Gene transfer of the uroporphyrinogen III synthase cDNA into haematopoietic progenitor cells in view of a future gene therapy in congenital erythropoietic porphyria

Journal of Inherited Metabolic Disease

Volumn 20, Issue 2, 1997, Pages 247-257

  Mazurier, F ^a   Moreau Gaudry, F ^a   Salesse, S ^a   Barbot, C ^a   Ged, C ^a   Reiffers, J ^a   De Verneuil, H ^a  

^a UNIVERSITÉ DE BORDEAUX   (France)

Author keywords

[No Author keywords available]

Indexed keywords

CD34 ANTIGEN; COMPLEMENTARY DNA; HEME; PORPHYRIN; UROPORPHYRINOGEN III SYNTHASE;

ALLOGENIC BONE MARROW TRANSPLANTATION; ANIMAL EXPERIMENT; ANIMAL MODEL; AUTOTRANSPLANTATION; BIOACCUMULATION; BLOOD TRANSFUSION; BONE MARROW; BONE MARROW CELL; CELL DIFFERENTIATION; CELL IMMORTALIZATION; CONFERENCE PAPER; CONGENITAL ERYTHROPOIETIC PORPHYRIA; DISEASE SEVERITY; ENZYME ACTIVITY; EXPRESSION VECTOR; FIBROBLAST; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; HEMATOPOIETIC STEM CELL; HEME SYNTHESIS; LYMPHOBLAST; METABOLIC DISORDER; MOLECULAR CLONING; NONHUMAN; RETROVIRUS; SKIN DISEASE; STEM CELL; TRANSGENE;

3T3 CELLS; ANIMALS; ANTIGENS, CD34; DNA, COMPLEMENTARY; ERYTHROID PROGENITOR CELLS; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER TECHNIQUES; HEMATOPOIETIC STEM CELLS; HUMANS; MICE; PORPHYRIA, ERYTHROPOIETIC; TRANSFORMATION, GENETIC; TUMOR CELLS, CULTURED; UROPORPHYRINOGEN III SYNTHETASE;

EID: 0030905555     PISSN: 01418955     EISSN: None     Source Type: Journal    
DOI: 10.1023/A:1005365008147     Document Type: Conference Paper

References (34)

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