Long-term high-level reconstitution of NADPH oxidase activity in murine X-linked chronic granulomatous disease using a bicistronic vector expressing gp91phox and a ΔLNGFR cell surface marker

Human Gene Therapy

Volumn 14, Issue 7, 2003, Pages 651-666

  Sadat, Mohammed A ^a   Pech, Nancy ^a   Saulnier, So ^b   Leroy, Brendan A ^a   Hossle, Johann P ^b   Grez, Manuel ^c   Dinauer, Mary C ^a  

^a INDIANA UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b UNIVERSITY CHILDREN S HOSPITAL   (Switzerland)

^c Laboratory for Molecular Virology   (Germany)

Author keywords

[No Author keywords available]

Indexed keywords

GENE PRODUCT; NERVE GROWTH FACTOR RECEPTOR; REDUCED NICOTINAMIDE ADENINE DINUCLEOTIDE PHOSPHATE OXIDASE; REDUCED NICOTINAMIDE ADENINE DINUCLEOTIDE PHOSPHATE OXIDASE 2; RETROVIRUS VECTOR; UNCLASSIFIED DRUG;

ANIMAL CELL; ARTICLE; BONE MARROW; CELL SURFACE; CHRONIC GRANULOMATOUS DISEASE; CISTRON; CONTROLLED STUDY; ENZYME ACTIVITY; ERYTHROCYTE; GENE EXPRESSION; GENE SILENCING; GRANULOCYTE; HUMAN; HUMAN CELL; IMMUNE DEFICIENCY; LONG TERMINAL REPEAT; LYMPHOCYTE; LYMPHOID ORGAN; MOUSE; NEUTROPHIL; NONHUMAN; PHAGOCYTE; PROVIRUS; TRANSGENE; VIRUS EXPRESSION; X CHROMOSOME LINKED DISORDER;

ANIMALS; ANTIGENS, SURFACE; BIOLOGICAL MARKERS; BLOOD CELL COUNT; BONE MARROW TRANSPLANTATION; CELL LINE; GENE EXPRESSION; GENETIC VECTORS; GRANULOMATOUS DISEASE, CHRONIC; HUMANS; KINETICS; L-LACTATE DEHYDROGENASE; L-LACTATE DEHYDROGENASE (CYTOCHROME); MEMBRANE GLYCOPROTEINS; MEMBRANE TRANSPORT PROTEINS; MICE; MICE, INBRED C57BL; NADPH DEHYDROGENASE; NADPH OXIDASE; NEUTROPHILS; PHOSPHOPROTEINS; RECEPTOR, NERVE GROWTH FACTOR; RESPIRATORY BURST; RETROVIRIDAE; SPLEEN FOCUS-FORMING VIRUSES; TRANSDUCTION, GENETIC;

ANIMALIA; MURINAE; SPLEEN FOCUS-FORMING VIRUS; UNIDENTIFIED RETROVIRUS;

EID: 0038407862     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/104303403321618164     Document Type: Article

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