Targeting Photoreceptors via Intravitreal Delivery Using Novel, Capsid-Mutated AAV Vectors

PLoS ONE

Volumn 8, Issue 4, 2013, Pages

  Kay, Christine N ^a   Ryals, Renee C ^a   Aslanidi, George V ^a   Min, Seok Hong ^a   Ruan, Qing ^a   Sun, Jingfen ^a   Dyka, Frank M ^a   Kasuga, Daniel ^a   Ayala, Andrea E ^a   Van Vliet, Kim ^a   Agbandje McKenna, Mavis ^a   Hauswirth, William W ^a   Boye, Sanford L ^a   Boye, Shannon E ^a  

^a UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; COMPLEMENTARY DNA; MICRORNA; MICRORNA 181; PHENYLALANINE; RHODOPSIN; RHODOPSIN KINASE; THREONINE; TYROSINE; UNCLASSIFIED DRUG; VALINE;

ADENO ASSOCIATED VIRUS; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONTROLLED STUDY; FLUORESCENCE ACTIVATED CELL SORTING; FUSION GENE; GENE EXPRESSION REGULATION; MOUSE; NONHUMAN; PHOTORECEPTOR; PROMOTER REGION; PROTEIN EXPRESSION; RNA SEQUENCE; SIGNAL TRANSDUCTION; TRANSGENIC MOUSE; VIRAL GENE DELIVERY SYSTEM; VIRUS CAPSID;

ANIMALS; CAPSID; CELL LINE; CHICKENS; DEPENDOVIRUS; G-PROTEIN-COUPLED RECEPTOR KINASE 1; GENE EXPRESSION; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; INTRAVITREAL INJECTIONS; MICE; MICE, INBRED C57BL; MICE, TRANSGENIC; MICRORNAS; MUTATION; PHOTORECEPTOR CELLS, VERTEBRATE; PROMOTER REGIONS, GENETIC; SEROTYPING; TRANSDUCTION, GENETIC; TRANSGENES; VIRAL TROPISM;

MIRIDAE; MUS; MUS MUSCULUS;

EID: 84876860169     PISSN: None     EISSN: 19326203     Source Type: Journal    
DOI: 10.1371/journal.pone.0062097     Document Type: Article

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