Targeted gene addition of microdystrophin in mice skeletal muscle via human myoblast transplantation

Molecular Therapy Nucleic Acids

Volumn 2, Issue , 2013, Pages

  Benabdallah, Basma F ^a   Duval, Arnaud ^a   Rousseau, Joel ^b   Chapdelaine, Pierre ^b   Holmes, Michael C ^c   Haddad, Eli ^d   Tremblay, Jacques P ^b   Beauséjour, Christian M ^a  

^a UNIVERSITY OF MONTREAL   (Canada)

^b LAVAL UNIVERSITY   (Canada)

^c SANGAMO BIOSCIENCES INC   (United States)

^d UNIVERSITÉ DE MONTRÉAL   (Canada)

Author keywords

dystrophin; gene addition; gene therapy; myoblast; zinc finger nuclease

Indexed keywords

6 O METHYLGUANINE; ADENOVIRUS VECTOR; CHEMOKINE RECEPTOR CCR5; DNA; DNA METHYLTRANSFERASE; DYSTROPHIN; ENHANCED GREEN FLUORESCENT PROTEIN; LENTIVIRUS VECTOR; MICRODYSTROPHIN; UNCLASSIFIED DRUG; ZINC FINGER NUCLEASE;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL THERAPY; CONTROLLED STUDY; GENE; GENE LOCUS; GENE TARGETING; HUMAN; HUMAN CELL; IMMUNE DEFICIENCY; IN VITRO STUDY; IN VIVO STUDY; MALE; MITOGENESIS; MOUSE; MUSCLE DISEASE; MUSCLE TRANSPLANTATION; MYOBLAST; MYOBLAST TRANSPLANTATION; MYOTUBE; NONHUMAN; PRIORITY JOURNAL; SKELETAL MUSCLE; TIBIALIS ANTERIOR MUSCLE;

EID: 84878828595     PISSN: None     EISSN: 21622531     Source Type: Journal    
DOI: 10.1038/mtna.2012.55     Document Type: Article

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