메뉴 건너뛰기




Volumn 21, Issue 4, 2008, Pages 583-593

Gene therapy using adeno-associated virus vectors

Author keywords

[No Author keywords available]

Indexed keywords

ADALIMUMAB; ASPARTOACYLASE; DYSTROPHIN; EYE PROTEIN; FC RECEPTOR; GLUTAMATE DECARBOXYLASE 65; GRANULOCYTE MACROPHAGE COLONY STIMULATING FACTOR; MINIDYSTROPHIN; NERVE GROWTH FACTOR BETA SUBUNIT; NEUROPEPTIDE Y; NEURTURIN; PARVOVIRUS VECTOR; PLATELET DERIVED GROWTH FACTOR RECEPTOR; PROTEIN CLN2; PROTEOHEPARAN SULFATE; RETINAL PIGMENT EPITHELIUM SPECIFIC PROTEIN 65; SARCOGLYCAN; SARCOPLASMIC RETICULUM CALCIUM TRANSPORTING ADENOSINE TRIPHOSPHATASE; SARCOPLASMIC RETICULUM CALCIUM TRANSPORTING ADENOSINE TRIPHOSPHATASE 2A; SERINE PROTEINASE; SIALIC ACID; TRANSMEMBRANE CONDUCTANCE REGULATOR; TRYPSIN INHIBITOR; TUMOR NECROSIS FACTOR RECEPTOR; UNCLASSIFIED DRUG;

EID: 54249126862     PISSN: 08938512     EISSN: None     Source Type: Journal    
DOI: 10.1128/CMR.00008-08     Document Type: Review
Times cited : (716)

References (80)
  • 3
    • 33748945422 scopus 로고    scopus 로고
    • The 37/67-kilodalton laminin receptor is a receptor for adeno-associated virus serotypes 8, 2, 3, and 9
    • Akache, B., D. Grimm, K. Pandy, S. R. Yant, Y. Xu, and M. A. Kay. 2006. The 37/67-kilodalton laminin receptor is a receptor for adeno-associated virus serotypes 8, 2, 3, and 9. J. Virol. 80:9831-9836.
    • (2006) J. Virol , vol.80 , pp. 9831-9836
    • Akache, B.1    Grimm, D.2    Pandy, K.3    Yant, S.R.4    Xu, Y.5    Kay, M.A.6
  • 4
    • 33846324384 scopus 로고    scopus 로고
    • A two-hybrid screen identifies cathepsin B and L as uncoating factors for adeno-associated virus 2 and 8
    • Akache, B., D. Grimm, X. Shen, S. Fuess, S. R. Yant, D. S. Glazer, J. Park, and M. A. Kay. 2007. A two-hybrid screen identifies cathepsin B and L as uncoating factors for adeno-associated virus 2 and 8. Mol. Ther. 15:330-339.
    • (2007) Mol. Ther , vol.15 , pp. 330-339
    • Akache, B.1    Grimm, D.2    Shen, X.3    Fuess, S.4    Yant, S.R.5    Glazer, D.S.6    Park, J.7    Kay, M.A.8
  • 5
    • 0036166251 scopus 로고    scopus 로고
    • A deviant immune response to viral proteins and transgene product is generated on subretinal administration of adenovirus and adeno-associated virus
    • Anand, V., B. Duffy, Z. Yang, N. S. Dejneka, A. M. Maguire, and J. Bennett. 2002. A deviant immune response to viral proteins and transgene product is generated on subretinal administration of adenovirus and adeno-associated virus. Mol. Ther. 5:125-132.
    • (2002) Mol. Ther , vol.5 , pp. 125-132
    • Anand, V.1    Duffy, B.2    Yang, Z.3    Dejneka, N.S.4    Maguire, A.M.5    Bennett, J.6
  • 6
    • 33646821738 scopus 로고    scopus 로고
    • Metabolic biotinylation provides a unique platform for the purification and targeting of multiple AAV vectors serotypes
    • Arnold, G. S., A. K. Sasser, M. D. Stachler, and J. S. Bartlett. 2006. Metabolic biotinylation provides a unique platform for the purification and targeting of multiple AAV vectors serotypes. Mol. Ther. 14:97-106.
    • (2006) Mol. Ther , vol.14 , pp. 97-106
    • Arnold, G.S.1    Sasser, A.K.2    Stachler, M.D.3    Bartlett, J.S.4
  • 7
    • 33748494015 scopus 로고    scopus 로고
    • Adeno-associated virus type 2 contains an integrin α5β1 binding domain essential for viral cell entry
    • Asokan, A., J. B. Hamra, L. Govindasamy, M. Agbandje-McKenna, and R. J. Samulski. 2006. Adeno-associated virus type 2 contains an integrin α5β1 binding domain essential for viral cell entry. J. Virol. 80:8961-8969.
    • (2006) J. Virol , vol.80 , pp. 8961-8969
    • Asokan, A.1    Hamra, J.B.2    Govindasamy, L.3    Agbandje-McKenna, M.4    Samulski, R.J.5
  • 8
    • 0033007934 scopus 로고    scopus 로고
    • Targeted adeno-associated virus vector transduction of nonpermissive cells mediated by a bispecific F(ab′gamma)2 antibody
    • Bartlett, J. S., J. Kleinschmidt, R. C. Boucher, and R. J. Samulski. 1999. Targeted adeno-associated virus vector transduction of nonpermissive cells mediated by a bispecific F(ab′gamma)2 antibody. Nat. Biotechnol. 17:181-186.
    • (1999) Nat. Biotechnol , vol.17 , pp. 181-186
    • Bartlett, J.S.1    Kleinschmidt, J.2    Boucher, R.C.3    Samulski, R.J.4
  • 9
    • 0033998692 scopus 로고    scopus 로고
    • Infectious entry pathways of adeno-associated virus and adeno-associated virus vectors
    • Bartlett, J. S., R. Wilcher, and R. J. Samulski. 2000. Infectious entry pathways of adeno-associated virus and adeno-associated virus vectors. J. Virol. 74:2777-2785.
    • (2000) J. Virol , vol.74 , pp. 2777-2785
    • Bartlett, J.S.1    Wilcher, R.2    Samulski, R.J.3
  • 10
    • 13444310872 scopus 로고    scopus 로고
    • Mutational analysis of narrow pores at the fivefold symmetry axes of adeno-associated virus type 2 capsids reveal a dual role in genome packaging and activation of phospholipase A2 activity
    • Bleker, S., F. Sonntage, and J. A. Kleinschmidt. 2005. Mutational analysis of narrow pores at the fivefold symmetry axes of adeno-associated virus type 2 capsids reveal a dual role in genome packaging and activation of phospholipase A2 activity. J. Virol. 79:2528-2540.
    • (2005) J. Virol , vol.79 , pp. 2528-2540
    • Bleker, S.1    Sonntage, F.2    Kleinschmidt, J.A.3
  • 11
    • 0032977833 scopus 로고    scopus 로고
    • Induction of immunity to antigens expressed by recombinant adeno-associated virus depends on route of administration
    • Brockstedt, D. G., G. M. Podsakoff, L. Fong, G. Kurtzman, W. Mueller-Ruchholtz, and E. G. Engleman. 1999. Induction of immunity to antigens expressed by recombinant adeno-associated virus depends on route of administration. Clin. Immunol. 92:67-75.
    • (1999) Clin. Immunol , vol.92 , pp. 67-75
    • Brockstedt, D.G.1    Podsakoff, G.M.2    Fong, L.3    Kurtzman, G.4    Mueller-Ruchholtz, W.5    Engleman, E.G.6
  • 14
    • 0033977047 scopus 로고    scopus 로고
    • Humoral immunity to adeno-associated virus type 2 vectors following administration to murine and non-human primate muscle
    • Chirmule, N., W. Xiao, A. Truneh, M. A. Schnell, J. V. Hughes, P. Zoltick, and J. M. Wilson. 2000. Humoral immunity to adeno-associated virus type 2 vectors following administration to murine and non-human primate muscle. J. Virol. 74:2420-2425.
    • (2000) J. Virol , vol.74 , pp. 2420-2425
    • Chirmule, N.1    Xiao, W.2    Truneh, A.3    Schnell, M.A.4    Hughes, J.V.5    Zoltick, P.6    Wilson, J.M.7
  • 15
    • 0032737034 scopus 로고    scopus 로고
    • Dynamin is required for recombinant adeno-associated virus type 2 infection
    • Duan, D., Q. Li, A. W. Kao, Y. Yue, J. E. Pessin, and J. F. Engelhardt. 1999. Dynamin is required for recombinant adeno-associated virus type 2 infection. J. Virol. 73:10371-10376.
    • (1999) J. Virol , vol.73 , pp. 10371-10376
    • Duan, D.1    Li, Q.2    Kao, A.W.3    Yue, Y.4    Pessin, J.E.5    Engelhardt, J.F.6
  • 16
    • 0034712849 scopus 로고    scopus 로고
    • Adeno-associated virus site-specifically integrates into a muscle-specific DNA region
    • Dutheil, N., F. Shi, T. Dupressoir, and R. M. Linden. 2000. Adeno-associated virus site-specifically integrates into a muscle-specific DNA region. Proc. Natl. Acad. Sci. USA 97:4862-4866.
    • (2000) Proc. Natl. Acad. Sci. USA , vol.97 , pp. 4862-4866
    • Dutheil, N.1    Shi, F.2    Dupressoir, T.3    Linden, R.M.4
  • 18
    • 33645100006 scopus 로고    scopus 로고
    • A 16bp rep binding element is sufficient for mediating rep-dependent integration into AAVS1
    • Feng, D., J. Chen, Y. Yue, H. Zhu, J. Xue, and W. W. Jia. 2006. A 16bp rep binding element is sufficient for mediating rep-dependent integration into AAVS1. J. Mol. Biol. 358:38-45.
    • (2006) J. Mol. Biol , vol.358 , pp. 38-45
    • Feng, D.1    Chen, J.2    Yue, Y.3    Zhu, H.4    Xue, J.5    Jia, W.W.6
  • 19
    • 0029923638 scopus 로고    scopus 로고
    • Second-strand synthesis is a rate-limiting step for efficient transduction by recombinant adeno-associated virus vectors
    • Ferrari, F. K., T. Samulski, T. Shenk, and R. J. Samulski. 1996. Second-strand synthesis is a rate-limiting step for efficient transduction by recombinant adeno-associated virus vectors. J. Virol. 70:3227-3234.
    • (1996) J. Virol , vol.70 , pp. 3227-3234
    • Ferrari, F.K.1    Samulski, T.2    Shenk, T.3    Samulski, R.J.4
  • 20
    • 29544433568 scopus 로고    scopus 로고
    • Gene therapy of severe combined immunodeficiency disease: Proof of efficiency and safety issues
    • In French
    • Fischer, A., S. Hacein-Bey-Abina, C. Lagresle, A. Garrigue, and M. Cavazana-Calvo. 2005. Gene therapy of severe combined immunodeficiency disease: proof of efficiency and safety issues. Bull. Acad. Natl. Med. 189:779-785. (In French.)
    • (2005) Bull. Acad. Natl. Med , vol.189 , pp. 779-785
    • Fischer, A.1    Hacein-Bey-Abina, S.2    Lagresle, C.3    Garrigue, A.4    Cavazana-Calvo, M.5
  • 24
  • 25
    • 33645223689 scopus 로고    scopus 로고
    • Viral serotype and transgene sequence overlapping adeno-associated virus (AAV) vector-mediated gene transfer in skeletal muscle
    • Ghosh, A., Y. Yue, and D. Dongsheng. 2006. Viral serotype and transgene sequence overlapping adeno-associated virus (AAV) vector-mediated gene transfer in skeletal muscle. J. Gen. Med. 8:298-305.
    • (2006) J. Gen. Med , vol.8 , pp. 298-305
    • Ghosh, A.1    Yue, Y.2    Dongsheng, D.3
  • 26
    • 0028033782 scopus 로고
    • Site-specific integration by adeno-associated virus is directed by a cellular DNA sequence
    • Giraud, C., E. Winocour, and K. I. Berns. 1994. Site-specific integration by adeno-associated virus is directed by a cellular DNA sequence. Proc. Natl. Acad. Sci. USA 91:10039-10043.
    • (1994) Proc. Natl. Acad. Sci. USA , vol.91 , pp. 10039-10043
    • Giraud, C.1    Winocour, E.2    Berns, K.I.3
  • 27
    • 0036246727 scopus 로고    scopus 로고
    • The VP1 capsid protein of adeno-associated virus type 2 is carrying a phospholipase A2 domain required for virus infectivity
    • Girod, A., C. E. Wobus, Z. Zadori, M. Ried, K. Leike, P. Tijssen, J. A. Kleinschmidt, and M. Hallek. 2002. The VP1 capsid protein of adeno-associated virus type 2 is carrying a phospholipase A2 domain required for virus infectivity. J. Gen. Virol. 83:973-978.
    • (2002) J. Gen. Virol , vol.83 , pp. 973-978
    • Girod, A.1    Wobus, C.E.2    Zadori, Z.3    Ried, M.4    Leike, K.5    Tijssen, P.6    Kleinschmidt, J.A.7    Hallek, M.8
  • 28
    • 0031743947 scopus 로고    scopus 로고
    • Successful readministration of adeno-associated virus vectors to the mouse lung requires transient immunosuppression during the initial exposure
    • Halbert, C. L., T. A. Standaert, C. B. Wilson, and A. D. Miller. 1998. Successful readministration of adeno-associated virus vectors to the mouse lung requires transient immunosuppression during the initial exposure. J. Virol. 72:9795-9805.
    • (1998) J. Virol , vol.72 , pp. 9795-9805
    • Halbert, C.L.1    Standaert, T.A.2    Wilson, C.B.3    Miller, A.D.4
  • 29
    • 0034759535 scopus 로고    scopus 로고
    • Infection of purified nuclei by adeno-associated virus 2
    • Hansen, J., K. Qing, and A. Srivastava. 2001. Infection of purified nuclei by adeno-associated virus 2. Mol. Ther. 4:289-296.
    • (2001) Mol. Ther , vol.4 , pp. 289-296
    • Hansen, J.1    Qing, K.2    Srivastava, A.3
  • 30
    • 10044222300 scopus 로고    scopus 로고
    • Intracellular viral processing, not single-stranded DNA accumulation, is crucial for recombinant adeno-associated virus transduction
    • Hauck, B., W. Zhao, K. High, and W. Xiao. 2004. Intracellular viral processing, not single-stranded DNA accumulation, is crucial for recombinant adeno-associated virus transduction. J. Virol. 78:13678- 13686.
    • (2004) J. Virol , vol.78 , pp. 13678-13686
    • Hauck, B.1    Zhao, W.2    High, K.3    Xiao, W.4
  • 31
    • 0030902985 scopus 로고    scopus 로고
    • Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus
    • Herzog, R. W., J. N. Hagstrom, S. H. Kung, S. J. Tai, J. M. Wilson, K. J. Fisher, and K. A. High. 1997. Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus. Proc. Natl. Acad. Sci. USA 94:5804-5809.
    • (1997) Proc. Natl. Acad. Sci. USA , vol.94 , pp. 5804-5809
    • Herzog, R.W.1    Hagstrom, J.N.2    Kung, S.H.3    Tai, S.J.4    Wilson, J.M.5    Fisher, K.J.6    High, K.A.7
  • 33
    • 36849053913 scopus 로고    scopus 로고
    • Gene transfer an unlikely contributor to patient's death
    • Kaiser, J. 2007. Gene transfer an unlikely contributor to patient's death. Science 318:1535.
    • (2007) Science , vol.318 , pp. 1535
    • Kaiser, J.1
  • 39
    • 24944551962 scopus 로고    scopus 로고
    • Spliceosome-mediated RNA trans-splicing with recombinant adeno-associated virus partially restores cystic fibrosis transmembrane conductance regulator function to polarized human cystic fibrosis airway epithelial cells
    • Liu, X., M. Luo, L. N. Zhang, Z. Yan, R. Zak, W. Ding, S. G. Mansfield, L. G. Mitchell, and J. F. Engelhardt. 2005. Spliceosome-mediated RNA trans-splicing with recombinant adeno-associated virus partially restores cystic fibrosis transmembrane conductance regulator function to polarized human cystic fibrosis airway epithelial cells. Hum. Gene Ther. 16:1116-1123.
    • (2005) Hum. Gene Ther , vol.16 , pp. 1116-1123
    • Liu, X.1    Luo, M.2    Zhang, L.N.3    Yan, Z.4    Zak, R.5    Ding, W.6    Mansfield, S.G.7    Mitchell, L.G.8    Engelhardt, J.F.9
  • 40
    • 0032031816 scopus 로고    scopus 로고
    • Transient immunosuppression allows transgene expression following readministration of adeno-associated viral vectors
    • Manning, W. C., S. Zhou, M. P. Bland, J. A. Escobedo, and V. Dwarki. 1998. Transient immunosuppression allows transgene expression following readministration of adeno-associated viral vectors. Hum. Gene Ther. 9:477-485.
    • (1998) Hum. Gene Ther , vol.9 , pp. 477-485
    • Manning, W.C.1    Zhou, S.2    Bland, M.P.3    Escobedo, J.A.4    Dwarki, V.5
  • 42
    • 33644820684 scopus 로고    scopus 로고
    • Manno, C. S., G. F. Pierce, V. R. Arruda, B. Glader, M. Ragni, J. J. Rasko, M. C. Ozelo, K. Hoots, P. Blatt, B. Konkle, M. Dake, R. Kaye, M. Razavi, A. Zajko, J. Zehnder, P. K. Rustagi, H. Nakai, A. Chew, D. Leonard, J. F. Wright, R. R. Lessard, J. M. Sommer, M. Tigges, B. Sabatino, A. Luk, H. Jiang, F. Mingossi, L. Couto, H. C. Ertl, K. A. High, and M. A. Kay. 2006. Successful transduction of liver in hemophilia by AAV-factor IX and limitations imposed by the host immune response. Nat. Med. 12:342-347.
    • Manno, C. S., G. F. Pierce, V. R. Arruda, B. Glader, M. Ragni, J. J. Rasko, M. C. Ozelo, K. Hoots, P. Blatt, B. Konkle, M. Dake, R. Kaye, M. Razavi, A. Zajko, J. Zehnder, P. K. Rustagi, H. Nakai, A. Chew, D. Leonard, J. F. Wright, R. R. Lessard, J. M. Sommer, M. Tigges, B. Sabatino, A. Luk, H. Jiang, F. Mingossi, L. Couto, H. C. Ertl, K. A. High, and M. A. Kay. 2006. Successful transduction of liver in hemophilia by AAV-factor IX and limitations imposed by the host immune response. Nat. Med. 12:342-347.
  • 43
    • 0036315299 scopus 로고    scopus 로고
    • Immunological aspects of recombinant adeno-associated virus delivery to the mammalian brain
    • Mastakov, M. Y., K. Baer, C. W. Symes, C. B. Leichtlein, R. M. Kotin, and M. J. During. 2002. Immunological aspects of recombinant adeno-associated virus delivery to the mammalian brain. J. Virol. 76:8446-8454.
    • (2002) J. Virol , vol.76 , pp. 8446-8454
    • Mastakov, M.Y.1    Baer, K.2    Symes, C.W.3    Leichtlein, C.B.4    Kotin, R.M.5    During, M.J.6
  • 44
    • 0034882826 scopus 로고    scopus 로고
    • Self complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis
    • McCarty, D. M., P. E. Monahan, and R. J. Samulski. 2001. Self complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis. Gene Ther. 16:1248-1254.
    • (2001) Gene Ther , vol.16 , pp. 1248-1254
    • McCarty, D.M.1    Monahan, P.E.2    Samulski, R.J.3
  • 46
    • 10744227749 scopus 로고    scopus 로고
    • Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis; a multicenter, double-blind placebo-controlled trial
    • Moss, R. B., D. Rodman, L. T. Spencer, M. L. Aitken, P. L. Zeitlin, D. Waltz, C. Milla, A. S. Brody, J. P. Clancy, B. Ramsey, N. Hamblett, and D. Milla. 2004. Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis; a multicenter, double-blind placebo-controlled trial. Chest 125:509-521.
    • (2004) Chest , vol.125 , pp. 509-521
    • Moss, R.B.1    Rodman, D.2    Spencer, L.T.3    Aitken, M.L.4    Zeitlin, P.L.5    Waltz, D.6    Milla, C.7    Brody, A.S.8    Clancy, J.P.9    Ramsey, B.10    Hamblett, N.11    Milla, D.12
  • 47
    • 37549003977 scopus 로고    scopus 로고
    • Prolonged susceptibility to antibody-mediated neutralization for adeno-associated vectors targeted to the liver
    • Murphy, S. L., H. Li, S. Zhou, A. Schlachterman, and K. High. 2008. Prolonged susceptibility to antibody-mediated neutralization for adeno-associated vectors targeted to the liver. Mol. Ther. 16:138-145.
    • (2008) Mol. Ther , vol.16 , pp. 138-145
    • Murphy, S.L.1    Li, H.2    Zhou, S.3    Schlachterman, A.4    High, K.5
  • 48
    • 0031014018 scopus 로고    scopus 로고
    • The adeno-associated virus (AAV) Rep protein acts as both a repressor and an activator to regulate AAV transcription during a productive infection
    • Pereira, D. J., D. M. McCarty, and N. Muzyczka. 1997. The adeno-associated virus (AAV) Rep protein acts as both a repressor and an activator to regulate AAV transcription during a productive infection. J. Virol. 71:1079-1088.
    • (1997) J. Virol , vol.71 , pp. 1079-1088
    • Pereira, D.J.1    McCarty, D.M.2    Muzyczka, N.3
  • 49
    • 0037125986 scopus 로고    scopus 로고
    • A p5 integration efficiency element mediates rep-dependent integration into AAVS1 at chromosome 19
    • Philpott, N. J., J. Gomos, K. I. Berns, and E. Falck-Pedersen. 2002. A p5 integration efficiency element mediates rep-dependent integration into AAVS1 at chromosome 19. Proc. Natl. Acad. Sci. USA 99:12381-12385.
    • (2002) Proc. Natl. Acad. Sci. USA , vol.99 , pp. 12381-12385
    • Philpott, N.J.1    Gomos, J.2    Berns, K.I.3    Falck-Pedersen, E.4
  • 50
    • 0036893196 scopus 로고    scopus 로고
    • Ponnazhagen, S., G. Mahendra, S. Kumar, J. A. Thompson, and M. Castillas, Jr. 2002. Conjugate-based targeting of recombinant adeno-associated virus type 2 vector using avidin-linked ligands. J. Virol. 76:12900-12907.
    • Ponnazhagen, S., G. Mahendra, S. Kumar, J. A. Thompson, and M. Castillas, Jr. 2002. Conjugate-based targeting of recombinant adeno-associated virus type 2 vector using avidin-linked ligands. J. Virol. 76:12900-12907.
  • 51
    • 0034849529 scopus 로고    scopus 로고
    • Adeno-associated virus type 2-mediated gene transfer: Role of cellular FKBP52 protein in transgene expression
    • Qing, K., J. Hansen, K. A. Weigel-Kelley, M. Tan, S. Zhou, and A. Srivastava. 2001. Adeno-associated virus type 2-mediated gene transfer: role of cellular FKBP52 protein in transgene expression. J. Virol. 75:8968-8976.
    • (2001) J. Virol , vol.75 , pp. 8968-8976
    • Qing, K.1    Hansen, J.2    Weigel-Kelley, K.A.3    Tan, M.4    Zhou, S.5    Srivastava, A.6
  • 52
    • 0037322124 scopus 로고    scopus 로고
    • Adeno-associated virus type 2-mediated gene transfer: Role of cellular T-cell protein tyrosine phosphatase in transgene expression in established cell lines in vitro and transgenic mice in vivo
    • Qing, K., W. Li, L. Zhong, M. Tan, J. Hansen, K. A. Wiegel-Kelly, L. Chen, M. C. Yoder, and A. Srivastava. 2003. Adeno-associated virus type 2-mediated gene transfer: role of cellular T-cell protein tyrosine phosphatase in transgene expression in established cell lines in vitro and transgenic mice in vivo. J. Virol. 77:2741-2746.
    • (2003) J. Virol , vol.77 , pp. 2741-2746
    • Qing, K.1    Li, W.2    Zhong, L.3    Tan, M.4    Hansen, J.5    Wiegel-Kelly, K.A.6    Chen, L.7    Yoder, M.C.8    Srivastava, A.9
  • 53
    • 0033010884 scopus 로고    scopus 로고
    • Human fibroblast growth factor 1 is a co-receptor for infection by adeno-associated virus 2
    • Qing, K., C. Mah, J. Hansen, S. Zhou, V. Dwarki, and A. Srivastava. 1999. Human fibroblast growth factor 1 is a co-receptor for infection by adeno-associated virus 2. Nat. Med. 5:71-77.
    • (1999) Nat. Med , vol.5 , pp. 71-77
    • Qing, K.1    Mah, C.2    Hansen, J.3    Zhou, S.4    Dwarki, V.5    Srivastava, A.6
  • 54
    • 4644285407 scopus 로고    scopus 로고
    • Site-specific integration of functional transgenes into the human genome by adeno/AAV hybrid vectors
    • Recchia, A., L. Perani, D. Sartori, C. Olgiati, and F. Malvilio. 2004. Site-specific integration of functional transgenes into the human genome by adeno/AAV hybrid vectors. Mol. Ther. 10:660-670.
    • (2004) Mol. Ther , vol.10 , pp. 660-670
    • Recchia, A.1    Perani, L.2    Sartori, D.3    Olgiati, C.4    Malvilio, F.5
  • 55
    • 12244311258 scopus 로고    scopus 로고
    • Efficient trans-splicing in the retina expands the utility of adeno-associated virus as a vector for gene therapy
    • Reich, S. J., A. Auricchio, M. Hildinger, E. Glover, A. M. Maguire, J. M. Wilson, and J. Bennett. 2003. Efficient trans-splicing in the retina expands the utility of adeno-associated virus as a vector for gene therapy. Hum. Gene Ther. 14:37-44.
    • (2003) Hum. Gene Ther , vol.14 , pp. 37-44
    • Reich, S.J.1    Auricchio, A.2    Hildinger, M.3    Glover, E.4    Maguire, A.M.5    Wilson, J.M.6    Bennett, J.7
  • 57
    • 0033799367 scopus 로고    scopus 로고
    • Endocytosis and nuclear trafficking of adeno-associated virus type 2 are controlled by Rac1 and phophatidylinositol-3 kinase activation
    • Sanlioglu, S., P. K. Benson, J. Yang, E. M. Atkinson, T. Reynolds, and J. F. Engelhardt. 2000. Endocytosis and nuclear trafficking of adeno-associated virus type 2 are controlled by Rac1 and phophatidylinositol-3 kinase activation. J. Virol. 74:9184-9196.
    • (2000) J. Virol , vol.74 , pp. 9184-9196
    • Sanlioglu, S.1    Benson, P.K.2    Yang, J.3    Atkinson, E.M.4    Reynolds, T.5    Engelhardt, J.F.6
  • 58
    • 0033818902 scopus 로고    scopus 로고
    • Adeno-associated virus type 2 Rep78 induces apoptosis through caspase activation independently of p53
    • Schmidt, M., S. Afione, and R. M. Kotin. 2000. Adeno-associated virus type 2 Rep78 induces apoptosis through caspase activation independently of p53. J. Virol. 74:9441-9450.
    • (2000) J. Virol , vol.74 , pp. 9441-9450
    • Schmidt, M.1    Afione, S.2    Kotin, R.M.3
  • 59
    • 27744584507 scopus 로고    scopus 로고
    • Characterization of adeno-associated virus genomes isolated from human tissues
    • Schnepp, B. C., R. L. Jensen, C. L. Chen, P. R. Johnson, and K. R. Clark. 2005. Characterization of adeno-associated virus genomes isolated from human tissues. J. Virol. 79:4793-4803.
    • (2005) J. Virol , vol.79 , pp. 4793-4803
    • Schnepp, B.C.1    Jensen, R.L.2    Chen, C.L.3    Johnson, P.R.4    Clark, K.R.5
  • 60
    • 0020684648 scopus 로고
    • Nucleotide sequence and organization of the adeno-associated virus 2 genome
    • Srivastava, A., E. W. Lusby, and K. I. Berns. 1983. Nucleotide sequence and organization of the adeno-associated virus 2 genome. J. Virol. 45:555-564.
    • (1983) J. Virol , vol.45 , pp. 555-564
    • Srivastava, A.1    Lusby, E.W.2    Berns, K.I.3
  • 61
    • 33646760315 scopus 로고    scopus 로고
    • Mosaic vectors comprised of modified AAV 1 capsid proteins for efficient vector purification and targeting to vascular endothelial cells
    • Stachler, M. D., and J. S. Bartlett. 2006. Mosaic vectors comprised of modified AAV 1 capsid proteins for efficient vector purification and targeting to vascular endothelial cells. Gene Ther. 13:926-931.
    • (2006) Gene Ther , vol.13 , pp. 926-931
    • Stachler, M.D.1    Bartlett, J.S.2
  • 62
    • 0031906147 scopus 로고    scopus 로고
    • Membrane-associated heparin sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions
    • Summerford, C., and R. J. Samulski. 1998. Membrane-associated heparin sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions. J. Virol. 72:1438-1445.
    • (1998) J. Virol , vol.72 , pp. 1438-1445
    • Summerford, C.1    Samulski, R.J.2
  • 63
  • 64
    • 0035877583 scopus 로고    scopus 로고
    • Phosphorylation of a novel myosin binding subunit of protein phosphatase 1 reveals a conserved mechanism in the regulation of actin cytoskeleton
    • Tan, I., C. H. Ng, L. Lim, and T. Leung. 2001. Phosphorylation of a novel myosin binding subunit of protein phosphatase 1 reveals a conserved mechanism in the regulation of actin cytoskeleton. J. Biol. Chem. 276:21209-21216.
    • (2001) J. Biol. Chem , vol.276 , pp. 21209-21216
    • Tan, I.1    Ng, C.H.2    Lim, L.3    Leung, T.4
  • 67
    • 34247200575 scopus 로고    scopus 로고
    • Cross-presentation of adeno-associated virus serotype 2 capsids activated cytotoxic T cells but does not render hepatocytes effective cytolytic targets
    • Wang, L., J. Figueredo, R. Calcedo, J. Lin, and J. M. Wilson. 2007. Cross-presentation of adeno-associated virus serotype 2 capsids activated cytotoxic T cells but does not render hepatocytes effective cytolytic targets. Hum. Gene Ther. 18:185-194.
    • (2007) Hum. Gene Ther , vol.18 , pp. 185-194
    • Wang, L.1    Figueredo, J.2    Calcedo, R.3    Lin, J.4    Wilson, J.M.5
  • 68
    • 0028307303 scopus 로고
    • Adeno-associated virus (AAV) rep proteins mediate complex formation between AAV DNA and its integration site in human DNA
    • Weitzman, M. D., S. Kyostio, R. M. Kotin, and R. A. Owens. 1994. Adeno-associated virus (AAV) rep proteins mediate complex formation between AAV DNA and its integration site in human DNA. Proc. Natl. Acad. Sci. USA 91:5808-5812.
    • (1994) Proc. Natl. Acad. Sci. USA , vol.91 , pp. 5808-5812
    • Weitzman, M.D.1    Kyostio, S.2    Kotin, R.M.3    Owens, R.A.4
  • 70
    • 36348956106 scopus 로고    scopus 로고
    • A RAC reviews serious adverse event associated with AAV therapy trial
    • Williams, D. 2007. A RAC reviews serious adverse event associated with AAV therapy trial. Mol. Ther. 15:2053.
    • (2007) Mol. Ther , vol.15 , pp. 2053
    • Williams, D.1
  • 71
    • 33947410764 scopus 로고    scopus 로고
    • Self-complementary recombinant adeno-associated viral vectors: Packaging capacity and the role of the rep proteins in vectors purity
    • Wu, J., W. Zhao, L. Zhong, Z. Han, B. Li, W. Ma, K. A. Weigel-Kelley, K. H. Warrington, and A. Srivastava. 2007. Self-complementary recombinant adeno-associated viral vectors: packaging capacity and the role of the rep proteins in vectors purity. Hum. Gene Ther. 18:171-182.
    • (2007) Hum. Gene Ther , vol.18 , pp. 171-182
    • Wu, J.1    Zhao, W.2    Zhong, L.3    Han, Z.4    Li, B.5    Ma, W.6    Weigel-Kelley, K.A.7    Warrington, K.H.8    Srivastava, A.9
  • 72
    • 0029843596 scopus 로고    scopus 로고
    • Efficient long-term gene transfer into muscle of immunocompetent mice by adeno-associated virus vectors
    • Xiao, X., J. Li, and R. J. Samulski. 1996. Efficient long-term gene transfer into muscle of immunocompetent mice by adeno-associated virus vectors. J. Virol. 70:8098-8108.
    • (1996) J. Virol , vol.70 , pp. 8098-8108
    • Xiao, X.1    Li, J.2    Samulski, R.J.3
  • 74
    • 0034612248 scopus 로고    scopus 로고
    • trans-Splicing vectors expand utility of adeno-associated virus for gene therapy
    • Yan, Z., Y. Zhang, D. Duan, and J. F. Engelhardt. 2000. trans-Splicing vectors expand utility of adeno-associated virus for gene therapy. Proc. Natl. Acad. Sci. USA 97:6716-6721.
    • (2000) Proc. Natl. Acad. Sci. USA , vol.97 , pp. 6716-6721
    • Yan, Z.1    Zhang, Y.2    Duan, D.3    Engelhardt, J.F.4
  • 75
    • 0028228449 scopus 로고
    • Characterization of cell lines that inducibly express the adeno-associated virus Rep proteins
    • Yang, Q., F. Chen, and J. P. Trempe. 1994. Characterization of cell lines that inducibly express the adeno-associated virus Rep proteins. J. Virol. 68:4847-4856.
    • (1994) J. Virol , vol.68 , pp. 4847-4856
    • Yang, Q.1    Chen, F.2    Trempe, J.P.3
  • 76
    • 0036227449 scopus 로고    scopus 로고
    • Differential activation of innate immune response by adenovirus and adeno-associated virus vectors
    • Zaiss, A. K., Q. Liu, G. P. Bowen, N. C. Wong, J. S. Bartlett, and D. A. Muruve. 2002. Differential activation of innate immune response by adenovirus and adeno-associated virus vectors. J. Virol. 76:4580-4590.
    • (2002) J. Virol , vol.76 , pp. 4580-4590
    • Zaiss, A.K.1    Liu, Q.2    Bowen, G.P.3    Wong, N.C.4    Bartlett, J.S.5    Muruve, D.A.6
  • 77
    • 34848910204 scopus 로고    scopus 로고
    • Characterization of a bipartite recombinant adeno-associated virus vector for site-specific integration
    • Zhang, C., N. Cortez, and K. I. Berns. 2007. Characterization of a bipartite recombinant adeno-associated virus vector for site-specific integration. Hum. Gene Ther. 18:787-797.
    • (2007) Hum. Gene Ther , vol.18 , pp. 787-797
    • Zhang, C.1    Cortez, N.2    Berns, K.I.3
  • 78
    • 0033882190 scopus 로고    scopus 로고
    • CD40 ligand-dependent activation of cytotoxic T lymphocytes by adeno-associated virus vector in vivo: Role of immature dendritic cells
    • Zhang, Y. I., N. Chirmule, G. P. Gao, and J. M. Wilson. 2000. CD40 ligand-dependent activation of cytotoxic T lymphocytes by adeno-associated virus vector in vivo: role of immature dendritic cells. J. Virol. 74:8003-8010.
    • (2000) J. Virol , vol.74 , pp. 8003-8010
    • Zhang, Y.I.1    Chirmule, N.2    Gao, G.P.3    Wilson, J.M.4
  • 79
    • 33847789949 scopus 로고    scopus 로고
    • Adeno-associated virus 2-mediated gene transfer: Role of a cellular serine/threonine protein phosphatase in augmenting transduction efficiency
    • Zhao, W., J. Wu, L. Zhong, and A. Srivastava. 2007. Adeno-associated virus 2-mediated gene transfer: role of a cellular serine/threonine protein phosphatase in augmenting transduction efficiency. Gene Ther. 14:545-550.
    • (2007) Gene Ther , vol.14 , pp. 545-550
    • Zhao, W.1    Wu, J.2    Zhong, L.3    Srivastava, A.4
  • 80
    • 34250727017 scopus 로고    scopus 로고
    • A dual-role of EGFR protein kinase signaling in ubiquitination of AAV 2 capsids and viral second strand synthesis
    • Zhong, L., W. Zhao, J. Wu, B. Li, S. Zolotukhin, L. Govindasamy, M. Agbandje-McKenna, and A. Srivastava. 2007. A dual-role of EGFR protein kinase signaling in ubiquitination of AAV 2 capsids and viral second strand synthesis. Mol. Ther. 17:1323-1330.
    • (2007) Mol. Ther , vol.17 , pp. 1323-1330
    • Zhong, L.1    Zhao, W.2    Wu, J.3    Li, B.4    Zolotukhin, S.5    Govindasamy, L.6    Agbandje-McKenna, M.7    Srivastava, A.8


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.