Correction of deficient CD34+ cells from peripheral blood after mobilization in a patient with congenital erythropoietic porphyria

Molecular Therapy

Volumn 3, Issue 3, 2001, Pages 411-417

  Mazurier, Frédéric ^a   Géronimi, Fabien ^a   Lamrissi Garcia, Isabelle ^a   Morel, Carine ^a   Richard, Emmanuel ^a   Ged, Cécile ^a   Fontanellas, Antonio ^a   Moreau Gaudry, François ^a   Morey, Miquel ^b   De Verneuil, Hubert ^a  

^a UNIVERSITÉ DE BORDEAUX   (France)

^b HOSPITAL UNIVERSITARIO SON ESPASES   (Spain)

Author keywords

Gene therapy; Hematopoietic stem cells; Mobilized peripheral blood; Porphyria; Retroviral vectors

Indexed keywords

CD34 ANTIGEN; DNA; GREEN FLUORESCENT PROTEIN; HEME; PORPHYRIN; UROPORPHYRIN; UROPORPHYRINOGEN III SYNTHASE;

ADULT; ALLOGENIC BONE MARROW TRANSPLANTATION; ARTICLE; AUTOGRAFT; BLOOD; BLOOD TRANSFUSION; BONE MARROW; CASE REPORT; CELL CULTURE; CELL DIFFERENTIATION; CELL POPULATION; CHILD; CONGENITAL ERYTHROPOIETIC PORPHYRIA; CONTROLLED STUDY; DISEASE SEVERITY; DNA MODIFICATION; ENZYME ACTIVITY; ENZYME KINETICS; ERYTHROID CELL; FEMALE; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; GENETIC STABILITY; GENETIC TRANSDUCTION; HEME SYNTHESIS; HEMOLYSIS; HUMAN; HUMAN CELL; IN VITRO STUDY; INFANCY; INHERITANCE; LEUKAPHERESIS; METABOLISM; ONSET AGE; PATIENT CARE; PHOTODERMATOSIS; PROTEIN EXPRESSION; RETROVIRUS; STEM CELL TRANSPLANTATION; SYMPTOM;

EID: 0034992431     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.2001.0270     Document Type: Article

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