Monogenic diseases that can be cured by liver transplantation

Journal of Hepatology

Volumn 59, Issue 3, 2013, Pages 595-612

  Fagiuoli, Stefano ^a   Daina, Erica ^b   D'Antiga, Lorenzo ^a   Colledan, Michele ^a   Remuzzi, Giuseppe ^a,b  

^a PAPA GIOVANNI XXIII HOSPITAL   (Italy)

^b MARIO NEGRI INSTITUTE FOR PHARMACOLOGICAL RESEARCH   (Italy)

Author keywords

Genetic diseases Inborn; Liver transplantation; Metabolic diseases; Rare diseases; Surgical gene therapy

Indexed keywords

ACIDURIA; ALAGILLE SYNDROME; ARTICLE; CHOLESTASIS; CRIGLER NAJJAR SYNDROME; FAMILIAL AMYLOID POLYNEUROPATHY; GENE THERAPY; GENETIC DISORDER; HEMOCHROMATOSIS; HEMOLYTIC UREMIC SYNDROME; HUMAN; INTRAHEPATIC CHOLESTASIS; IRON CHELATION; LIVER DISEASE; LIVER TRANSPLANTATION; MONOGENIC DISORDER; OXALOSIS 1; PRIORITY JOURNAL; PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS; TYROSINEMIA; UREA CYCLE DISORDER; WILSON DISEASE;

GENETIC DISEASES; INBORN; LIVER TRANSPLANTATION; METABOLIC DISEASES; RARE DISEASES; SURGICAL GENE THERAPY;

ADULT; CHILD; FEMALE; GENETIC DISEASES, INBORN; GENETIC THERAPY; HUMANS; LIVER DISEASES; LIVER TRANSPLANTATION; MALE;

EID: 84882814879     PISSN: 01688278     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.jhep.2013.04.004     Document Type: Note

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