Site-directed gene repair of the dystrophin gene mediated by PNA-ssODNs

Human Molecular Genetics

Volumn 19, Issue 16, 2010, Pages 3266-3281

  Kayali, Refik ^a   Bury, Frederic ^a   Ballard, McIver ^a   Bertoni, Carmen ^a  

^a UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

DYSTROPHIN; OLIGODEOXYNUCLEOTIDE; PEPTIDE NUCLEIC ACID; SINGLE STRANDED OLIGODEOXYNUCLEOTIDE; UNCLASSIFIED DRUG;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DNA HELIX; DNA ISOLATION; DNA REPAIR; DUCHENNE MUSCULAR DYSTROPHY; GENE SEQUENCE; GENE TARGETING; GENE THERAPY; GENETIC TRANSFECTION; MOUSE; MUSCLE CELL; NONHUMAN; POINT MUTATION; PRIORITY JOURNAL; PROTEIN EXPRESSION; REAL TIME POLYMERASE CHAIN REACTION; SEQUENCE ANALYSIS; SKELETAL MUSCLE; TREATMENT OUTCOME;

ANIMALS; ANIMALS, NEWBORN; BASE SEQUENCE; BLOTTING, WESTERN; CELLS, CULTURED; DNA REPAIR; DNA, SINGLE-STRANDED; DYSTROPHIN; GENE EXPRESSION; INJECTIONS, INTRAMUSCULAR; MICE; MICE, INBRED C57BL; MICE, INBRED MDX; MUSCLES; MUTATION; MYOBLASTS; OLIGODEOXYRIBONUCLEOTIDES; PEPTIDE NUCLEIC ACIDS; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION; TRANSFECTION;

MUS;

EID: 77955025555     PISSN: 09646906     EISSN: 14602083     Source Type: Journal    
DOI: 10.1093/hmg/ddq235     Document Type: Article

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