Transfer of full-length Dmd of the diaphragm muscle of Dmdmdx/mdx mice through systemic administration of plasmid DNA

Molecular Therapy

Volumn 4, Issue 1, 2001, Pages 45-51

  Liu, Feng ^a   Nishikawa, Makiya ^a   Clemens, Paula R ^b   Huang, Leaf ^a  

^a UNIVERSITY OF PITTSBURGH   (United States)

^b UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

Author keywords

Diaphragm; Dystrophin; Naked DNA; Systemic delivery

Indexed keywords

COMPLEMENTARY DNA; CYTOSKELETON PROTEIN; DYSTROPHIN; MUSCLE PROTEIN; PLASMID DNA;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BLOOD FLOW; CAUSE OF DEATH; CAVA VEIN; CONTROLLED STUDY; DIAPHRAGM MUSCLE; DUCHENNE MUSCULAR DYSTROPHY; GENE MUTATION; GENE SEQUENCE; GENE TRANSFER; GENETIC ANALYSIS; GENETIC CODE; MOUSE; MOUSE STRAIN; MUSCLE ATROPHY; NONHUMAN; PROTEIN ANALYSIS; RESPIRATORY FAILURE; TREATMENT PLANNING;

ANIMALIA;

EID: 0034920631     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.2001.0419     Document Type: Article

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