Adeno-associated virus gene repair corrects a mouse model of hereditary tyrosinemia in vivo

Hepatology

Volumn 51, Issue 4, 2010, Pages 1200-1208

  Paulk, Nicole K ^a   Wursthorn, Karsten ^a,b   Wang, Zhongya ^a   Finegold, Milton J ^c   Kay, Mark A ^d   Grompe, Markus ^a  

^a OREGON HEALTH AND SCIENCE UNIVERSITY   (United States)

^b HANNOVER MEDICAL SCHOOL   (Germany)

^c TEXAS CHILDREN S HOSPITAL   (United States)

^d STANFORD UNIVERSITY   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

FUMARYLACETOACETASE; PARVOVIRUS VECTOR; VIRUS DNA;

ADENO ASSOCIATED VIRUS; ANALYTICAL PARAMETERS; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CELL PROLIFERATION; CONTROLLED STUDY; DNA REPAIR; GENE EXPRESSION; GENE FREQUENCY; GENE MUTATION; GENE SEQUENCE; HOMOLOGOUS RECOMBINATION; IMMUNOHISTOCHEMISTRY; IN VIVO STUDY; LIVER CELL; MOUSE; NEWBORN; NONHUMAN; NUCLEOTIDE SEQUENCE; POINT MUTATION; PRIORITY JOURNAL; REPRODUCIBILITY; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; SEROLOGY; SEROTYPE; TYROSINEMIA; VIRUS GENE;

ANIMALS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENETIC VECTORS; HYDROLASES; MICE; MICE, INBRED C57BL; TYROSINEMIAS;

EID: 77950610272     PISSN: 02709139     EISSN: 15273350     Source Type: Journal    
DOI: 10.1002/hep.23481     Document Type: Article

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