Prolonged dystrophin expression and functional correction of mdx mouse muscle following gene transfer with a helper-dependent (gutted) adenovirus-encoding murine dystrophin

Human Molecular Genetics

Volumn 12, Issue 11, 2003, Pages 1287-1299

  Gilbert, Rénald ^a,c   Dudley, Roy W R ^b   Liu, An Bang ^a,d   Petrof, Basil J ^b   Nalbantoglu, Josephine ^a   Karpati, George ^a  

^a MCGILL UNIVERSITY   (Canada)

^b MCGILL UNIVERSITY   (Canada)

^c NATIONAL RESEARCH COUNCIL CANADA   (Canada)

^d BUDDHIST TZU CHI GENERAL HOSPITAL   (Taiwan)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; BETA ACTIN; COMPLEMENTARY DNA; DYSTROPHIN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL MEMBRANE; CELL NUCLEUS; COMPLEX FORMATION; CONTROLLED STUDY; CYTOMEGALOVIRUS; DRUG RESPONSE; DUCHENNE MUSCULAR DYSTROPHY; ENHANCER REGION; GENE DELETION; GENE EXPRESSION; GENE TRANSFER; GENETIC TRANSDUCTION; HUMORAL IMMUNITY; INFLAMMATION; MOUSE; MUSCLE CONTRACTION; MUSCLE FORCE; MUSCLE HYPERTROPHY; MUSCLE INJURY; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; PROTEIN LOCALIZATION; TIBIALIS ANTERIOR MUSCLE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; VIRUS GENE;

ACTINS; ADENOVIRIDAE; AGE FACTORS; ANIMALS; ANIMALS, NEWBORN; ANTIBODY FORMATION; DYSTROPHIN; GENE EXPRESSION REGULATION; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; INFLAMMATION; INJECTIONS, INTRAMUSCULAR; MICE; MICE, INBRED MDX; MUSCLE FIBERS; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE; PROMOTER REGIONS (GENETICS);

ADENOVIRIDAE; ANIMALIA; CYTOMEGALOVIRUS; DNA VIRUSES; MURINAE;

EID: 0038344798     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/ddg141     Document Type: Article

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