Optimization of AAV expression cassettes to improve packaging capacity and transgene expression in neurons

Molecular Brain

Volumn 7, Issue 1, 2014, Pages

  Choi, Jun Hyeok ^a   Yu, Nam Kyung ^a   Baek, Gi Chul ^a   Bakes, Joseph ^a   Seo, Daekwan ^a,b   Nam, Hye Jin ^a   Baek, Sung Hee ^a   Lim, Chae Seok ^a   Lee, Yong Seok ^c   Kaang, Bong Kiun ^a  

^a Seoul National University   (South Korea)

^b Institute for Basic Science   (South Korea)

^c Chung Ang University   (South Korea)

Author keywords

Adeno associated virus; Neuron; SV40 late polyadenylation signal sequence; WPRE

Indexed keywords

ADENO ASSOCIATED VIRUS; ANIMAL CELL; ARTICLE; CONTROLLED STUDY; DNA MODIFICATION; DNA PACKAGING; GENE CASSETTE; GENE EXPRESSION; NERVE CELL; NONHUMAN; NUCLEOTIDE SEQUENCE; POLYADENYLATION; PRIORITY JOURNAL; SIGNAL TRANSDUCTION; TRANSGENE;

ANIMALS; BRAIN; DEPENDOVIRUS; GENE EXPRESSION; GENETIC TECHNIQUES; GENETIC VECTORS; HEK293 CELLS; HUMANS; MALE; MICE; MICE, INBRED C57BL; NEURONS; POLYADENYLATION; RATS; REGULATORY SEQUENCES, NUCLEIC ACID; SEQUENCE DELETION; TRANSGENES; VIRUS ASSEMBLY;

EID: 84898477363     PISSN: None     EISSN: 17566606     Source Type: Journal    
DOI: 10.1186/1756-6606-7-17     Document Type: Article

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