Efficient expression of CFTR function with adeno-associated virus vectors that carry shortened CFTR genes

Proceedings of the National Academy of Sciences of the United States of America

Volumn 95, Issue 17, 1998, Pages 10158-10163

  Zhang, Lei ^a   Wang, Danher ^a   Fischer, Horst ^b   Fan, Pei Dong ^a   Widdicombe, Jonathan H ^b   Kan, Yuet Wai ^a,c   Dong, Jian Yun ^a  

^a UNIVERSITY OF CALIFORNIA   (United States)

^b CHILDREN S HOSPITAL OAKLAND RESEARCH INSTITUTE   (United States)

^c UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

Chloride channel; Cystic fibrosis; Deletions; Gene therapy; Patch clamp

Indexed keywords

CHLORIDE CHANNEL; COMPLEMENTARY DNA; GENE PRODUCT; TRANSMEMBRANE CONDUCTANCE REGULATOR; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ARTICLE; CONTROLLED STUDY; CYSTIC FIBROSIS; GENE THERAPY; GENE TRANSFER; GENETIC ENGINEERING; HUMAN; HUMAN CELL; PRIORITY JOURNAL; RESPIRATORY EPITHELIUM; VIRION;

CELL LINE; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; DEPENDOVIRUS; DNA, COMPLEMENTARY; GENE EXPRESSION; GENE THERAPY; GENETIC ENGINEERING; GENETIC VECTORS; HELA CELLS; HUMANS; PROMOTER REGIONS (GENETICS); SEQUENCE DELETION; TRANSDUCTION, GENETIC;

ADENO-ASSOCIATED VIRUS; ANIMALIA;

EID: 0032544053     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.95.17.10158     Document Type: Article

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