Single-stranded oligonucleotide-mediated in vivo gene repair in the rd1 retina

Molecular Vision

Volumn 13, Issue , 2007, Pages 692-706

  Andrieu Soler, Charlotte ^a,b,c,d   Halhal, Mounia ^a,b,c   Boatright, Jeffrey H ^e   Padove, Staci A ^e   Nickerson, John M ^e   Stodulkova, Eva ^e   Stewart, Rachael E ^e   Ciavatta, Vincent T ^e   Doat, Marc ^a,b,c   Jeanny, Jean Claude ^a,b,c   de Bizemont, Therèse ^a,b,c   Sennlaub, Florian ^a,b,c   Courtois, Yves ^a,b,c   Behar Cohen, Francine ^a,b,c,f,g  

^a CENTRE DE RECHERCHE DES CORDELIERS   (France)

^b UNIVERSITÉ PARIS DESCARTES   (France)

^c SORBONNE UNIVERSITÉ   (France)

^d Optis France   (France)

^e EMORY UNIVERSITY SCHOOL OF MEDICINE   (United States)

^f FONDATION OPHTALMOLOGIQUE ADOLPHE DE ROTHSCHILD   (France)

^g INSERM   (France)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; CYCLIC GMP PHOSPHODIESTERASE; GENOMIC DNA; RHODOPSIN;

ALLELE; ANIMAL CELL; ANIMAL TISSUE; ARTICLE; CELL COUNT; CELL NUCLEUS; CELL SURVIVAL; CONTROLLED STUDY; DNA REPAIR; GENE CONVERSION; GENE DELIVERY SYSTEM; GENE SEQUENCE; GENE TARGETING; IMMUNOHISTOCHEMISTRY; IMMUNOREACTIVITY; IN VIVO STUDY; IONTOPHORESIS; MEDICAL RESEARCH; MOUSE; NEWBORN; NON INVASIVE PROCEDURE; NONHUMAN; NUCLEOTIDE SEQUENCE; PHOTORECEPTOR; PHOTORECEPTOR CELL; POINT MUTATION; PRIORITY JOURNAL; QUANTITATIVE ANALYSIS; REAL TIME POLYMERASE CHAIN REACTION; REPRODUCIBILITY; RETINA DEGENERATION; RETINA ROD; TISSUE SECTION; TREATMENT OUTCOME; WILD TYPE;

AGING; ANIMALS; ANIMALS, NEWBORN; EYE; IMMUNOHISTOCHEMISTRY; IONTOPHORESIS; MICE; MICE, INBRED C3H; MICE, MUTANT STRAINS; OLIGONUCLEOTIDES; PHOSPHORIC DIESTER HYDROLASES; POINT MUTATION; RETINA; RETINAL DEGENERATION; RHODOPSIN; STAINING AND LABELING; TARGETED GENE REPAIR;

EID: 34248200353     PISSN: None     EISSN: 10900535     Source Type: Journal    
DOI: None     Document Type: Article

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