-
1
-
-
0030773892
-
Coupled effects of polybrene and calf serum on the efficiency of retroviral transduction and the stability of retroviral vectors
-
Andreadis S, Palsson BO (1997) Coupled effects of polybrene and calf serum on the efficiency of retroviral transduction and the stability of retroviral vectors. Hum Gene Ther 8:285-291
-
(1997)
Hum Gene Ther
, vol.8
, pp. 285-291
-
-
Andreadis, S.1
Palsson, B.O.2
-
2
-
-
0030865201
-
Moloney murine leukemia virus-derived retroviral vectors decay intracellularly with a half-life in the range of 5.5 to 7.5 h
-
Andreadis ST, Brott D, Fuller AO, Palsson BO (1997) Moloney murine leukemia virus-derived retroviral vectors decay intracellularly with a half-life in the range of 5.5 to 7.5 h. J Virol 71:7541-7548
-
(1997)
J Virol
, vol.71
, pp. 7541-7548
-
-
Andreadis, S.T.1
Brott, D.2
Fuller, A.O.3
Palsson, B.O.4
-
3
-
-
59449098985
-
Gene therapy for immunodeficiency due to adenosine deaminase deficiency
-
Aiuti A, Cattaneo F, Galimberti S, Benninghoff U, Cassani B, Callegaro L, Scaramuzza S, Andolfi G, Mirolo M, Brigida I, Tabucchi A, Carlucci F, Eibl M, Aker M, Slavin S, Al-Mousa H, Al Ghonaium A, Ferster A, Duppenthaler A, Notarangelo L, Wintergerst U, Buckley RH, Bregni M, Marktel S, Valsecchi MG, Rossi P, Ciceri F, Miniero R, Bordignon C, and Roncarolo MG (2009) Gene therapy for immunodeficiency due to adenosine deaminase deficiency. N Engl J Med 360:447-458
-
(2009)
N Engl J Med
, vol.360
, pp. 447-458
-
-
Aiuti, A.1
Cattaneo, F.2
Galimberti, S.3
Benninghoff, U.4
Cassani, B.5
Callegaro, L.6
Scaramuzza, S.7
Andolfi, G.8
Mirolo, M.9
Brigida, I.10
Tabucchi, A.11
Carlucci, F.12
Eibl, M.13
Aker, M.14
Slavin, S.15
Al-Mousa, H.16
Al Ghonaium, A.17
Ferster, A.18
Duppenthaler, A.19
Notarangelo, L.20
Wintergerst, U.21
Buckley, R.H.22
Bregni, M.23
Marktel, S.24
Valsecchi, M.G.25
Rossi, P.26
Ciceri, F.27
Miniero, R.28
Bordignon, C.29
Roncarolo, M.G.30
more..
-
4
-
-
44249120315
-
Effect of gene therapy on visual function in Leber's congenital amaurosis
-
Bainbridge JW, Smith AJ, Barker SS, Robbie S, Henderson R, Balaggan K, Viswanathan A, Holder GE, Stockman A, Tyler N, Petersen-Jones S, Bhattacharya SS, Thrasher AJ, Fitzke FW, Carter BJ, Rubin GS, Moore AT, Ali RR (2008) Effect of gene therapy on visual function in Leber's congenital amaurosis. N Engl J Med 358:2231-2239
-
(2008)
N Engl J Med
, vol.358
, pp. 2231-2239
-
-
Bainbridge, J.W.1
Smith, A.J.2
Barker, S.S.3
Robbie, S.4
Henderson, R.5
Balaggan, K.6
Viswanathan, A.7
Holder, G.E.8
Stockman, A.9
Tyler, N.10
Petersen-Jones, S.11
Bhattacharya, S.S.12
Thrasher, A.J.13
Fitzke, F.W.14
Carter, B.J.15
Rubin, G.S.16
Moore, A.T.17
Ali, R.R.18
-
5
-
-
44849130087
-
Genotoxicity in gene therapy: An account of vector integration and designer nucleases
-
Bohne J, Cathomen T (2008) Genotoxicity in gene therapy: an account of vector integration and designer nucleases. Curr Opin Mol Ther 10:214-223
-
(2008)
Curr Opin Mol Ther
, vol.10
, pp. 214-223
-
-
Bohne, J.1
Cathomen, T.2
-
6
-
-
0034724857
-
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
-
Cavazzana-Calvo M, Hacein-Bey S, de Saint Basile G, Gross F, Yvon E, Nusbaum P, Selz F, Hue C, Certain S, Casanova JL, Bousso P, Deist FL, Fischer A (2000) Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease. Science 288:669-672
-
(2000)
Science
, vol.288
, pp. 669-672
-
-
Cavazzana-Calvo, M.1
Hacein-Bey, S.2
De Saint Basile, G.3
Gross, F.4
Yvon, E.5
Nusbaum, P.6
Selz, F.7
Hue, C.8
Certain, S.9
Casanova, J.L.10
Bousso, P.11
Deist, F.L.12
Fischer, A.13
-
8
-
-
0033054126
-
Hightiter recombinant adeno-associated virus production utilizing a recombinant herpes simplex virus type i vector expressing AAV-2 rep and cap
-
Conway J, Rhys C, Zolotukhin I, Zolotukhin S, Muzyczka N, Hayward G, Byrne B (1999) Hightiter recombinant adeno-associated virus production utilizing a recombinant herpes simplex virus type I vector expressing AAV-2 rep and cap. Gene Ther 6:986-993
-
(1999)
Gene Ther
, vol.6
, pp. 986-993
-
-
Conway, J.1
Rhys, C.2
Zolotukhin, I.3
Zolotukhin, S.4
Muzyczka, N.5
Hayward, G.6
Byrne, B.7
-
9
-
-
0035835599
-
Supplemental guidance on testing for replication-competent retrovirus in retroviral vector-based gene therapy products and during follow-up of patients in clinical trials using retroviral vectors
-
FDA
-
FDA (2001) Supplemental guidance on testing for replication-competent retrovirus in retroviral vector-based gene therapy products and during follow-up of patients in clinical trials using retroviral vectors. Hum Gene Ther 12:315-320
-
(2001)
Hum Gene Ther
, vol.12
, pp. 315-320
-
-
-
10
-
-
15744365969
-
Integration of retroviruses: A fine balance between efficiency and danger
-
Fischer A, Cavazzana-Calvo M (2005) Integration of retroviruses: a fine balance between efficiency and danger. PLoS Med 2:e10
-
(2005)
PLoS Med
, vol.2
-
-
Fischer, A.1
Cavazzana-Calvo, M.2
-
11
-
-
19944421384
-
Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector
-
Gaspar HB, Parsley KL, Howe S, King D, Gilmour KC, Sinclair J, Brouns G, Schmidt M, Von Kalle C, Barington T, Jakobsen MA, Christensen HO, Al Ghonaium A, White HN, Smith JL, Levinsky RJ, Ali RR, Kinnon C, Thrasher AJ (2004) Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector. Lancet 364:2181-2187
-
(2004)
Lancet
, vol.364
, pp. 2181-2187
-
-
Gaspar, H.B.1
Parsley, K.L.2
Howe, S.3
King, D.4
Gilmour, K.C.5
Sinclair, J.6
Brouns, G.7
Schmidt, M.8
Von Kalle, C.9
Barington, T.10
Jakobsen, M.A.11
Christensen, H.O.12
Al Ghonaium, A.13
White, H.N.14
Smith, J.L.15
Levinsky, R.J.16
Ali, R.R.17
Kinnon, C.18
Thrasher, A.J.19
-
12
-
-
0001469617
-
-
Knipe DM, Howley PM (eds) Fields Virology, Lippincott, Philadelphia
-
Goff S (2001) Retroviridae: the retroviruses and theit replication. In: Knipe DM, Howley PM (eds) Fields Virology, vol 2. Lippincott, Philadelphia, pp 1871-1940
-
(2001)
Retroviridae: The Retroviruses and Theit Replication
, vol.2
, pp. 1871-1940
-
-
Goff, S.1
-
13
-
-
1542369977
-
From virus evolution to vector revolution: Use of naturally occurring serotypes of adeno-associated virus (AAV) as novel vectors for human gene therapy
-
Grimm D, Kay MA (2003) From virus evolution to vector revolution: use of naturally occurring serotypes of adeno-associated virus (AAV) as novel vectors for human gene therapy. Curr Gene Ther 3:281-304
-
(2003)
Curr Gene Ther
, vol.3
, pp. 281-304
-
-
Grimm, D.1
Kay, M.A.2
-
14
-
-
0038150506
-
Helper virus-free, optically controllable, and twoplasmid- based production of adeno-associated virus vectors of serotypes 1 to 6
-
Grimm D, Kay MA, Kleinschmidt JA (2003) Helper virus-free, optically controllable, and twoplasmid- based production of adeno-associated virus vectors of serotypes 1 to 6. Mol Ther 7:839-850
-
(2003)
Mol Ther
, vol.7
, pp. 839-850
-
-
Grimm, D.1
Kay, M.A.2
Kleinschmidt, J.A.3
-
15
-
-
0032506752
-
Novel tools for production and purification of recombinant adenoassociated virus vectors
-
Grimm D, Kern A, Rittner K, Kleinschmidt JA (1998) Novel tools for production and purification of recombinant adenoassociated virus vectors. Hum Gene Ther 9:2745-2760
-
(1998)
Hum Gene Ther
, vol.9
, pp. 2745-2760
-
-
Grimm, D.1
Kern, A.2
Rittner, K.3
Kleinschmidt, J.A.4
-
16
-
-
0142084745
-
LMO2- associated clonal T cell proliferation in two patients after gene therapy for SCID-X1
-
Hacein-Bey-Abina S, Von Kalle C, Schmidt M, McCormack MP, Wulffraat N, Leboulch P, Lim A, Osborne CS, Pawliuk R, Morillon E, Sorensen R, Forster A, Fraser P, Cohen JI, de Saint Basile G, Alexander I, Wintergerst U, Frebourg T, Aurias A, Stoppa-Lyonnet D, Romana S, Radford-Weiss I, Gross F, Valensi F, Delabesse E, Macintyre E, Sigaux F, Soulier J, Leiva LE, Wissler M, Prinz C, Rabbitts TH, Le Deist F, Fischer A, Cavazzana-Calvo M (2003) LMO2- associated clonal T cell proliferation in two patients after gene therapy for SCID-X1. Science 302:415-419
-
(2003)
Science
, vol.302
, pp. 415-419
-
-
Hacein-Bey-Abina, S.1
Von Kalle, C.2
Schmidt, M.3
McCormack, M.P.4
Wulffraat, N.5
Leboulch, P.6
Lim, A.7
Osborne, C.S.8
Pawliuk, R.9
Morillon, E.10
Sorensen, R.11
Forster, A.12
Fraser, P.13
Cohen, J.I.14
De Saint Basile, G.15
Alexander, I.16
Wintergerst, U.17
Frebourg, T.18
Aurias, A.19
Stoppa-Lyonnet, D.20
Romana, S.21
Radford-Weiss, I.22
Gross, F.23
Valensi, F.24
Delabesse, E.25
MacIntyre, E.26
Sigaux, F.27
Soulier, J.28
Leiva, L.E.29
Wissler, M.30
Prinz, C.31
Rabbitts, T.H.32
Le Deist, F.33
Fischer, A.34
Cavazzana-Calvo, M.35
more..
-
17
-
-
54949104686
-
Phase i trial of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: Shortterm results
-
Hauswirth W, Aleman TS, Kaushal S, Cideciyan AV, Schwartz SB, Wang L, Conlon T, Boye SL, Flotte TR, Byrne B, Jacobson SG (2008) Phase I trial of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: shortterm results. Hum Gene Ther 19:979-990
-
(2008)
Hum Gene Ther
, vol.19
, pp. 979-990
-
-
Hauswirth, W.1
Aleman, T.S.2
Kaushal, S.3
Cideciyan, A.V.4
Schwartz, S.B.5
Wang, L.6
Conlon, T.7
Boye, S.L.8
Flotte, T.R.9
Byrne, B.10
Jacobson, S.G.11
-
18
-
-
0344442392
-
SsDNA-dependent colocalization of adeno-associated virus Rep and herpes simplex virus ICP8 in nuclear replication domains
-
Heilbronn R, Engstler M, Weger S, Krahn A, Schetter C, Boshart M (2003) ssDNA-dependent colocalization of adeno-associated virus Rep and herpes simplex virus ICP8 in nuclear replication domains. Nucleic Acids Res 31:6206-6213
-
(2003)
Nucleic Acids Res
, vol.31
, pp. 6206-6213
-
-
Heilbronn, R.1
Engstler, M.2
Weger, S.3
Krahn, A.4
Schetter, C.5
Boshart, M.6
-
19
-
-
60449087086
-
An efficient rHSV-based complementation system for the production of multiple rAAV vector serotypes
-
Kang W, Wang L, Harrell H, Liu J, Thomas DL, Mayfield TL, Scotti MM, Ye GJ, Veres G, Knop DR (2009) An efficient rHSV-based complementation system for the production of multiple rAAV vector serotypes. Gene Ther 16:229-239
-
(2009)
Gene Ther
, vol.16
, pp. 229-239
-
-
Kang, W.1
Wang, L.2
Harrell, H.3
Liu, J.4
Thomas, D.L.5
Mayfield, T.L.6
Scotti, M.M.7
Ye, G.J.8
Veres, G.9
Knop, D.R.10
-
20
-
-
59449108477
-
Gene therapy fulfilling its promise
-
Kohn DB, Candotti F (2009) Gene therapy fulfilling its promise. N Engl J Med 360:518-521
-
(2009)
N Engl J Med
, vol.360
, pp. 518-521
-
-
Kohn, D.B.1
Candotti, F.2
-
21
-
-
27944479711
-
Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors
-
Lai Y, Yue Y, Liu M, Ghosh A, Engelhardt JF, Chamberlain JS, Duan D (2005) Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors. Nat Biotechnol 23:1435-1439
-
(2005)
Nat Biotechnol
, vol.23
, pp. 1435-1439
-
-
Lai, Y.1
Yue, Y.2
Liu, M.3
Ghosh, A.4
Engelhardt, J.F.5
Chamberlain, J.S.6
Duan, D.7
-
22
-
-
45749099260
-
Engineering and selection of shuffled AAV genomes: A new strategy for producing targeted biological nanoparticles
-
Li W, Asokan A, Wu Z, Van Dyke T, DiPrimio N, Johnson JS, Govindaswamy L, Agbandje- McKenna M, Leichtle S, Redmond DE Jr, McCown TJ, Petermann KB, Sharpless NE, Samulski RJ (2008) Engineering and selection of shuffled AAV genomes: a new strategy for producing targeted biological nanoparticles. Mol Ther 16:1252-1260
-
(2008)
Mol Ther
, vol.16
, pp. 1252-1260
-
-
Li, W.1
Asokan, A.2
Wu, Z.3
Van Dyke, T.4
Diprimio, N.5
Johnson, J.S.6
Govindaswamy, L.7
Agbandje- McKenna, M.8
Leichtle, S.9
Redmond Jr., D.E.10
McCown, T.J.11
Petermann, K.B.12
Sharpless, N.E.13
Samulski, R.J.14
-
23
-
-
0037431266
-
Real-time quantitative reverse transcriptase-polymerase chain reaction as a method for determining lentiviral vector titers and measuring transgene expression
-
Lizee G, Aerts JL, Gonzales MI, Chinnasamy N, Morgan RA, Topalian SL (2003) Real-time quantitative reverse transcriptase-polymerase chain reaction as a method for determining lentiviral vector titers and measuring transgene expression. Hum Gene Ther 14:497-507
-
(2003)
Hum Gene Ther
, vol.14
, pp. 497-507
-
-
Lizee, G.1
Aerts, J.L.2
Gonzales, M.I.3
Chinnasamy, N.4
Morgan, R.A.5
Topalian, S.L.6
-
24
-
-
44249085878
-
Safety and efficacy of gene transfer for Leber's congenital amaurosis
-
Maguire AM, Simonelli F, Pierce EA, Pugh EN Jr, Mingozzi F, Bennicelli J, Banfi S, Marshall KA, Testa F, Surace EM, Rossi S, Lyubarsky A, Arruda VR, Konkle B, Stone E, Sun J, Jacobs J, Dell'Osso L, Hertle R, Ma JX, Redmond TM, Zhu X, Hauck B, Zelenaia O, Shindler KS, Maguire MG, Wright JF, Volpe NJ, McDonnell JW, Auricchio A, High KA, Bennett J (2008) Safety and efficacy of gene transfer for Leber's congenital amaurosis. N Engl J Med 358:2240-2248
-
(2008)
N Engl J Med
, vol.358
, pp. 2240-2248
-
-
Maguire, A.M.1
Simonelli, F.2
Pierce, E.A.3
Mingozzi, F.4
Bennicelli, J.5
Banfi, S.6
Marshall, K.A.7
Testa, F.8
Surace, E.M.9
Rossi, S.10
Lyubarsky, A.11
Arruda, V.R.12
Konkle, B.13
Stone, E.14
Sun, J.15
Jacobs, J.16
Dell'Osso, L.17
Hertle, R.18
Ma, J.X.19
Redmond, T.M.20
Zhu, X.21
Hauck, B.22
Zelenaia, O.23
Shindler, K.S.24
Maguire, M.G.25
Wright, J.F.26
Volpe, N.J.27
McDonnell, J.W.28
Auricchio, A.29
High, K.A.30
Bennett, J.31
more..
-
25
-
-
4644323951
-
State-of-the-art of the production of retroviral vectors
-
Merten OW (2004) State-of-the-art of the production of retroviral vectors. J Gene Med 6(Suppl 1): S105-124
-
(2004)
J Gene Med
, vol.6
, Issue.SUPPL. 1
-
-
Merten, O.W.1
-
26
-
-
0025279872
-
Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection
-
Miller DG, Adam MA, Miller AD (1990) Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection. Mol Cell Biol 10:4239-4242
-
(1990)
Mol Cell Biol
, vol.10
, pp. 4239-4242
-
-
Miller, D.G.1
Adam, M.A.2
Miller, A.D.3
-
27
-
-
23844556421
-
Large-scale analysis of adeno-associated virus vector integration sites in normal human cells
-
Miller DG, Trobridge GD, Petek LM, Jacobs MA, Kaul R, Russell DW (2005) Large-scale analysis of adeno-associated virus vector integration sites in normal human cells. J Virol 79:11434-11442
-
(2005)
J Virol
, vol.79
, pp. 11434-11442
-
-
Miller, D.G.1
Trobridge, G.D.2
Petek, L.M.3
Jacobs, M.A.4
Kaul, R.5
Russell, D.W.6
-
28
-
-
19344375031
-
Retroviral DNA integration: ASLV, HIV, and MLV show distinct target site preferences
-
Mitchell RS, Beitzel BF, Schroder AR, Shinn P, Chen H, Berry CC, Ecker JR, Bushman FD (2004) Retroviral DNA integration: ASLV, HIV, and MLV show distinct target site preferences. PLoS Biol 2:E234
-
(2004)
PLoS Biol
, vol.2
-
-
Mitchell, R.S.1
Beitzel, B.F.2
Schroder, A.R.3
Shinn, P.4
Chen, H.5
Berry, C.C.6
Ecker, J.R.7
Bushman, F.D.8
-
29
-
-
33750624015
-
Cellculture assays reveal the importance of retroviral vector design for insertional genotoxicity
-
Modlich U, Bohne J, Schmidt M, von Kalle C, Knoss S, Schambach A, Baum C (2006) Cellculture assays reveal the importance of retroviral vector design for insertional genotoxicity. Blood 108:2545-2553
-
(2006)
Blood
, vol.108
, pp. 2545-2553
-
-
Modlich, U.1
Bohne, J.2
Schmidt, M.3
Von Kalle, C.4
Knoss, S.5
Schambach, A.6
Baum, C.7
-
30
-
-
0042360384
-
Random peptide libraries displayed on adeno-associated virus to select for targeted gene therapy vectors
-
Muller OJ, Kaul F, Weitzman MD, Pasqualini R, Arap W, Kleinschmidt JA, Trepel M (2003) Random peptide libraries displayed on adeno-associated virus to select for targeted gene therapy vectors. Nat Biotechnol 21:1040-1046
-
(2003)
Nat Biotechnol
, vol.21
, pp. 1040-1046
-
-
Muller, O.J.1
Kaul, F.2
Weitzman, M.D.3
Pasqualini, R.4
Arap, W.5
Kleinschmidt, J.A.6
Trepel, M.7
-
31
-
-
0001142644
-
-
Knipe DM, Howley PM (eds) Fields virology, Lippincott, Philadelphia
-
Muzyczka N, Berns KI (2001) Parvoviridae: the viruses and their replication. In: Knipe DM, Howley PM (eds) Fields virology, vol 2. Lippincott, Philadelphia, pp 2327-2359
-
(2001)
Parvoviridae: The Viruses and Their Replication
, vol.2
, pp. 2327-2359
-
-
Muzyczka, N.1
Berns, K.I.2
-
32
-
-
0042031468
-
In vitro selection of viral vectors with modified tropism: The adeno-associated virus display
-
Perabo L, Buning H, Kofler DM, Ried MU, Girod A, Wendtner CM, Enssle J, Hallek M (2003) In vitro selection of viral vectors with modified tropism: the adeno-associated virus display. Mol Ther 8:151-157
-
(2003)
Mol Ther
, vol.8
, pp. 151-157
-
-
Perabo, L.1
Buning, H.2
Kofler, D.M.3
Ried, M.U.4
Girod, A.5
Wendtner, C.M.6
Enssle, J.7
Hallek, M.8
-
33
-
-
61649095399
-
High-efficiency transduction of the mouse retina by tyrosine-mutant AAV serotype vectors
-
Petrs-Silva H, Dinculescu A, Li Q, Min SH, Chiodo V, Pang JJ, Zhong L, Zolotukhin S, Srivastava A, Lewin AS, Hauswirth WW (2009) High-efficiency transduction of the mouse retina by tyrosine-mutant AAV serotype vectors. Mol Ther 17:463-471
-
(2009)
Mol Ther
, vol.17
, pp. 463-471
-
-
Petrs-Silva, H.1
Dinculescu, A.2
Li, Q.3
Min, S.H.4
Chiodo, V.5
Pang, J.J.6
Zhong, L.7
Zolotukhin, S.8
Srivastava, A.9
Lewin, A.S.10
Hauswirth, W.W.11
-
34
-
-
34447134838
-
Use of nonintegrating lentiviral vectors for gene therapy
-
Philpott NJ, Thrasher AJ (2007) Use of nonintegrating lentiviral vectors for gene therapy. Hum Gene Ther 18:483-489
-
(2007)
Hum Gene Ther
, vol.18
, pp. 483-489
-
-
Philpott, N.J.1
Thrasher, A.J.2
-
35
-
-
0033675531
-
Breeding of retroviruses by DNA shuffling for improved stability and processing yields
-
Powell SK, Kaloss MA, Pinkstaff A, McKee R, Burimski I, Pensiero M, Otto E, Stemmer WP, Soong NW (2000) Breeding of retroviruses by DNA shuffling for improved stability and processing yields. Nat Biotechnol 18:1279-1282
-
(2000)
Nat Biotechnol
, vol.18
, pp. 1279-1282
-
-
Powell, S.K.1
Kaloss, M.A.2
Pinkstaff, A.3
McKee, R.4
Burimski, I.5
Pensiero, M.6
Otto, E.7
Stemmer, W.P.8
Soong, N.W.9
-
36
-
-
34248526597
-
Purification of retroviral vectors for clinical application: Biological implications and technological challenges
-
Rodrigues T, Carrondo MJ, Alves PM, Cruz PE (2007) Purification of retroviral vectors for clinical application: biological implications and technological challenges. J Biotechnol 127:520-541
-
(2007)
J Biotechnol
, vol.127
, pp. 520-541
-
-
Rodrigues, T.1
Carrondo, M.J.2
Alves, P.M.3
Cruz, P.E.4
-
37
-
-
0036713630
-
Titering lentiviral vectors: Comparison of DNA, RNA and marker expression methods
-
Sastry L, Johnson T, Hobson MJ, Smucker B, Cornetta K (2002) Titering lentiviral vectors: comparison of DNA, RNA and marker expression methods. Gene Ther 9:1155-1162
-
(2002)
Gene Ther
, vol.9
, pp. 1155-1162
-
-
Sastry, L.1
Johnson, T.2
Hobson, M.J.3
Smucker, B.4
Cornetta, K.5
-
38
-
-
20344394438
-
A novel purification strategy for retrovirus gene therapy vectors using heparin affinity chromatography
-
Segura MM, Kamen A, Trudel P, Garnier A (2005) A novel purification strategy for retrovirus gene therapy vectors using heparin affinity chromatography. Biotechnol Bioeng 90:391-404
-
(2005)
Biotechnol Bioeng
, vol.90
, pp. 391-404
-
-
Segura, M.M.1
Kamen, A.2
Trudel, P.3
Garnier, A.4
-
39
-
-
33645888418
-
Downstream processing of oncoretroviral and lentiviral gene therapy vectors
-
Segura MM, Kamen A, Garnier A (2006) Downstream processing of oncoretroviral and lentiviral gene therapy vectors. Biotechnol Adv 24:321-337
-
(2006)
Biotechnol Adv
, vol.24
, pp. 321-337
-
-
Segura, M.M.1
Kamen, A.2
Garnier, A.3
-
40
-
-
0036811528
-
Production of clinical-grade recombinant adeno-associated virus vectors
-
Snyder RO, Flotte TR (2002) Production of clinical-grade recombinant adeno-associated virus vectors. Curr Opin Biotechnol 13:418-423
-
(2002)
Curr Opin Biotechnol
, vol.13
, pp. 418-423
-
-
Snyder, R.O.1
Flotte, T.R.2
-
41
-
-
23844507993
-
Oncogenesis following delivery of a nonprimate lentiviral gene therapy vector to fetal and neonatal mice
-
Themis M, Waddington SN, Schmidt M, von Kalle C, Wang Y, Al-Allaf F, Gregory LG, Nivsarkar M, Themis M, Holder MV, Buckley SM, Dighe N, Ruthe AT, Mistry A, Bigger B, Rahim A, Nguyen TH, Trono D, Thrasher AJ, Coutelle C (2005) Oncogenesis following delivery of a nonprimate lentiviral gene therapy vector to fetal and neonatal mice. Mol Ther 12:763-771
-
(2005)
Mol Ther
, vol.12
, pp. 763-771
-
-
Themis, M.1
Waddington, S.N.2
Schmidt, M.3
Von Kalle, C.4
Wang, Y.5
Al-Allaf, F.6
Gregory, L.G.7
Nivsarkar, M.8
Themis, M.9
Holder, M.V.10
Buckley, S.M.11
Dighe, N.12
Ruthe, A.T.13
Mistry, A.14
Bigger, B.15
Rahim, A.16
Nguyen, T.H.17
Trono, D.18
Thrasher, A.J.19
Coutelle, C.20
more..
-
42
-
-
13644257036
-
Identification of a replication-defective herpes simplex virus for recombinant adeno-associated virus type 2 (rAAV2) particle assembly using stable producer cell lines
-
Toublanc E, Benraiss A, Bonnin D, Blouin V, Brument N, Cartier N, Epstein AL, Moullier P, Salvetti A (2004) Identification of a replication-defective herpes simplex virus for recombinant adeno-associated virus type 2 (rAAV2) particle assembly using stable producer cell lines. J Gene Med 6:555-564
-
(2004)
J Gene Med
, vol.6
, pp. 555-564
-
-
Toublanc, E.1
Benraiss, A.2
Bonnin, D.3
Blouin, V.4
Brument, N.5
Cartier, N.6
Epstein, A.L.7
Moullier, P.8
Salvetti, A.9
-
43
-
-
0036431701
-
Insect cells as a factory to produce adeno-associated virus type 2 vectors
-
Urabe M, Ding C, Kotin RM (2002) Insect cells as a factory to produce adeno-associated virus type 2 vectors. Hum Gene Ther 13:1935-1943
-
(2002)
Hum Gene Ther
, vol.13
, pp. 1935-1943
-
-
Urabe, M.1
Ding, C.2
Kotin, R.M.3
-
44
-
-
44349098092
-
Good news on the clinical gene transfer front
-
Wilson JM, Gansbacher B, Berns KI, Bosch F, Kay MA, Naldini L, Wei YQ (2008) Good news on the clinical gene transfer front. Hum Gene Ther 19:429-430
-
(2008)
Hum Gene Ther
, vol.19
, pp. 429-430
-
-
Wilson, J.M.1
Gansbacher, B.2
Berns, K.I.3
Bosch, F.4
Kay, M.A.5
Naldini, L.6
Wei, Y.Q.7
-
45
-
-
2642642141
-
Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus
-
Xiao X, Li J, Samulski RJ (1998) Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus. J Virol 72:2224-2232
-
(1998)
J Virol
, vol.72
, pp. 2224-2232
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
-
46
-
-
45549090635
-
Next generation of adeno-associated virus 2 vectors: Point mutations in tyrosines lead to high-efficiency transduction at lower doses
-
Zhong L, Li B, Mah CS, Govindasamy L, Agbandje-McKenna M, Cooper M, Herzog RW, Zolotukhin I, Warrington KH Jr, Weigel-Van Aken KA, Hobbs JA, Zolotukhin S, Muzyczka N, Srivastava A (2008) Next generation of adeno-associated virus 2 vectors: point mutations in tyrosines lead to high-efficiency transduction at lower doses. Proc Natl Acad Sci USA 105:7827-7832
-
(2008)
Proc Natl Acad Sci USA
, vol.105
, pp. 7827-7832
-
-
Zhong, L.1
Li, B.2
Mah, C.S.3
Govindasamy, L.4
Agbandje-Mckenna, M.5
Cooper, M.6
Herzog, R.W.7
Zolotukhin, I.8
Warrington Jr., K.H.9
Weigel-Van Aken, K.A.10
Hobbs, J.A.11
Zolotukhin, S.12
Muzyczka, N.13
Srivastava, A.14
-
47
-
-
19644381507
-
Production of recombinant adeno-associated virus vectors
-
Zolotukhin S (2005) Production of recombinant adeno-associated virus vectors. Hum Gene Ther 16:551-557
-
(2005)
Hum Gene Ther
, vol.16
, pp. 551-557
-
-
Zolotukhin, S.1
-
48
-
-
0033022953
-
Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield
-
Zolotukhin S, Byrne BJ, Mason E, Zolotukhin I, Potter M, Chesnut K, Summerford C, Samulski RJ, Muzyczka N (1999) Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield. Gene Ther 6:973-985
-
(1999)
Gene Ther
, vol.6
, pp. 973-985
-
-
Zolotukhin, S.1
Byrne, B.J.2
Mason, E.3
Zolotukhin, I.4
Potter, M.5
Chesnut, K.6
Summerford, C.7
Samulski, R.J.8
Muzyczka, N.9
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