A shortened adeno-associated virus expression cassette for CFTR gene transfer to cystic fibrosis airway epithelia

Proceedings of the National Academy of Sciences of the United States of America

Volumn 102, Issue 8, 2005, Pages 2952-2957

  Ostedgaard, Lynda S ^a   Rokhlina, Tatiana ^a   Karp, Philip H ^a   Lashmit, Philip ^a   Afione, Sandra ^b   Schmidt, Michael ^b   Zabner, Joseph ^a   Stinski, Mark F ^a   Chiorini, Jay A ^b   Welsh, Michael J ^a  

^a UNIVERSITY OF IOWA   (United States)

^b NATIONAL INSTITUTE OF DENTAL AND CRANIOFACIAL RESEARCH   (United States)

Author keywords

CMV; Gene therapy; Promoter

Indexed keywords

PARVOVIRUS VECTOR; TRANSMEMBRANE CONDUCTANCE REGULATOR;

ADENOVIRUS 5; ARTICLE; CFTR GENE; CHLORIDE TRANSPORT; CYSTIC FIBROSIS; CYTOMEGALOVIRUS; ENHANCER REGION; GENE; GENE CASSETTE; GENE SEQUENCE; GENE TRANSFER; GENETIC TRANSDUCTION; HUMAN; HUMAN CELL; INTRON; NONHUMAN; PRIORITY JOURNAL; RESPIRATORY EPITHELIUM; TRANSGENE; VIRUS EXPRESSION;

CELLS, CULTURED; CHLORIDES; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; DEPENDOVIRUS; ENHANCER ELEMENTS (GENETICS); EPITHELIUM; GENE THERAPY; GENE TRANSFER, HORIZONTAL; GENETIC VECTORS; HUMANS; INTRONS; ION TRANSPORT; PROMOTER REGIONS (GENETICS); TRACHEA;

EID: 20044381100     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.0409845102     Document Type: Article

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