Is it better than it seems or just good enough? The tafamidis saga

Muscle and Nerve

Volumn 46, Issue 6, 2012, Pages 14-

  De Carvalho, Mamede ^a,b  

^a INSTITUTO DE MEDICINA MOLECULAR   (Portugal)

^b HOSPITAL DE SANTA MARIA   (Portugal)

Author keywords

[No Author keywords available]

Indexed keywords

CREATININE; FX 003; PREALBUMIN; TAFAMIDIS; UNCLASSIFIED DRUG;

AUTOSOMAL DOMINANT DISORDER; BODY MASS; CREATININE CLEARANCE; DISEASE COURSE; DRUG APPROVAL; DRUG EFFICACY; EDITORIAL; FAMILIAL AMYLOID POLYNEUROPATHY; GENETIC VARIABILITY; HEART ARRHYTHMIA; HUMAN; HYPERPNEA; IMMUNOSUPPRESSIVE TREATMENT; INFECTION; KIDNEY FAILURE; LIVER FUNCTION; LIVER TRANSPLANTATION; METABOLIC DISORDER; MULTICENTER STUDY (TOPIC); NAMED INVENTORIES, QUESTIONNAIRES AND RATING SCALES; NEUROPATHY IMPAIRMENT SCORE LOWER LIMB; NORFOLK QUALITY OF LIFE DIABETIC NEUROPATHY SCALE; PHASE 2 CLINICAL TRIAL (TOPIC); PHASE 3 CLINICAL TRIAL (TOPIC); PLASMAPHERESIS; PRIORITY JOURNAL; RANDOMIZED CONTROLLED TRIAL (TOPIC); SENSORY DYSFUNCTION; SURGICAL MORTALITY; SURVIVAL RATE; TRANSTHYRETIN TYPE FAMILIAL AMYLOID POLYNEUROPATHY; TREATMENT OUTCOME;

EID: 84870174295     PISSN: 0148639X     EISSN: 10974598     Source Type: Journal    
DOI: 10.1002/mus.23665     Document Type: Editorial

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