Challenges and opportunities in dystrophin-deficient cardiomyopathy gene therapy

Human Molecular Genetics

Volumn 15, Issue SUPPL. 2, 2006, Pages

  Duan, Dongsheng ^a  

^a University of Missouri   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

DYSTROPHIN; PARVOVIRUS VECTOR; UTROPHIN; VERAPAMIL;

BECKER MUSCULAR DYSTROPHY; CARDIOTOXICITY; CONGESTIVE CARDIOMYOPATHY; DRUG FATALITY; DUCHENNE MUSCULAR DYSTROPHY; GENE OVEREXPRESSION; GENE TARGETING; GENE TRANSFER; GENE VECTOR; HEART FUNCTION; HUMAN; MORBIDITY; MORTALITY; NONHUMAN; PRIORITY JOURNAL; PROTEIN DEFICIENCY; PROTEIN EXPRESSION; REVIEW; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; VIRUS RECOMBINANT; X CHROMOSOME LINKED DISORDER;

ANIMALS; CARDIOMYOPATHIES; CARDIOMYOPATHY, DILATED; DYSTROPHIN; FEMALE; GENE THERAPY; HUMANS; MALE; MICE; MICE, INBRED MDX; MICE, KNOCKOUT; MUSCULAR DYSTROPHY, ANIMAL; MUSCULAR DYSTROPHY, DUCHENNE; MYOCARDIUM; MYOD PROTEIN; UTROPHIN;

ANIMALIA; RODENTIA;

EID: 33749004495     PISSN: 09646906     EISSN: 14602083     Source Type: Journal    
DOI: 10.1093/hmg/ddl180     Document Type: Review

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