Wolff, G.2
Falck-Pedersen, E.3
Crystal, R.G.4
-
18
-
-
0029028989
-
Clearance of adenovirus-infected hepatocytes by MHC class I restricted CD4+ CTLs in vivo
-
Yang Y, Wilson JM: Clearance of adenovirus-infected hepatocytes by MHC class I restricted CD4+ CTLs in vivo. J Immmunol (1995) 155(5):2564-2569.
-
(1995)
J Immmunol
, vol.155
, Issue.5
, pp. 2564-2569
-
-
Yang, Y.1
Wilson, J.M.2
-
19
-
-
0031041586
-
Effect of the E4 region on the persistence of transgene expression from adenovirus vectors
-
Armentano D, Zabner J, Sacks C, Sookdeo CC, Smith MP, St George JA Wadsworth SC, Smith AE, Gregory RJ: Effect of the E4 region on the persistence of transgene expression from adenovirus vectors. J Virol (1997) 71(3):2408-2416.
-
(1997)
J Virol
, vol.71
, Issue.3
, pp. 2408-2416
-
-
Armentano, D.1
Zabner, J.2
Sacks, C.3
Sookdeo, C.C.4
Smith, M.P.5
St George, J.A.6
Wadsworth, S.C.7
Smith, A.E.8
Gregory, R.J.9
-
20
-
-
0031916435
-
Genomic DNA transfer with a high capacity adenovirus vector results in improved in vivo gene expression and decreased toxicity
-
Schiedner G, Morral N, Parks RJ, Wu Y, Koopmans SC, Langston C, Graham FL, Beaudet AL, Kochanek S: Genomic DNA transfer with a high capacity adenovirus vector results in improved in vivo gene expression and decreased toxicity. Nat Genet (1998) 18(3):180-183.
-
(1998)
Nat Genet
, vol.18
, Issue.3
, pp. 180-183
-
-
Schiedner, G.1
Morral, N.2
Parks, R.J.3
Wu, Y.4
Koopmans, S.C.5
Langston, C.6
Graham, F.L.7
Beaudet, A.L.8
Kochanek, S.9
-
21
-
-
0025214094
-
Site-specific integration by adeno-associated virus
-
Kotin RM, Siniscalco M, Samulski RJ, Zhu XD, Hunter L, Laughlin CA, McLaughlin S, Muzyczka N, Rocchi M, Berns KI: Site-specific integration by adeno-associated virus. Proc Natl Acad Sci USA (1990) 87(6):2211-2215.
-
(1990)
Proc Natl Acad Sci USA
, vol.87
, Issue.6
, pp. 2211-2215
-
-
Kotin, R.M.1
Siniscalco, M.2
Samulski, R.J.3
Zhu, X.D.4
Hunter, L.5
Laughlin, C.A.6
McLaughlin, S.7
Muzyczka, N.8
Rocchi, M.9
Berns, K.I.10
-
22
-
-
0030773872
-
Adeno-associated virus integration junctions
-
Rutledge EA, Russell DW. Adeno-associated virus integration junctions. J Virol (1997) 71(11):8429-8436
-
(1997)
J Virol
, vol.71
, Issue.11
, pp. 8429-8436
-
-
Rutledge, E.A.1
Russell, D.W.2
-
23
-
-
0028834822
-
Viral vectors in gone therapy
-
Smith AE: Viral vectors in gone therapy. Annu Rev Microbiol (1995) 49:807-838.
-
(1995)
Annu Rev Microbiol
, vol.49
, pp. 807-838
-
-
Smith, A.E.1
-
24
-
-
20844433393
-
Adeno-associated virus-mediated gene transfer for lung diseases
-
Flotte TR: Adeno-associated virus-mediated gene transfer for lung diseases. Hum Gene Ther (2005) 16(6):643-648.
-
(2005)
Hum Gene Ther
, vol.16
, Issue.6
, pp. 643-648
-
-
Flotte, T.R.1
-
25
-
-
0037197740
-
Phase 1/2 placebo-controlled, double-blind, dose-escalating trial of myocardial vascular endothelial growth factor 2 gene transfer by catheter delivery in patients with chronic myocardial ischaemia
-
Losardo DW, Vale PR, Hendel RC, Milliken CE, Fortuin FD, Cummings N, Schatz RA, Asahara T, Isner JM, Kuntz RE: Phase 1/2 placebo-controlled, double-blind, dose-escalating trial of myocardial vascular endothelial growth factor 2 gene transfer by catheter delivery in patients with chronic myocardial ischaemia. Circulation (2002) 105(17):2012-2018.
-
(2002)
Circulation
, vol.105
, Issue.17
, pp. 2012-2018
-
-
Losardo, D.W.1
Vale, P.R.2
Hendel, R.C.3
Milliken, C.E.4
Fortuin, F.D.5
Cummings, N.6
Schatz, R.A.7
Asahara, T.8
Isner, J.M.9
Kuntz, R.E.10
-
26
-
-
0035004884
-
Improvement in chronic Ischaemic neuropathy after intramuscular phVEGF165 gene transfer in patients with critical limb ischaemia
-
Simovic D, Isner JM, Ropper AH, Pieczek A, Wainberg DH: Improvement in chronic Ischaemic neuropathy after intramuscular phVEGF165 gene transfer in patients with critical limb ischaemia. Arch Neurol (2001) 68(5):761-788.
-
(2001)
Arch Neurol
, vol.68
, Issue.5
, pp. 761-788
-
-
Simovic, D.1
Isner, J.M.2
Ropper, A.H.3
Pieczek, A.4
Wainberg, D.H.5
-
27
-
-
0030759153
-
Comparison of DNA-lipid complexes and DNA alone for gene transfer to cystic fibrosis airway epithelia in vivo
-
Zabner J, Cheng SH, Meeker D, Launspach J, Balfour R, Perricone MA, Morris JE, Marshall J, Fasbender A, Smith AE, Welsh MJ: Comparison of DNA-lipid complexes and DNA alone for gene transfer to cystic fibrosis airway epithelia in vivo. J Clin Invest (1997) 100(6):1529-1537.
-
(1997)
J Clin Invest
, vol.100
, Issue.6
, pp. 1529-1537
-
-
Zabner, J.1
Cheng, S.H.2
Meeker, D.3
Launspach, J.4
Balfour, R.5
Perricone, M.A.6
Morris, J.E.7
Marshall, J.8
Fasbender, A.9
Smith, A.E.10
Welsh, M.J.11
-
28
-
-
84867563642
-
Nonviral gene delivery: Techniques and implications for molecular medicine
-
Parker AL, Newman C, Briggs S, Seymour L, Sheridan PJ: Nonviral gene delivery: Techniques and implications for molecular medicine. Expert Rev Mol Med (2003) 5:1-15.
-
(2003)
Expert Rev Mol Med
, vol.5
, pp. 1-15
-
-
Parker, A.L.1
Newman, C.2
Briggs, S.3
Seymour, L.4
Sheridan, P.J.5
-
29
-
-
0031056543
-
Gene transfer by guanidinium-cholosterol cationic lipids into airway epithelial cells in vitro and in vivo
-
Oudrhiri N, Vigneron JP, Peuchmaur M, Leclerc T, Lehn JM, Lehn P: Gene transfer by guanidinium-cholosterol cationic lipids into airway epithelial cells in vitro and in vivo. Proc Natl Acad Sci USA (1997) 94(5):1651-1656.
-
(1997)
Proc Natl Acad Sci USA
, vol.94
, Issue.5
, pp. 1651-1656
-
-
Oudrhiri, N.1
Vigneron, J.P.2
Peuchmaur, M.3
Leclerc, T.4
Lehn, J.M.5
Lehn, P.6
-
30
-
-
17344362631
-
Cationic phosphonolipids as nonvirall gene transfer agents in the lungs of mice
-
Guillaume-Gable C, Floch V, Mercier B, Audrezet MP, Gobin E, Le Bolch G, Yaouanc JJ, Clement JC, des Abbayes H, Leroy JP, Morin V et al: Cationic phosphonolipids as nonvirall gene transfer agents in the lungs of mice. Hum Gene Ther (1998) 9(16):2309-2319.
-
(1998)
Hum Gene Ther
, vol.9
, Issue.16
, pp. 2309-2319
-
-
Guillaume-Gable, C.1
Floch, V.2
Mercier, B.3
Audrezet, M.P.4
Gobin, E.5
Le Bolch, G.6
Yaouanc, J.J.7
Clement, J.C.8
des Abbayes, H.9
Leroy, J.P.10
Morin, V.11
-
31
-
-
0033660570
-
Safety and biological efficacy of a Lipid-CFTR complex for gene transfer in the nasal epithelium of adult patients with cystic fibrosis
-
Noone PG, Hohneker KW, Zhou Z, Johnson LG, Foy C, Gipson C, Jones K, Noah TL, Leigh MW, Schwartybach C, Efthimiou J et al: Safety and biological efficacy of a Lipid-CFTR complex for gene transfer in the nasal epithelium of adult patients with cystic fibrosis. Mol Ther (2000) 1(1):105-114.
-
(2000)
Mol Ther
, vol.1
, Issue.1
, pp. 105-114
-
-
Noone, P.G.1
Hohneker, K.W.2
Zhou, Z.3
Johnson, L.G.4
Foy, C.5
Gipson, C.6
Jones, K.7
Noah, T.L.8
Leigh, M.W.9
Schwartybach, C.10
Efthimiou, J.11
-
32
-
-
0034915570
-
A clinical inflammatory syndrome attributable to aerosolized lipid-DNA administration in cystic fibrosis
-
Ruiz FE, Clancy JP, Perricone MA, Bebok Z, Hong JS, Cheng SH, Meeker DP, Young KR, Schoumacher RA, Weatherly MR, Wing L et al: A clinical inflammatory syndrome attributable to aerosolized lipid-DNA administration in cystic fibrosis. Hum Gene Ther (2001) 12(7):751-761.
-
(2001)
Hum Gene Ther
, vol.12
, Issue.7
, pp. 751-761
-
-
Ruiz, F.E.1
Clancy, J.P.2
Perricone, M.A.3
Bebok, Z.4
Hong, J.S.5
Cheng, S.H.6
Meeker, D.P.7
Young, K.R.8
Schoumacher, R.A.9
Weatherly, M.R.10
Wing, L.11
-
33
-
-
0034070034
-
Gene delivery and expression in human retinal pigment epithelial cells: Effects of synthetic carriers, serum, extracellular matrix and viral promoters
-
Urtti A, Polansky J, Lui GM, Szoka FC: Gene delivery and expression in human retinal pigment epithelial cells: Effects of synthetic carriers, serum, extracellular matrix and viral promoters. J Drug Target (2000) 7(6):413-421.
-
(2000)
J Drug Target
, vol.7
, Issue.6
, pp. 413-421
-
-
Urtti, A.1
Polansky, J.2
Lui, G.M.3
Szoka, F.C.4
-
34
-
-
0031717882
-
Stable and monodisperse lipoplex formulations for gene delivery
-
Zelphati O, Nguyen C, Ferrari M, Felgner J, Tsai Y, Felgner PL: Stable and monodisperse lipoplex formulations for gene delivery. Gene Ther (1998) 5(9):1272-1282.
-
(1998)
Gene Ther
, vol.5
, Issue.9
, pp. 1272-1282
-
-
Zelphati, O.1
Nguyen, C.2
Ferrari, M.3
Felgner, J.4
Tsai, Y.5
Felgner, P.L.6
-
35
-
-
0022558795
-
Construction of transferrin-coated liposomes for in vivo transport of exogenous DNA to bone marrow erythroblasts in rabbits
-
Stavridis JC, Deliconstantinos G, Psallidopoulos MC, Armenakas NS, Hadjiminas DJ, Hadjiminas J: Construction of transferrin-coated liposomes for in vivo transport of exogenous DNA to bone marrow erythroblasts in rabbits. Exp Cell Res (1986) 164(2):568-572.
-
(1986)
Exp Cell Res
, vol.164
, Issue.2
, pp. 568-572
-
-
Stavridis, J.C.1
Deliconstantinos, G.2
Psallidopoulos, M.C.3
Armenakas, N.S.4
Hadjiminas, D.J.5
Hadjiminas, J.6
-
36
-
-
0029859574
-
Fusigenic viral liposome for gene therapy in cardiovascular disease
-
Dzau JV, Mann MJ, Morishita R, Kaneda Y: Fusigenic viral liposome for gene therapy in cardiovascular disease. Proc Natl Acad Sci USA (1998) 93(21):11421-11425.
-
(1998)
Proc Natl Acad Sci USA
, vol.93
, Issue.21
, pp. 11421-11425
-
-
Dzau, J.V.1
Mann, M.J.2
Morishita, R.3
Kaneda, Y.4
-
37
-
-
0029160083
-
A versatile vector for gene and oligonucleotide transfer into cells in culture and in vivo. Polyethylenimine
-
Boussif O, Lezoualc'h F, Zanta MA, Mergny M, Scherman D, Demeneix B, Behr JP: A versatile vector for gene and oligonucleotide transfer into cells in culture and in vivo. Polyethylenimine. Proc Natl Acad Sci USA (1995) 92(16):7297-7301.
-
(1995)
Proc Natl Acad Sci USA
, vol.92
, Issue.16
, pp. 7297-7301
-
-
Boussif, O.1
Lezoualc'h, F.2
Zanta, M.A.3
Mergny, M.4
Scherman, D.5
Demeneix, B.6
Behr, J.P.7
-
38
-
-
0034152683
-
Systemic linear polyethylenimine (L-PEI)-modiated gene delivery in the mouse
-
Zou SM, Erbacher P, Remy JS, Behr JP: Systemic linear polyethylenimine (L-PEI)-modiated gene delivery in the mouse. J Gene Med (2000) 2(2):128-134.
-
(2000)
J Gene Med
, vol.2
, Issue.2
, pp. 128-134
-
-
Zou, S.M.1
Erbacher, P.2
Remy, J.S.3
Behr, J.P.4
-
39
-
-
0034136169
-
Aerosol delivery of robust PEI-DNA complexes for gene therapy and genetic immunization
-
Densmore CL, Orson F, Xu B, Kinsey BM, Waldrep JC, Hue P, Bhogal B, Knight V: Aerosol delivery of robust PEI-DNA complexes for gene therapy and genetic immunization. Mol Ther (2000) 1(2):180-188.
-
(2000)
Mol Ther
, vol.1
, Issue.2
, pp. 180-188
-
-
Densmore, C.L.1
Orson, F.2
Xu, B.3
Kinsey, B.M.4
Waldrep, J.C.5
Hue, P.6
Bhogal, B.7
Knight, V.8
-
40
-
-
23844528337
-
Aerosolized nanogram quantities of plasmid DNA mediate highly efficient gene delivery to mouse airway epithelium
-
Rudolph C, Schillinger U, Ortiz A, Plank C, Golas MM, Sander B, Stark H, Rosenecker J: Aerosolized nanogram quantities of plasmid DNA mediate highly efficient gene delivery to mouse airway epithelium. Mol Ther (2005) 12(3):493-501.
-
(2005)
Mol Ther
, vol.12
, Issue.3
, pp. 493-501
-
-
Rudolph, C.1
Schillinger, U.2
Ortiz, A.3
Plank, C.4
Golas, M.M.5
Sander, B.6
Stark, H.7
Rosenecker, J.8
-
41
-
-
0034952813
-
Nuclear translocation of lactosylated Poly-L-lysine/cDNA complex in cystic fibrosis airway epithelial cells
-
Klink DT, Chao S, Glick MC, Scanlin TF: Nuclear translocation of lactosylated Poly-L-lysine/cDNA complex in cystic fibrosis airway epithelial cells. Mol Ther (2001) 3(6):831-841.
-
(2001)
Mol Ther
, vol.3
, Issue.6
, pp. 831-841
-
-
Klink, D.T.1
Chao, S.2
Glick, M.C.3
Scanlin, T.F.4
-
42
-
-
2242492171
-
Molecular conjugate mediated CFTR gene transfer in CF mice affects secondary CF defects
-
Ziady AG, Kelley T, Davis PB: Molecular conjugate mediated CFTR gene transfer in CF mice affects secondary CF defects. Pediatr Pulmonol Suppl (2001) 22:254.
-
(2001)
Pediatr Pulmonol Suppl
, vol.22
, pp. 254
-
-
Ziady, A.G.1
Kelley, T.2
Davis, P.B.3
-
43
-
-
0033764455
-
Supramolecular structure and nuclear targeting efficiency determine the enhancement of transfection by modified polylysines
-
Chan CK, Senden T, Jans DA: Supramolecular structure and nuclear targeting efficiency determine the enhancement of transfection by modified polylysines. Gene Ther(2000) 7(19):1690-1697.
-
(2000)
Gene Ther
, vol.7
, Issue.19
, pp. 1690-1697
-
-
Chan, C.K.1
Senden, T.2
Jans, D.A.3
-
44
-
-
0037063996
-
Nuclear targeting of macromolecular polyanions by an HIV-Tat derived peptide
-
Sandgren S, Cheng F, Belting M: Nuclear targeting of macromolecular polyanions by an HIV-Tat derived peptide. J Biol Chem (2002) 277(41):38877-38883.
-
(2002)
J Biol Chem
, vol.277
, Issue.41
, pp. 38877-38883
-
-
Sandgren, S.1
Cheng, F.2
Belting, M.3
-
45
-
-
15944400651
-
Towards safe, non-viral therapeutic gene expression in humans
-
Glover DJ, Lipps HJ, Jens DA: Towards safe, non-viral therapeutic gene expression in humans. Nat Rev Genet (2005) 6(4):299-310.
-
(2005)
Nat Rev Genet
, vol.6
, Issue.4
, pp. 299-310
-
-
Glover, D.J.1
Lipps, H.J.2
Jens, D.A.3
-
46
-
-
14744301443
-
Controlling the kinetics of transgene expression by plasmid design
-
Yew NS: Controlling the kinetics of transgene expression by plasmid design. Adv Drug Deliv Rev (2005) 67(5):769-780.
-
(2005)
Adv Drug Deliv Rev
, vol.67
, Issue.5
, pp. 769-780
-
-
Yew, N.S.1
-
47
-
-
17444363398
-
Vectors and delivery systems in gone therapy
-
Gardlik R, Palffy R, Hodosy J, Lukacs J, Turna J, Celec P: Vectors and delivery systems in gone therapy. Med Sci Monit (2005) 11(4):RA110-RA121.
-
(2005)
Med Sci Monit
, vol.11
, Issue.4
-
-
Gardlik, R.1
Palffy, R.2
Hodosy, J.3
Lukacs, J.4
Turna, J.5
Celec, P.6
-
48
-
-
22144464502
-
φC31 integrase confers genomic integration and long-term transgene expression in rat retina
-
Chalberg TW, Genise HL, Vollrath D, Calos MP: φC31 integrase confers genomic integration and long-term transgene expression in rat retina. Invest Ophthalmol Vis Sci (2005) 46(6):2140-2146.
-
(2005)
Invest Ophthalmol Vis Sci
, vol.46
, Issue.6
, pp. 2140-2146
-
-
Chalberg, T.W.1
Genise, H.L.2
Vollrath, D.3
Calos, M.P.4
-
49
-
-
14044257947
-
In vivo correction of murine hereditary tyrosinemia type I by φC31 integrase-mediated gene delivery
-
Held PK, Olivares EC, Aguilar CP, Finegold M, Calos MP, Grompe M: In vivo correction of murine hereditary tyrosinemia type I by φC31 integrase-mediated gene delivery. Mol Ther (2005) 11(3):399-408.
-
(2005)
Mol Ther
, vol.11
, Issue.3
, pp. 399-408
-
-
Held, P.K.1
Olivares, E.C.2
Aguilar, C.P.3
Finegold, M.4
Calos, M.P.5
Grompe, M.6
-
50
-
-
4644292834
-
Nucleofection of muscle-derived stem cells and myoblasts with φC31 integrase: Stable expression of a full-length-dystrophin fusion gene by human myoblasts
-
Quenneville SP, Chapdelaine P, Rousseau J, Beaulieu J, Caron NJ, Skuk D, Mills P, Olivares EC, Calos MP, Tremblay JP: Nucleofection of muscle-derived stem cells and myoblasts with φC31 integrase: Stable expression of a full-length-dystrophin fusion gene by human myoblasts. Mol Ther (2004) 10(4):679-687.
-
(2004)
Mol Ther
, vol.10
, Issue.4
, pp. 679-687
-
-
Quenneville, S.P.1
Chapdelaine, P.2
Rousseau, J.3
Beaulieu, J.4
Caron, N.J.5
Skuk, D.6
Mills, P.7
Olivares, E.C.8
Calos, M.P.9
Tremblay, J.P.10
-
51
-
-
18944373328
-
Highly efficient endogenous human gene correction using designed zinc-finger nucleases
-
Urnov FD, Miller JC, Lee YL, Beausejour CM, Rock JM, Augustus S, Jamieson AC, Porteus MH, Gregory PD, Holmes MC: Highly efficient endogenous human gene correction using designed zinc-finger nucleases. Nature (2005) 435(7042):646-651.
-
(2005)
Nature
, vol.435
, Issue.7042
, pp. 646-651
-
-
Urnov, F.D.1
Miller, J.C.2
Lee, Y.L.3
Beausejour, C.M.4
Rock, J.M.5
Augustus, S.6
Jamieson, A.C.7
Porteus, M.H.8
Gregory, P.D.9
Holmes, M.C.10
-
52
-
-
0035858344
-
Tumor Targeting with surface-shielded ligand-polycation DNA complexes
-
Kircheis R, Blessing T, Brunner S, Wightman L, Wagner E: Tumor Targeting with surface-shielded ligand-polycation DNA complexes. J Control Release (2001) 72(1-3):165-170.
-
(2001)
J Control Release
, vol.72
, Issue.1-3
, pp. 165-170
-
-
Kircheis, R.1
Blessing, T.2
Brunner, S.3
Wightman, L.4
Wagner, E.5
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