Lifelong elimination of hyperbilirubinemia in the Gunn rat with a single injection of helper-dependent adenoviral vector

Proceedings of the National Academy of Sciences of the United States of America

Volumn 102, Issue 11, 2005, Pages 3930-3935

  Toietta, Gabriele ^a,c   Mane, Viraj P ^a   Norona, Wilma S ^b   Finegold, Milton J ^a   Ng, Philip ^a   McDonagh, Antony F ^b   Beaudet, Arthur L ^a   Lee, Brendan ^a  

^a BAYLOR COLLEGE OF MEDICINE   (United States)

^b UNIVERSITY OF CALIFORNIA   (United States)

^c LABORATORIO DI PATOLOGIA VASCOLARE   (Italy)

Author keywords

Adenovirus; Bilirubin; Gene therapy

Indexed keywords

ADENOVIRUS VECTOR; ALANINE AMINOTRANSFERASE; BILIRUBIN; BILIRUBIN GLUCURONIDE; CELL PROTEIN; GLUCURONOSYLTRANSFERASE 1A1; LIVER ENZYME; VIRUS DNA;

ANIMAL MODEL; ARTICLE; BILE; BILIRUBIN BLOOD LEVEL; BLOOD SAMPLING; CHRONIC TOXICITY; CRIGLER NAJJAR SYNDROME; DNA SEQUENCE; ENDOPLASMIC RETICULUM; FEMALE; GENE EXPRESSION; GENE THERAPY; HIGH PERFORMANCE LIQUID CHROMATOGRAPHY; HYPERBILIRUBINEMIA; KERNICTERUS; NONHUMAN; NUCLEOTIDE SEQUENCE; PHOTOTHERAPY; PRIORITY JOURNAL; RAT; TRANSGENE;

ADENOVIRIDAE; ALANINE TRANSAMINASE; ANIMALS; BILIRUBIN; DNA; GENE THERAPY; GENETIC VECTORS; GLUCURONOSYLTRANSFERASE; HUMANS; HYPERBILIRUBINEMIA; RATS; RATS, GUNN; RNA, MESSENGER;

EID: 15244353548     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.0500930102     Document Type: Article

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