메뉴 건너뛰기




Volumn 93, Issue 10, 1999, Pages 3276-3285

Transcriptional targeting of retroviral vectors to the erythroblastic progeny of transduced hematopoietic stem cells

Author keywords

[No Author keywords available]

Indexed keywords

DNA; TRANSCRIPTION FACTOR GATA 1; VIRUS VECTOR;

EID: 0033562853     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood.v93.10.3276.410k08_3276_3285     Document Type: Article
Times cited : (54)

References (54)
  • 1
    • 0027595949 scopus 로고
    • The basic science of gene therapy
    • Mulligan RC: The basic science of gene therapy. Science 260:926, 1993
    • (1993) Science , vol.260 , pp. 926
    • Mulligan, R.C.1
  • 2
    • 0028875936 scopus 로고
    • Transfer of genes to humans: Early lessons and obstacles to success
    • Crystal RG: Transfer of genes to humans: Early lessons and obstacles to success. Science 270:404, 1995
    • (1995) Science , vol.270 , pp. 404
    • Crystal, R.G.1
  • 3
    • 0030928619 scopus 로고    scopus 로고
    • Gene therapy-promises, problems and prospects
    • Verma IM, Somia N: Gene therapy-Promises, problems and prospects. Nature 389:239, 1997
    • (1997) Nature , vol.389 , pp. 239
    • Verma, I.M.1    Somia, N.2
  • 4
    • 0021726790 scopus 로고
    • Genes with promoters in retrovirus vectors can be independently suppressed by an epigenetic mechanism
    • Emerman M, Temin HM: Genes with promoters in retrovirus vectors can be independently suppressed by an epigenetic mechanism. Cell 39:449, 1984
    • (1984) Cell , vol.39 , pp. 449
    • Emerman, M.1    Temin, H.M.2
  • 5
    • 0022625565 scopus 로고
    • Quantitative analysis of gene suppression in integrated retrovirus vectors
    • Emerman M, Temin HM: Quantitative analysis of gene suppression in integrated retrovirus vectors. Mol Cell Biol 6:792, 1986
    • (1986) Mol Cell Biol , vol.6 , pp. 792
    • Emerman, M.1    Temin, H.M.2
  • 6
    • 0030996011 scopus 로고    scopus 로고
    • Progress in transcriptionally targeted and regulatable vectors for genetic therapy
    • Miller N, Whelan J: Progress in transcriptionally targeted and regulatable vectors for genetic therapy. Hum Gene Ther 8:803, 1997
    • (1997) Hum Gene Ther , vol.8 , pp. 803
    • Miller, N.1    Whelan, J.2
  • 11
    • 0024672667 scopus 로고
    • Improved gene expression upon transfer of the adenosine deaminase minigene outside the transcriptional unit of a retroviral vector
    • Hantzopoulos PA, Sullenger BA, Ungers G, Gilboa E: Improved gene expression upon transfer of the adenosine deaminase minigene outside the transcriptional unit of a retroviral vector. Proc Natl Acad Sci USA 86:3519, 1989
    • (1989) Proc Natl Acad Sci USA , vol.86 , pp. 3519
    • Hantzopoulos, P.A.1    Sullenger, B.A.2    Ungers, G.3    Gilboa, E.4
  • 12
    • 0022002466 scopus 로고
    • Suppression of leukaemia virus pathogenicity by polyoma virus enhancers
    • Davis B, Linney E, Fan H: Suppression of leukaemia virus pathogenicity by polyoma virus enhancers. Nature 314:550, 1985
    • (1985) Nature , vol.314 , pp. 550
    • Davis, B.1    Linney, E.2    Fan, H.3
  • 13
    • 0029079981 scopus 로고
    • A retroviral vector containing a muscle-specific enhancer drives gene expression only in differentiated muscle fibers
    • Ferrari G, Salvatori G, Rossi C, Cossu G, Mavilio F: A retroviral vector containing a muscle-specific enhancer drives gene expression only in differentiated muscle fibers. Hum Gene Ther 6:733, 1995
    • (1995) Hum Gene Ther , vol.6 , pp. 733
    • Ferrari, G.1    Salvatori, G.2    Rossi, C.3    Cossu, G.4    Mavilio, F.5
  • 14
    • 0031984750 scopus 로고    scopus 로고
    • Exchange of viral promoter/enhancer elements with heterologous regulatory sequences generates targeted hybrid long terminal repeat vectors for gene therapy of melanoma
    • Diaz RM, Eisen T, Hart IR, Vile RG: Exchange of viral promoter/enhancer elements with heterologous regulatory sequences generates targeted hybrid long terminal repeat vectors for gene therapy of melanoma. J Virol 72:789, 1998
    • (1998) J Virol , vol.72 , pp. 789
    • Diaz, R.M.1    Eisen, T.2    Hart, I.R.3    Vile, R.G.4
  • 15
    • 0024373139 scopus 로고
    • Cloning of cDNA for the major DNA-binding protein of the erythroid lineage through expression in mammalian cells
    • Tsai SF, Martin DI, Zon LI, D'Andrea AD, Wong GG, Orkin SH: Cloning of cDNA for the major DNA-binding protein of the erythroid lineage through expression in mammalian cells. Nature 339:446, 1989
    • (1989) Nature , vol.339 , pp. 446
    • Tsai, S.F.1    Martin, D.I.2    Zon, L.I.3    D'Andrea, A.D.4    Wong, G.G.5    Orkin, S.H.6
  • 16
    • 0024417073 scopus 로고
    • The erythroid-specific transcription factor Eryf1: A new finger protein
    • Evans T, Felsenfeld G: The erythroid-specific transcription factor Eryf1: A new finger protein. Cell 58:877, 1989
    • (1989) Cell , vol.58 , pp. 877
    • Evans, T.1    Felsenfeld, G.2
  • 17
    • 0025876999 scopus 로고
    • Functional analysis and in vivo footprinting implicate the erythroid transcription factor GATA-1 as a positive regulator of its own promoter
    • Tsai SF, Strauss E, Orkin SH: Functional analysis and in vivo footprinting implicate the erythroid transcription factor GATA-1 as a positive regulator of its own promoter. Genes Dev 5:919, 1991
    • (1991) Genes Dev , vol.5 , pp. 919
    • Tsai, S.F.1    Strauss, E.2    Orkin, S.H.3
  • 20
    • 0030660432 scopus 로고    scopus 로고
    • Cell-surface marking of CD(34+)-restricted phenotypes of human hematopoietic progenitor cells by retrovirus-mediated gene transfer
    • Ruggieri L, Aiuti A, Salomoni M, Zappone E, Ferrari G, Bordignon C: Cell-surface marking of CD(34+)-restricted phenotypes of human hematopoietic progenitor cells by retrovirus-mediated gene transfer. Hum Gene Ther 8:1611, 1997
    • (1997) Hum Gene Ther , vol.8 , pp. 1611
    • Ruggieri, L.1    Aiuti, A.2    Salomoni, M.3    Zappone, E.4    Ferrari, G.5    Bordignon, C.6
  • 21
    • 0024460181 scopus 로고
    • Improved retroviral vectors for gene transfer and expression
    • Miller AD, Rosman GJ: Improved retroviral vectors for gene transfer and expression. Biotechniques 7:980, 1989
    • (1989) Biotechniques , vol.7 , pp. 980
    • Miller, A.D.1    Rosman, G.J.2
  • 22
    • 0023871422 scopus 로고
    • A safe packaging line for gene transfer: Separating viral genes on two different plasmids
    • Markowitz D, Goff S, Bank A: A safe packaging line for gene transfer: Separating viral genes on two different plasmids. J Virol 62:1120, 1988
    • (1988) J Virol , vol.62 , pp. 1120
    • Markowitz, D.1    Goff, S.2    Bank, A.3
  • 23
    • 0024239024 scopus 로고
    • Construction and use of a safe and efficient amphotropic packaging cell line
    • Markowitz D, Goff S, Bank A: Construction and use of a safe and efficient amphotropic packaging cell line. Virology 167:400, 1988
    • (1988) Virology , vol.167 , pp. 400
    • Markowitz, D.1    Goff, S.2    Bank, A.3
  • 24
    • 0029084785 scopus 로고
    • Generation of a high-titer retroviral vector capable of expressing high levels of the human beta-globin gene
    • Sadelain M, Wang CH, Antoniou M, Grosveld F, Mulligan RC: Generation of a high-titer retroviral vector capable of expressing high levels of the human beta-globin gene. Proc Nad Acad Sci USA 92:6728, 1995
    • (1995) Proc Nad Acad Sci USA , vol.92 , pp. 6728
    • Sadelain, M.1    Wang, C.H.2    Antoniou, M.3    Grosveld, F.4    Mulligan, R.C.5
  • 25
    • 0031910732 scopus 로고    scopus 로고
    • Identification of distinct elements of the stromal microenvironment that control human hematopoietic stem/progenitor cell growth and differentiation
    • Aiuti A, Friedrich C, Sieff CA, Gutierrez-Ramos JC: Identification of distinct elements of the stromal microenvironment that control human hematopoietic stem/progenitor cell growth and differentiation. Exp Hematol 26:143, 1998
    • (1998) Exp Hematol , vol.26 , pp. 143
    • Aiuti, A.1    Friedrich, C.2    Sieff, C.A.3    Gutierrez-Ramos, J.C.4
  • 27
    • 0023158748 scopus 로고
    • Flow cytometric analysis of human bone marrow: I. Normal erythroid development
    • Loken MR, Shah VO, Dattilio KL, Civin CI: Flow cytometric analysis of human bone marrow: I. Normal erythroid development. Blood 69:255, 1987
    • (1987) Blood , vol.69 , pp. 255
    • Loken, M.R.1    Shah, V.O.2    Dattilio, K.L.3    Civin, C.I.4
  • 29
    • 0029843415 scopus 로고    scopus 로고
    • Temporal mapping of gene expression levels during the differentiation of individual primary hematopoietic cells
    • Cheng T, Shen H, Giokas D, Gere J, Tenen DG, Scadden DT: Temporal mapping of gene expression levels during the differentiation of individual primary hematopoietic cells. Proc Natl Acad Sci USA 93:13158, 1996
    • (1996) Proc Natl Acad Sci USA , vol.93 , pp. 13158
    • Cheng, T.1    Shen, H.2    Giokas, D.3    Gere, J.4    Tenen, D.G.5    Scadden, D.T.6
  • 31
    • 0026691333 scopus 로고
    • GATA-binding transcription factors in hematopoietic cells
    • Orkin SH: GATA-binding transcription factors in hematopoietic cells. Blood 80:575, 1992
    • (1992) Blood , vol.80 , pp. 575
    • Orkin, S.H.1
  • 33
    • 0030963918 scopus 로고    scopus 로고
    • A "knockdown" mutation created by cis-element gene targeting reveals the dependence of erythroid cell maturation on the level of transcription factor GATA-1
    • McDevitt MA, Shivdasani RA, Fujiwara Y, Yang H, Orkin SH: A "knockdown" mutation created by cis-element gene targeting reveals the dependence of erythroid cell maturation on the level of transcription factor GATA-1. Proc Natl Acad Sci USA 94:6781, 1997
    • (1997) Proc Natl Acad Sci USA , vol.94 , pp. 6781
    • McDevitt, M.A.1    Shivdasani, R.A.2    Fujiwara, Y.3    Yang, H.4    Orkin, S.H.5
  • 34
    • 0030807246 scopus 로고    scopus 로고
    • An upstream, DNase I hypersensitive region of the hematopoietic-expressed transcription factor GATA-1 gene confers developmental specificity in transgenic mice
    • McDevitt MA, Fujiwara Y, Shivdasani RA, Orkin SH: An upstream, DNase I hypersensitive region of the hematopoietic-expressed transcription factor GATA-1 gene confers developmental specificity in transgenic mice. Proc Natl Acad Sci USA 94:7976, 1997
    • (1997) Proc Natl Acad Sci USA , vol.94 , pp. 7976
    • McDevitt, M.A.1    Fujiwara, Y.2    Shivdasani, R.A.3    Orkin, S.H.4
  • 35
    • 0030926006 scopus 로고    scopus 로고
    • A lineage-selective knock-out establishes the critical role of transcription factor GATA-1 in megacaryocyte growth and platelet development
    • Shivdasani RA, Fujiwara Y, McDevitt MA, Orkin SH: A lineage-selective knock-out establishes the critical role of transcription factor GATA-1 in megacaryocyte growth and platelet development. EMBO J 16:3965, 1997
    • (1997) EMBO J , vol.16 , pp. 3965
    • Shivdasani, R.A.1    Fujiwara, Y.2    McDevitt, M.A.3    Orkin, S.H.4
  • 36
    • 0025976935 scopus 로고
    • Genetically modified skin fibroblasts persist long after trasplantation but gradually inactivate introduced genes
    • Palmer TD, Rosman GJ, Osborne WRA, Miller AD: Genetically modified skin fibroblasts persist long after trasplantation but gradually inactivate introduced genes. Proc Natl Acad Sci USA 88:1330, 1991
    • (1991) Proc Natl Acad Sci USA , vol.88 , pp. 1330
    • Palmer, T.D.1    Rosman, G.J.2    Osborne, W.R.A.3    Miller, A.D.4
  • 37
    • 0027465539 scopus 로고
    • Towards gene therapy for haemophilia B using primary human keratinocytes
    • Gerrard AJ, Hudson DL, Brownlee GG, Watt FM: Towards gene therapy for haemophilia B using primary human keratinocytes. Nat Genet 3:180, 1993
    • (1993) Nat Genet , vol.3 , pp. 180
    • Gerrard, A.J.1    Hudson, D.L.2    Brownlee, G.G.3    Watt, F.M.4
  • 38
    • 0028230779 scopus 로고
    • Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo
    • Challita PM, Kohn DB: Lack of expression from a retroviral vector after transduction of murine hematopoietic stem cells is associated with methylation in vivo. Proc Natl Acad Sci USA 91:2567, 1994
    • (1994) Proc Natl Acad Sci USA , vol.91 , pp. 2567
    • Challita, P.M.1    Kohn, D.B.2
  • 40
    • 0026666055 scopus 로고
    • Long-term expression of human adenosine deaminase in rhesus monkeys transplanted with retrovirus-infected bone marrow cells
    • van Beusechem VW, Kukler A, Heidt PJ, Valerio D: Long-term expression of human adenosine deaminase in rhesus monkeys transplanted with retrovirus-infected bone marrow cells. Proc Natl Acad Sci USA 89:7640, 1992
    • (1992) Proc Natl Acad Sci USA , vol.89 , pp. 7640
    • Van Beusechem, V.W.1    Kukler, A.2    Heidt, P.J.3    Valerio, D.4
  • 41
    • 0029164582 scopus 로고
    • Effects of retroviral vector design on expression of human adenosine deaminase in murine bone marrow transplant recipients engrafted with genetically modified cells
    • Riviere I, Brose K, Mulligan RC: Effects of retroviral vector design on expression of human adenosine deaminase in murine bone marrow transplant recipients engrafted with genetically modified cells. Proc Natl Acad Sci USA 92:6733, 1995
    • (1995) Proc Natl Acad Sci USA , vol.92 , pp. 6733
    • Riviere, I.1    Brose, K.2    Mulligan, R.C.3
  • 42
    • 0031907987 scopus 로고    scopus 로고
    • Expression pattern of CD2 locus control region containing retroviral vectors in hemopoietic cells in vitro and in vivo
    • Kaptein LC, Breuer M, Valerio D, van Beusechem VW: Expression pattern of CD2 locus control region containing retroviral vectors in hemopoietic cells in vitro and in vivo. Gene Ther 5:320, 1998
    • (1998) Gene Ther , vol.5 , pp. 320
    • Kaptein, L.C.1    Breuer, M.2    Valerio, D.3    Van Beusechem, V.W.4
  • 45
    • 0030065802 scopus 로고    scopus 로고
    • Towards gene therapy of hemoglobinopathies
    • Beuzard Y: Towards gene therapy of hemoglobinopathies. Semin Hematol 33:43, 1996
    • (1996) Semin Hematol , vol.33 , pp. 43
    • Beuzard, Y.1
  • 46
    • 0030229352 scopus 로고    scopus 로고
    • Gene therapy for thalassaemia
    • Ioannou P: Gene therapy for thalassaemia. Gene Ther 3:746, 1996
    • (1996) Gene Ther , vol.3 , pp. 746
    • Ioannou, P.1
  • 47
    • 0025295890 scopus 로고
    • High-level beta-globin expression after retroviral transfer of locus activation region-containing human beta-globin gene derivatives into murine erythroleukemia cells
    • Novak U, Harris EA, Forrester W, Groudine M, Gelinas R: High-level beta-globin expression after retroviral transfer of locus activation region-containing human beta-globin gene derivatives into murine erythroleukemia cells. Proc Natl Acad Sci USA 87:3386, 1990
    • (1990) Proc Natl Acad Sci USA , vol.87 , pp. 3386
    • Novak, U.1    Harris, E.A.2    Forrester, W.3    Groudine, M.4    Gelinas, R.5
  • 48
    • 0028303758 scopus 로고
    • Mutagenesis of retroviral vectors transducing human beta-globin gene and beta-globin locus control region derivatives results in stable transmission of an active transcriptional structure
    • Leboulch P, Huang GM, Humphries RK, Oh YH, Eaves CJ, Tuan DY, London IM: Mutagenesis of retroviral vectors transducing human beta-globin gene and beta-globin locus control region derivatives results in stable transmission of an active transcriptional structure. EMBO J 13:3065, 1994
    • (1994) EMBO J , vol.13 , pp. 3065
    • Leboulch, P.1    Huang, G.M.2    Humphries, R.K.3    Oh, Y.H.4    Eaves, C.J.5    Tuan, D.Y.6    London, I.M.7
  • 49
    • 0030836297 scopus 로고    scopus 로고
    • Long-term transfer and expression of the human ß-globin gene in a mouse transplant model
    • Raftopoulos H, Ward M, Leboulch P, Bank A: Long-term transfer and expression of the human ß-globin gene in a mouse transplant model. Blood 90:3414, 1997
    • (1997) Blood , vol.90 , pp. 3414
    • Raftopoulos, H.1    Ward, M.2    Leboulch, P.3    Bank, A.4
  • 50
    • 0031708415 scopus 로고    scopus 로고
    • The locus control region is necessary for gene expression in the human ß-globin locus but not the maintainance of an open chromatin structure in erythroid cells
    • Reik A, Telling A, Zitnik G, Cimbora D, Epner E, Groudine M: The locus control region is necessary for gene expression in the human ß-globin locus but not the maintainance of an open chromatin structure in erythroid cells. Mol Cell Biol 18:5992, 1998
    • (1998) Mol Cell Biol , vol.18 , pp. 5992
    • Reik, A.1    Telling, A.2    Zitnik, G.3    Cimbora, D.4    Epner, E.5    Groudine, M.6
  • 52
    • 0029077347 scopus 로고
    • Regulation of globin gene expression in erythroid cells
    • Orkin SH: Regulation of globin gene expression in erythroid cells. Eur J Biochem 231:271, 1995
    • (1995) Eur J Biochem , vol.231 , pp. 271
    • Orkin, S.H.1
  • 53
    • 0030219342 scopus 로고    scopus 로고
    • Regulation of beta-globin gene expression: Straightening out the locus
    • Martin DI, Fiering S, Groudine M: Regulation of beta-globin gene expression: Straightening out the locus. Curr Opin Gen Dev 6:488, 1996
    • (1996) Curr Opin Gen Dev , vol.6 , pp. 488
    • Martin, D.I.1    Fiering, S.2    Groudine, M.3
  • 54
    • 0003154471 scopus 로고
    • The thalassemias
    • Stamatoyannopoulos G, Nienhuis AW, Majerus PW, Varmus H (eds): Philadelphia, PA, Saunders
    • Weatherall DJ: The thalassemias, in Stamatoyannopoulos G, Nienhuis AW, Majerus PW, Varmus H (eds): The Molecular Basis of Blood Diseases (ed 2). Philadelphia, PA, Saunders, 1994, p 157
    • (1994) The Molecular Basis of Blood Diseases (Ed 2) , pp. 157
    • Weatherall, D.J.1


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.