Fluorescence-based selection of gene-corrected hematopoietic stem and progenitor cells from acid sphingomyelinase-deficient mice: Implications for Niemann-Pick disease gene therapy and the development of improved stem cell gene transfer procedures

Blood

Volumn 93, Issue 1, 1999, Pages 80-86

  Erlich, Shai ^b   Miranda, Silvia R P ^b   Visser, Jan W M ^b   Dagan, Arie ^b   Gatt, Shimon ^b   Schuchman, Edward H ^a  

^a MOUNT SINAI SCHOOL OF MEDICINE   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

ANIMAL CELL; ANIMAL TISSUE; ARTICLE; BONE MARROW; CELL SELECTION; CONTROLLED STUDY; FETUS LIVER; FLUORESCENCE ACTIVATED CELL SORTER; GENE THERAPY; GENETIC TRANSDUCTION; HEMATOPOIETIC STEM CELL; MARKER GENE; MOUSE; NIEMANN PICK DISEASE; NONHUMAN; PRIORITY JOURNAL;

EID: 0032960253     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood.v93.1.80.401k28_80_86     Document Type: Article

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