Deferiprone for the treatment of Friedreich's ataxia

Journal of Neurochemistry

Volumn 126, Issue SUPPL.1, 2013, Pages 142-146

  Pandolfo, Massimo ^a   Hausmann, Laura ^b  

^a ERASME HOSPITAL   (Belgium)

^b UNIVERSITY HOSPITAL RWTH AACHEN   (Germany)

Author keywords

clinical study; Deferiprone; frataxin; Friedreich's ataxia (FRDA)

Indexed keywords

APOTRANSFERRIN; DEFERIPRONE; DEFEROXAMINE; FRATAXIN; IDEBENONE; IRON SULFUR PROTEIN; PLACEBO;

AGRANULOCYTOSIS; CELL PROLIFERATION; CONCENTRATION RESPONSE; FRIEDREICH ATAXIA; HUMAN; IRON METABOLISM; IRON OVERLOAD; MITOCHONDRIAL MEMBRANE POTENTIAL; NONHUMAN; OPEN STUDY; PHASE 2 CLINICAL TRIAL (TOPIC); PRIORITY JOURNAL; PROTEIN SYNTHESIS INHIBITION; RANDOMIZED CONTROLLED TRIAL (TOPIC); REVIEW;

CLINICAL STUDY; DEFERIPRONE; FRATAXIN; FRIEDREICH'S ATAXIA (FRDA);

ANIMALS; CLINICAL TRIALS AS TOPIC; DRUG EVALUATION, PRECLINICAL; FRIEDREICH ATAXIA; HUMANS; IRON; IRON CHELATING AGENTS; IRON-BINDING PROTEINS; PYRIDONES; SULFUR;

EID: 84880356885     PISSN: 00223042     EISSN: 14714159     Source Type: Journal    
DOI: 10.1111/jnc.12300     Document Type: Review

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