Suitability of oligonucleotide-mediated cystic fibrosis gene repair in airway epithelial cells

Journal of Gene Medicine

Volumn 5, Issue 7, 2003, Pages 625-639

  de Semir, David ^a   Nadal, Marga ^a   González, Juan R ^a   Larriba, Sara ^a   Avinyó, Anna ^a,b   Nunes, Virginia ^a   Casals, Teresa ^a   Estivill, Xavier ^a,c   Aran, Josep M ^a  

^a HOSPITAL DURAN I REYNALS   (Spain)

^b INSTITUT DE BIOLOGIA MOLECULAR DE BARCELONA   (Spain)

^c CENTRE FOR GENOMIC REGULATION CRG   (Spain)

Author keywords

Chimeraplasts; Non viral vectors; PCR OLA; W1282X mutation correction

Indexed keywords

GENOMIC DNA; OLIGONUCLEOTIDE; PHENYLALANINE; RNA; TRANSMEMBRANE CONDUCTANCE REGULATOR; TRYPTOPHAN; CFTR PROTEIN, HUMAN; HYBRID PROTEIN;

ALLELE; ARTICLE; BIOASSAY; BIOCHEMISTRY; BRONCHUS MUCOSA; CELL FREE SYSTEM; CELL NUCLEUS; CHIMERAPLASTY; CONFIDENCE INTERVAL; CONTROLLED STUDY; DRUG MECHANISM; DRUG STRUCTURE; ELECTROPORATION; EPITHELIUM CELL; EXON; GENE DELETION; GENE LOCUS; GENE MUTATION; GENE THERAPY; GENE VECTOR; GENOTYPE; HETEROZYGOTE; HUMAN; HUMAN CELL; LIVER CELL; LUNG CYST; LUNG FIBROSIS; METHODOLOGY; MISMATCH REPAIR; NONVIRAL GENE DELIVERY SYSTEM; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; QUANTITATIVE ANALYSIS; RESPIRATORY EPITHELIUM; STATISTICAL SIGNIFICANCE; WILD TYPE; BRONCHUS; CELL CULTURE; CYSTIC FIBROSIS; DNA REPAIR; EVALUATION; GENE EXPRESSION; GENE TARGETING; GENETICS; METABOLISM; MOLECULAR GENETICS; NUCLEOTIDE SEQUENCE; PHYSIOLOGY; POINT MUTATION;

BASE SEQUENCE; BRONCHI; CELL-FREE SYSTEM; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; DNA REPAIR; EPITHELIAL CELLS; GENE EXPRESSION; GENE TARGETING; GENE THERAPY; HUMANS; MOLECULAR SEQUENCE DATA; OLIGONUCLEOTIDES; POINT MUTATION; POLYMERASE CHAIN REACTION; RECOMBINANT FUSION PROTEINS; TUMOR CELLS, CULTURED;

EID: 0242525007     PISSN: 1099498X     EISSN: 15212254     Source Type: Journal    
DOI: 10.1002/jgm.374     Document Type: Article

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