Sustainable correction of junctional epidermolysis bullosa via transposon-mediated nonviral gene transfer

Gene Therapy

Volumn 10, Issue 13, 2003, Pages 1099-1104

  Ortiz Urda, S ^a   Lin, Q ^a   Yant, S R ^a   Keene, D ^b   Kay, M A ^a   Khavari, P A ^a  

^a STANFORD UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b SHRINERS HOSPITAL FOR CHILDREN   (United States)

Author keywords

Epidermolysis bullosa; Gene therapy; Skin

Indexed keywords

BETA GALACTOSIDASE; COMPLEMENTARY DNA; KALININ; LAMININ; TRANSPOSASE; CELL ADHESION MOLECULE;

ANIMAL CELL; ARTICLE; BLISTER; CELL CLONING; CLINICAL ARTICLE; CONTROLLED STUDY; DNA INTEGRATION; EPIDERMIS; EPIDERMOLYSIS BULLOSA; GENE TRANSFER; HEMIDESMOSOME; HUMAN; HUMAN CELL; HUMAN GENOME; HUMAN TISSUE; KERATINOCYTE; MOUSE; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; PRIORITY JOURNAL; PROTEIN EXPRESSION; STEM CELL; TISSUE REGENERATION; TRANSPOSON; ANIMAL; DESMOSOME; GENE THERAPY; GENETICS; IMMUNOELECTRON MICROSCOPY; METABOLISM; METHODOLOGY; MOUSE MUTANT; REGENERATION; SKIN; ULTRASTRUCTURE;

ANIMALIA; TRANSPOSONS;

ANIMALS; CELL ADHESION MOLECULES; DESMOSOMES; DNA TRANSPOSABLE ELEMENTS; EPIDERMOLYSIS BULLOSA, JUNCTIONAL; GENE THERAPY; HUMANS; MICE; MICE, SCID; MICROSCOPY, IMMUNOELECTRON; REGENERATION; SKIN; STEM CELLS;

EID: 0037587235     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3301978     Document Type: Article

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